JP5054975B2 - アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 - Google Patents

アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 Download PDF

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JP5054975B2
JP5054975B2 JP2006533879A JP2006533879A JP5054975B2 JP 5054975 B2 JP5054975 B2 JP 5054975B2 JP 2006533879 A JP2006533879 A JP 2006533879A JP 2006533879 A JP2006533879 A JP 2006533879A JP 5054975 B2 JP5054975 B2 JP 5054975B2
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aav
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sequences
syngeneic
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JP2007507223A (ja
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ウイルソン，ジエイムズ・エム
ガオ，グアングピング
アルビラ，モーリシオ・アール
バンデンバーグ，リユク・エイチ
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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    • C12N2750/14011—Parvoviridae
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    • C12N2750/14011—Parvoviridae
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    • C12N2830/80—Vector systems having a special element relevant for transcription from vertebrates
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JP2006533879A 2003-09-30 2004-09-30 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 Expired - Lifetime JP5054975B2 (ja)

Applications Claiming Priority (5)

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US50822603P 2003-09-30 2003-09-30
US60/508,226 2003-09-30
US56654604P 2004-04-29 2004-04-29
US60/566,546 2004-04-29
PCT/US2004/028817 WO2005033321A2 (en) 2003-09-30 2004-09-30 Adeno-associated virus (aav) clades, sequences, vectors containing same, and uses therefor

Related Child Applications (2)

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JP2010272649A Division JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Division JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途

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JP2007507223A JP2007507223A (ja) 2007-03-29
JP2007507223A5 JP2007507223A5 (enExample) 2007-11-22
JP5054975B2 true JP5054975B2 (ja) 2012-10-24

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JP2006533879A Expired - Lifetime JP5054975B2 (ja) 2003-09-30 2004-09-30 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2010272649A Expired - Lifetime JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Expired - Lifetime JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2013191907A Expired - Lifetime JP5911069B2 (ja) 2003-09-30 2013-09-17 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2015114170A Expired - Lifetime JP6335141B2 (ja) 2003-09-30 2015-06-04 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2016211386A Expired - Lifetime JP6516713B2 (ja) 2003-09-30 2016-10-28 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2018067535A Expired - Lifetime JP6673963B2 (ja) 2003-09-30 2018-03-30 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2019221986A Pending JP2020054373A (ja) 2003-09-30 2019-12-09 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2022161483A Pending JP2022173573A (ja) 2003-09-30 2022-10-06 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途

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JP2010272649A Expired - Lifetime JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Expired - Lifetime JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2013191907A Expired - Lifetime JP5911069B2 (ja) 2003-09-30 2013-09-17 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2015114170A Expired - Lifetime JP6335141B2 (ja) 2003-09-30 2015-06-04 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2016211386A Expired - Lifetime JP6516713B2 (ja) 2003-09-30 2016-10-28 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2018067535A Expired - Lifetime JP6673963B2 (ja) 2003-09-30 2018-03-30 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2019221986A Pending JP2020054373A (ja) 2003-09-30 2019-12-09 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2022161483A Pending JP2022173573A (ja) 2003-09-30 2022-10-06 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途

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US (13) US7906111B2 (enExample)
EP (7) EP3211085B1 (enExample)
JP (9) JP5054975B2 (enExample)
CN (4) CN1856576B (enExample)
AU (2) AU2004278684B2 (enExample)
BE (1) BE2021C533I2 (enExample)
CA (3) CA3072423A1 (enExample)
CY (3) CY1119833T1 (enExample)
DK (4) DK2292779T3 (enExample)
ES (5) ES2555612T3 (enExample)
FR (1) FR21C1037I1 (enExample)
HU (4) HUE033158T2 (enExample)
NZ (1) NZ545628A (enExample)
PL (2) PL3211085T3 (enExample)
PT (2) PT3211085T (enExample)
SI (2) SI3211085T1 (enExample)
WO (1) WO2005033321A2 (enExample)

Cited By (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2012175974A (ja) * 2003-09-30 2012-09-13 Trustees Of The Univ Of Pennsylvania アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
WO2020101042A1 (en) 2018-11-16 2020-05-22 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting utrophin gene
WO2020241903A1 (en) 2019-05-28 2020-12-03 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting dmpk gene

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HU230406B1 (hu) 2001-11-13 2016-04-28 The Trustees Of The University Of Pennsylvania Eljárás adeno-asszociált vírus(AAV)szekvenciák detektálására és/vagy azonosítására és az azzal azonosított új szekvenciák izolálására
FI3517134T3 (fi) 2001-12-17 2024-04-03 Univ Pennsylvania Adeno-assosioituneen viruksen (aav) serotyypin 8 sekvenssejä, niitä sisältäviä vektoreita ja niiden käyttöjä
US9233131B2 (en) 2003-06-30 2016-01-12 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
US9441244B2 (en) 2003-06-30 2016-09-13 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
WO2006033672A2 (en) 2004-04-28 2006-03-30 The Trustees Of The University Of Pennsylvania Immunization regimen with e4-deleted adenovirus prime and e1-deleted adenovirus boost
EP1742668B1 (en) 2004-04-28 2011-02-09 The Trustees of The University of Pennsylvania Sequential delivery of immunogenic molecules via adenovirus and adeno-associated virus-mediated administrations
WO2006110689A2 (en) * 2005-04-07 2006-10-19 The Trustees Of The University Of Pennsylvania Method of increasing the function of an aav vector
EP2007795B1 (en) 2006-03-30 2016-11-16 The Board Of Trustees Of The Leland Stanford Junior University Aav capsid proteins
DK2009990T3 (en) * 2006-04-07 2017-01-09 Univ Texas METHODS AND COMPOSITIONS RELATED TO adenoassociated VIRUSFAGPARTIKLER
CN101495624A (zh) * 2006-04-28 2009-07-29 宾夕法尼亚州立大学托管会 衣壳免疫原性降低的经修饰aav载体及其用途
JP5268890B2 (ja) 2006-04-28 2013-08-21 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア Ａａｖの規模適応性の製造方法
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