JP6401871B2 - パーキンソン病の治療のためのａａｄｃポリヌクレオチド - Google Patents

パーキンソン病の治療のためのａａｄｃポリヌクレオチド Download PDF

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JP6401871B2
JP6401871B2 JP2017544285A JP2017544285A JP6401871B2 JP 6401871 B2 JP6401871 B2 JP 6401871B2 JP 2017544285 A JP2017544285 A JP 2017544285A JP 2017544285 A JP2017544285 A JP 2017544285A JP 6401871 B2 JP6401871 B2 JP 6401871B2
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aadc
administration
sequence
aav
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JP2017535291A (ja
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コティン、ロバート
フィリップ ケルズ、エイドリアン
フィリップ ケルズ、エイドリアン
ラビナ、バーナード
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Voyager Therapeutics Inc
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    • C12Y401/01—Carboxy-lyases (4.1.1)
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14121—Viruses as such, e.g. new isolates, mutants or their genomic sequences
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
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    • C12N2830/00—Vector systems having a special element relevant for transcription
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    • C12N2830/00—Vector systems having a special element relevant for transcription
    • C12N2830/50—Vector systems having a special element relevant for transcription regulating RNA stability, not being an intron, e.g. poly A signal

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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
JP2017544285A 2014-11-05 2015-11-05 パーキンソン病の治療のためのａａｄｃポリヌクレオチド Active JP6401871B2 (ja)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US201462075298P 2014-11-05 2014-11-05
US62/075,298 2014-11-05
US201562155692P 2015-05-01 2015-05-01
US62/155,692 2015-05-01
US201562199578P 2015-07-31 2015-07-31
US62/199,578 2015-07-31
US201562243537P 2015-10-19 2015-10-19
US62/243,537 2015-10-19
PCT/US2015/059201 WO2016073693A2 (en) 2014-11-05 2015-11-05 Aadc polynucleotides for the treatment of parkinson's disease

Related Child Applications (2)

Application Number Title Priority Date Filing Date
JP2018165535A Division JP6878370B2 (ja) 2014-11-05 2018-09-05 パーキンソン病の治療のためのａａｄｃポリヌクレオチド
JP2018167418A Division JP2019010110A (ja) 2014-11-05 2018-09-07 パーキンソン病の治療のためのａａｄｃポリヌクレオチド

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JP2017535291A JP2017535291A (ja) 2017-11-30
JP6401871B2 true JP6401871B2 (ja) 2018-10-10

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JP2017544285A Active JP6401871B2 (ja) 2014-11-05 2015-11-05 パーキンソン病の治療のためのａａｄｃポリヌクレオチド
JP2018165535A Active JP6878370B2 (ja) 2014-11-05 2018-09-05 パーキンソン病の治療のためのａａｄｃポリヌクレオチド
JP2018167418A Pending JP2019010110A (ja) 2014-11-05 2018-09-07 パーキンソン病の治療のためのａａｄｃポリヌクレオチド
JP2021075923A Pending JP2021106619A (ja) 2014-11-05 2021-04-28 パーキンソン病の治療のためのａａｄｃポリヌクレオチド

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JP2018165535A Active JP6878370B2 (ja) 2014-11-05 2018-09-05 パーキンソン病の治療のためのａａｄｃポリヌクレオチド
JP2018167418A Pending JP2019010110A (ja) 2014-11-05 2018-09-07 パーキンソン病の治療のためのａａｄｃポリヌクレオチド
JP2021075923A Pending JP2021106619A (ja) 2014-11-05 2021-04-28 パーキンソン病の治療のためのａａｄｃポリヌクレオチド

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US (7) US10335466B2 (https=)
EP (1) EP3215191B1 (https=)
JP (4) JP6401871B2 (https=)
KR (1) KR20170096998A (https=)
CN (2) CN112553229A (https=)
AU (2) AU2015343037B2 (https=)
BR (1) BR112017009497A2 (https=)
CA (1) CA2966620A1 (https=)
HK (1) HK1243922A1 (https=)
IL (2) IL251787B (https=)
MX (1) MX2017005834A (https=)
RU (2) RU2716991C2 (https=)
SG (2) SG11201703148TA (https=)
WO (1) WO2016073693A2 (https=)

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