JP5054975B2 - アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 - Google Patents

アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 Download PDF

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JP5054975B2
JP5054975B2 JP2006533879A JP2006533879A JP5054975B2 JP 5054975 B2 JP5054975 B2 JP 5054975B2 JP 2006533879 A JP2006533879 A JP 2006533879A JP 2006533879 A JP2006533879 A JP 2006533879A JP 5054975 B2 JP5054975 B2 JP 5054975B2
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aav
nos
sequences
syngeneic
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JP2007507223A5 (enExample
JP2007507223A (ja
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ウイルソン，ジエイムズ・エム
ガオ，グアングピング
アルビラ，モーリシオ・アール
バンデンバーグ，リユク・エイチ
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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JP2006533879A 2003-09-30 2004-09-30 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 Expired - Lifetime JP5054975B2 (ja)

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US50822603P 2003-09-30 2003-09-30
US60/508,226 2003-09-30
US56654604P 2004-04-29 2004-04-29
US60/566,546 2004-04-29
PCT/US2004/028817 WO2005033321A2 (en) 2003-09-30 2004-09-30 Adeno-associated virus (aav) clades, sequences, vectors containing same, and uses therefor

Related Child Applications (2)

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JP2010272649A Division JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Division JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途

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JP2007507223A JP2007507223A (ja) 2007-03-29
JP2007507223A5 JP2007507223A5 (enExample) 2007-11-22
JP5054975B2 true JP5054975B2 (ja) 2012-10-24

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JP2006533879A Expired - Lifetime JP5054975B2 (ja) 2003-09-30 2004-09-30 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2010272649A Expired - Lifetime JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Expired - Lifetime JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2013191907A Expired - Lifetime JP5911069B2 (ja) 2003-09-30 2013-09-17 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2015114170A Expired - Lifetime JP6335141B2 (ja) 2003-09-30 2015-06-04 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2016211386A Expired - Lifetime JP6516713B2 (ja) 2003-09-30 2016-10-28 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2018067535A Expired - Lifetime JP6673963B2 (ja) 2003-09-30 2018-03-30 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2019221986A Pending JP2020054373A (ja) 2003-09-30 2019-12-09 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2022161483A Pending JP2022173573A (ja) 2003-09-30 2022-10-06 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途

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JP2010272649A Expired - Lifetime JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Expired - Lifetime JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2013191907A Expired - Lifetime JP5911069B2 (ja) 2003-09-30 2013-09-17 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2015114170A Expired - Lifetime JP6335141B2 (ja) 2003-09-30 2015-06-04 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2016211386A Expired - Lifetime JP6516713B2 (ja) 2003-09-30 2016-10-28 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2018067535A Expired - Lifetime JP6673963B2 (ja) 2003-09-30 2018-03-30 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2019221986A Pending JP2020054373A (ja) 2003-09-30 2019-12-09 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2022161483A Pending JP2022173573A (ja) 2003-09-30 2022-10-06 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途

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US (13) US7906111B2 (enExample)
EP (7) EP1668143B1 (enExample)
JP (9) JP5054975B2 (enExample)
CN (4) CN102212558B (enExample)
AU (2) AU2004278684B2 (enExample)
BE (1) BE2021C533I2 (enExample)
CA (3) CA2537793C (enExample)
CY (3) CY1119833T1 (enExample)
DK (4) DK2292779T3 (enExample)
ES (5) ES2874298T3 (enExample)
FR (1) FR21C1037I1 (enExample)
HU (4) HUE054805T2 (enExample)
NZ (1) NZ545628A (enExample)
PL (2) PL3211085T3 (enExample)
PT (2) PT3211085T (enExample)
SI (2) SI3211085T1 (enExample)
WO (1) WO2005033321A2 (enExample)

Cited By (3)

* Cited by examiner, † Cited by third party
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JP2012175974A (ja) * 2003-09-30 2012-09-13 Trustees Of The Univ Of Pennsylvania アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
WO2020101042A1 (en) 2018-11-16 2020-05-22 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting utrophin gene
WO2020241903A1 (en) 2019-05-28 2020-12-03 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting dmpk gene

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CN103589692B (zh) * 2001-11-13 2018-07-24 宾夕法尼亚大学托管会 检测和/或鉴定腺伴随病毒(aav)序列以及分离所鉴定的新型序列的方法
DK2359869T3 (en) 2001-12-17 2019-04-15 Univ Pennsylvania Sequences of adeno-associated virus (AAV) serotype 8, vectors containing these, and uses thereof
US9233131B2 (en) 2003-06-30 2016-01-12 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
US9441244B2 (en) 2003-06-30 2016-09-13 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
US9592284B2 (en) 2004-04-28 2017-03-14 The Trustees Of The University Of Pennsylvania Immunization regimen with E4-deleted adenovirus prime and E1-deleted adenovirus boost
WO2006078279A2 (en) 2004-04-28 2006-07-27 The Trustees Of The University Of Pennsylvania Sequential delivery of immunogenic molecules via adenovirus and adeno-associated virus-mediated administrations
DE23193606T1 (de) 2005-04-07 2024-02-15 The Trustees Of The University Of Pennsylvania Verfahren zur erhöhung der funktion eines aav-vektors
US7588772B2 (en) 2006-03-30 2009-09-15 Board Of Trustees Of The Leland Stamford Junior University AAV capsid library and AAV capsid proteins
EP2009990B1 (en) 2006-04-07 2016-09-21 The Board of Regents of The University of Texas System Methods and compositions related to adenoassociated virus-phage particles
CN101528916B (zh) 2006-04-28 2013-09-04 宾夕法尼亚大学托管会 规模可调的aav生产方法
JP2009535339A (ja) * 2006-04-28 2009-10-01 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア 低下されたキャプシド免疫原性を有する改変ａａｖベクターおよびその使用
US9725485B2 (en) 2012-05-15 2017-08-08 University Of Florida Research Foundation, Inc. AAV vectors with high transduction efficiency and uses thereof for gene therapy
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