MX388221B - ADMINISTRACIÓN DE VIRUS ADENO-ASOCIADO RECOMBINANTE DE CONSTRUCCIONES DE POLINUCLÉOTIDOS U7snRNA DIRIGIDA AL EXÓN 2. - Google Patents

ADMINISTRACIÓN DE VIRUS ADENO-ASOCIADO RECOMBINANTE DE CONSTRUCCIONES DE POLINUCLÉOTIDOS U7snRNA DIRIGIDA AL EXÓN 2.

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Publication number
MX388221B
MX388221B MX2015014712A MX2015014712A MX388221B MX 388221 B MX388221 B MX 388221B MX 2015014712 A MX2015014712 A MX 2015014712A MX 2015014712 A MX2015014712 A MX 2015014712A MX 388221 B MX388221 B MX 388221B
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MX
Mexico
Prior art keywords
associated virus
recombinant adeno
polynucleotide constructs
constructs targeting
targeting exon
Prior art date
Application number
MX2015014712A
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English (en)
Other versions
MX2015014712A (es
Inventor
Adeline Vulin-Chaffiol
Kevin Flanigan
Nicolas Wein
Original Assignee
Res Institute At Nationwide Children´S Hospital
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Application filed by Res Institute At Nationwide Children´S Hospital filed Critical Res Institute At Nationwide Children´S Hospital
Publication of MX2015014712A publication Critical patent/MX2015014712A/es
Publication of MX388221B publication Critical patent/MX388221B/es

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Abstract

La presente invención se refiere a un virus adeno-asociado recombinante (Raav), en donde el genoma del rAAV comprende al menos una construcción e polinucleótidos U7snRNA dirigida al exón 2 que comprende la secuencia de nucléotidos establecida en SEQ ID NO: 3, 5, 6, y u 8, o una combinación de dos o más de una construcción de polinucleótido U7snRNA dirigida al exón 2 que comprende la secuencia de nucleótidos establecida en la SEQ ID NO: 3, 5, 6 7 u 8 .
MX2015014712A 2013-04-20 2014-04-18 ADMINISTRACIÓN DE VIRUS ADENO-ASOCIADO RECOMBINANTE DE CONSTRUCCIONES DE POLINUCLÉOTIDOS U7snRNA DIRIGIDA AL EXÓN 2. MX388221B (es)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201361814256P 2013-04-20 2013-04-20
PCT/US2014/034702 WO2014172669A1 (en) 2013-04-20 2014-04-18 Recombinant adeno-associated virus delivery of exon 2-targeted u7snrna polynucleotide constructs

Publications (2)

Publication Number Publication Date
MX2015014712A MX2015014712A (es) 2016-04-27
MX388221B true MX388221B (es) 2025-03-19

Family

ID=50933493

Family Applications (2)

Application Number Title Priority Date Filing Date
MX2015014712A MX388221B (es) 2013-04-20 2014-04-18 ADMINISTRACIÓN DE VIRUS ADENO-ASOCIADO RECOMBINANTE DE CONSTRUCCIONES DE POLINUCLÉOTIDOS U7snRNA DIRIGIDA AL EXÓN 2.
MX2021002845A MX2021002845A (es) 2013-04-20 2015-10-20 Suministro de virus adeno-asociado recombinante de construcciones de polinucleotido u7snrna dirigido a exon 2.

Family Applications After (1)

Application Number Title Priority Date Filing Date
MX2021002845A MX2021002845A (es) 2013-04-20 2015-10-20 Suministro de virus adeno-asociado recombinante de construcciones de polinucleotido u7snrna dirigido a exon 2.

Country Status (10)

Country Link
US (3) US9862945B2 (es)
EP (2) EP3461838A1 (es)
JP (4) JP6461917B2 (es)
KR (4) KR102413498B1 (es)
CN (2) CN109652385A (es)
AU (5) AU2014253730B2 (es)
CA (2) CA2909807C (es)
EA (2) EA201990558A3 (es)
MX (2) MX388221B (es)
WO (1) WO2014172669A1 (es)

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