ES2389737T3 - Análogos de ácidos nucleicos bicíclicos modificados en 5' - Google Patents
Análogos de ácidos nucleicos bicíclicos modificados en 5' Download PDFInfo
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- ES2389737T3 ES2389737T3 ES07797414T ES07797414T ES2389737T3 ES 2389737 T3 ES2389737 T3 ES 2389737T3 ES 07797414 T ES07797414 T ES 07797414T ES 07797414 T ES07797414 T ES 07797414T ES 2389737 T3 ES2389737 T3 ES 2389737T3
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- -1 modified bicyclic nucleic acid Chemical class 0.000 title claims abstract description 166
- 102000039446 nucleic acids Human genes 0.000 title claims description 38
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- 125000003601 C2-C6 alkynyl group Chemical group 0.000 claims abstract description 27
- 125000000623 heterocyclic group Chemical group 0.000 claims abstract description 27
- 125000006239 protecting group Chemical group 0.000 claims abstract description 18
- 150000008300 phosphoramidites Chemical class 0.000 claims abstract description 17
- 229910052760 oxygen Inorganic materials 0.000 claims abstract description 14
- 229910052717 sulfur Inorganic materials 0.000 claims abstract description 14
- 125000002252 acyl group Chemical group 0.000 claims abstract description 13
- 125000002743 phosphorus functional group Chemical group 0.000 claims abstract description 12
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- 150000002367 halogens Chemical class 0.000 claims abstract description 8
- OAICVXFJPJFONN-UHFFFAOYSA-N Phosphorus Chemical compound [P] OAICVXFJPJFONN-UHFFFAOYSA-N 0.000 claims abstract description 7
- 239000011574 phosphorus Substances 0.000 claims abstract description 7
- 229910019142 PO4 Inorganic materials 0.000 claims abstract description 6
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Classifications
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- C—CHEMISTRY; METALLURGY
- C07—ORGANIC CHEMISTRY
- C07H—SUGARS; DERIVATIVES THEREOF; NUCLEOSIDES; NUCLEOTIDES; NUCLEIC ACIDS
- C07H19/00—Compounds containing a hetero ring sharing one ring hetero atom with a saccharide radical; Nucleosides; Mononucleotides; Anhydro-derivatives thereof
- C07H19/02—Compounds containing a hetero ring sharing one ring hetero atom with a saccharide radical; Nucleosides; Mononucleotides; Anhydro-derivatives thereof sharing nitrogen
- C07H19/04—Heterocyclic radicals containing only nitrogen atoms as ring hetero atom
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P3/00—Drugs for disorders of the metabolism
- A61P3/04—Anorexiants; Antiobesity agents
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P35/00—Antineoplastic agents
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- C—CHEMISTRY; METALLURGY
- C07—ORGANIC CHEMISTRY
- C07H—SUGARS; DERIVATIVES THEREOF; NUCLEOSIDES; NUCLEOTIDES; NUCLEIC ACIDS
- C07H21/00—Compounds containing two or more mononucleotide units having separate phosphate or polyphosphate groups linked by saccharide radicals of nucleoside groups, e.g. nucleic acids
Landscapes
- Chemical & Material Sciences (AREA)
- Health & Medical Sciences (AREA)
- Organic Chemistry (AREA)
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- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
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- Public Health (AREA)
- Pharmacology & Pharmacy (AREA)
- Chemical Kinetics & Catalysis (AREA)
- General Chemical & Material Sciences (AREA)
- Medicinal Chemistry (AREA)
- Child & Adolescent Psychology (AREA)
- Obesity (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Hematology (AREA)
- Diabetes (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Saccharide Compounds (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
Applications Claiming Priority (3)
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| US74705906P | 2006-05-11 | 2006-05-11 | |
| US747059P | 2006-05-11 | ||
| PCT/US2007/068690 WO2007134181A2 (en) | 2006-05-11 | 2007-05-10 | 5'-modified bicyclic nucleic acid analogs |
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|---|---|
| ES2389737T3 true ES2389737T3 (es) | 2012-10-31 |
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| ES07797414T Active ES2389737T3 (es) | 2006-05-11 | 2007-05-10 | Análogos de ácidos nucleicos bicíclicos modificados en 5' |
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| EP (1) | EP2066684B1 (enExample) |
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| AU (1) | AU2007249349B2 (enExample) |
| CA (1) | CA2651453C (enExample) |
| DK (1) | DK2066684T3 (enExample) |
| ES (1) | ES2389737T3 (enExample) |
| WO (1) | WO2007134181A2 (enExample) |
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| US7511131B2 (en) | 2002-11-13 | 2009-03-31 | Genzyme Corporation | Antisense modulation of apolipoprotein B expression |
| US7480382B2 (en) * | 2003-09-30 | 2009-01-20 | Microsoft Corporation | Image file container |
| US20050287558A1 (en) | 2004-05-05 | 2005-12-29 | Crooke Rosanne M | SNPs of apolipoprotein B and modulation of their expression |
| CN103301475B (zh) * | 2005-12-28 | 2016-08-03 | 斯克里普斯研究所 | 药物组合物和表达载体以及调节基因表达的方法和核酸分子的应用 |
| CA3042781C (en) | 2006-04-03 | 2021-10-19 | Roche Innovation Center Copenhagen A/S | Pharmaceutical composition comprising anti-mirna antisense oligonucleotides |
| EA201100811A1 (ru) | 2006-04-03 | 2012-06-29 | Сантарис Фарма А/С | Фармацевтическая композиция |
| US7666854B2 (en) * | 2006-05-11 | 2010-02-23 | Isis Pharmaceuticals, Inc. | Bis-modified bicyclic nucleic acid analogs |
| EP2410053B2 (en) * | 2006-10-18 | 2020-07-15 | Ionis Pharmaceuticals, Inc. | Antisense compounds |
| US8580756B2 (en) | 2007-03-22 | 2013-11-12 | Santaris Pharma A/S | Short oligomer antagonist compounds for the modulation of target mRNA |
| US8470791B2 (en) | 2007-03-22 | 2013-06-25 | Santaris Pharma A/S | RNA antagonist compounds for the inhibition of Apo-B100 expression |
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2007
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- 2007-05-10 WO PCT/US2007/068690 patent/WO2007134181A2/en not_active Ceased
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- 2007-05-10 CN CN2007800262854A patent/CN101490074B/zh active Active
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- 2007-05-10 EP EP07797414A patent/EP2066684B1/en active Active
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| Publication number | Publication date |
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| CA2651453C (en) | 2014-10-14 |
| EP2066684A2 (en) | 2009-06-10 |
| EP2066684B1 (en) | 2012-07-18 |
| US7750131B2 (en) | 2010-07-06 |
| JP2009536955A (ja) | 2009-10-22 |
| CN101490074B (zh) | 2013-06-26 |
| US7547684B2 (en) | 2009-06-16 |
| AU2007249349A1 (en) | 2007-11-22 |
| CN101490074A (zh) | 2009-07-22 |
| CA2651453A1 (en) | 2007-11-22 |
| JP5441688B2 (ja) | 2014-03-12 |
| WO2007134181A3 (en) | 2008-01-10 |
| US8030467B2 (en) | 2011-10-04 |
| US20100184966A1 (en) | 2010-07-22 |
| US20070287831A1 (en) | 2007-12-13 |
| US20090192302A1 (en) | 2009-07-30 |
| US8268980B2 (en) | 2012-09-18 |
| AU2007249349B2 (en) | 2012-03-08 |
| DK2066684T3 (da) | 2012-10-22 |
| US20120010393A1 (en) | 2012-01-12 |
| WO2007134181A2 (en) | 2007-11-22 |
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