JP2016501531A - 配列操作および治療適用のための系、方法および組成物の送達、エンジニアリングおよび最適化 - Google Patents

配列操作および治療適用のための系、方法および組成物の送達、エンジニアリングおよび最適化 Download PDF

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JP2016501531A
JP2016501531A JP2015547543A JP2015547543A JP2016501531A JP 2016501531 A JP2016501531 A JP 2016501531A JP 2015547543 A JP2015547543 A JP 2015547543A JP 2015547543 A JP2015547543 A JP 2015547543A JP 2016501531 A JP2016501531 A JP 2016501531A
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sequence
crispr
target
tracr
polynucleotide
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JP2016501531A5 (enExample
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フェン・ジャン
マティアス・ハイデンライク
フェイ・ラン
ウーカシュ・スウィーチ
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Broad Institute
Harvard University
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Broad Institute
Harvard University
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WO2023038020A1 (ja) 2021-09-07 2023-03-16 国立大学法人千葉大学 核酸配列改変用組成物および核酸配列の標的部位を改変する方法
WO2026034576A1 (ja) * 2024-08-07 2026-02-12 学校法人順天堂 ゲノムを切断しないゲノム編集方法、これを利用した遺伝子治療用組成物、及び組換えアデノウイルスベクター

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