KR102622411B1 - 핵염기 에디터의 aav 전달 - Google Patents

핵염기 에디터의 aav 전달 Download PDF

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KR102622411B1
KR102622411B1 KR1020197013648A KR20197013648A KR102622411B1 KR 102622411 B1 KR102622411 B1 KR 102622411B1 KR 1020197013648 A KR1020197013648 A KR 1020197013648A KR 20197013648 A KR20197013648 A KR 20197013648A KR 102622411 B1 KR102622411 B1 KR 102622411B1
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KR20190065403A (ko
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데이비드 알. 리우
조나단 마 레비
웨이 시 예
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프레지던트 앤드 펠로우즈 오브 하바드 칼리지
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    • C12N9/14—Hydrolases (3)
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    • C12N9/22—Ribonucleases [RNase]; Deoxyribonucleases [DNase]
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    • C12Y305/04—Hydrolases acting on carbon-nitrogen bonds, other than peptide bonds (3.5) in cyclic amidines (3.5.4)
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    • C12Y305/04—Hydrolases acting on carbon-nitrogen bonds, other than peptide bonds (3.5) in cyclic amidines (3.5.4)
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KR1020197013648A 2016-10-14 2017-10-13 핵염기 에디터의 aav 전달 Active KR102622411B1 (ko)

Priority Applications (1)

Application Number Priority Date Filing Date Title
KR1020247000273A KR20240007715A (ko) 2016-10-14 2017-10-13 핵염기 에디터의 aav 전달

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201662408575P 2016-10-14 2016-10-14
US62/408,575 2016-10-14
US201762475780P 2017-03-23 2017-03-23
US62/475,780 2017-03-23
PCT/US2017/056671 WO2018071868A1 (en) 2016-10-14 2017-10-13 Aav delivery of nucleobase editors

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KR20190065403A KR20190065403A (ko) 2019-06-11
KR102622411B1 true KR102622411B1 (ko) 2024-01-10

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US (2) US11306324B2 (enExample)
EP (1) EP3526320A1 (enExample)
JP (3) JP7588390B2 (enExample)
KR (2) KR20240007715A (enExample)
CN (1) CN110214180A (enExample)
AU (1) AU2017342543B2 (enExample)
CA (1) CA3039928A1 (enExample)
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US20150044192A1 (en) 2013-08-09 2015-02-12 President And Fellows Of Harvard College Methods for identifying a target site of a cas9 nuclease
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US9526784B2 (en) 2013-09-06 2016-12-27 President And Fellows Of Harvard College Delivery system for functional nucleases
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CN108026526B (zh) 2015-06-09 2023-05-12 爱迪塔斯医药公司 用于改善移植的crispr/cas相关方法和组合物
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