KR102268473B9 - 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달 - Google Patents

엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달

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KR102268473B9
KR102268473B9 KR1020157033190A KR20157033190A KR102268473B9 KR 102268473 B9 KR102268473 B9 KR 102268473B9 KR 1020157033190 A KR1020157033190 A KR 1020157033190A KR 20157033190 A KR20157033190 A KR 20157033190A KR 102268473 B9 KR102268473 B9 KR 102268473B9
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us7nrna
u7snrna
exon
targeted
associated virus
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KR1020157033190A
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KR20160003002A (ko
KR102268473B1 (ko
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케빈 플라니간
아델린 불린-차피올
니콜라스 웨인
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더 리서치 인스티튜트 앳 네이션와이드 칠드런스 하스피탈
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Priority to KR1020217018724A priority Critical patent/KR102413498B1/ko
Publication of KR20160003002A publication Critical patent/KR20160003002A/ko
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KR1020157033190A 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달 KR102268473B1 (ko)

Priority Applications (1)

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KR1020217018724A KR102413498B1 (ko) 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201361814256P 2013-04-20 2013-04-20
US61/814,256 2013-04-20
PCT/US2014/034702 WO2014172669A1 (en) 2013-04-20 2014-04-18 Recombinant adeno-associated virus delivery of exon 2-targeted u7snrna polynucleotide constructs

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KR1020217018724A Division KR102413498B1 (ko) 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달

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KR20160003002A KR20160003002A (ko) 2016-01-08
KR102268473B1 KR102268473B1 (ko) 2021-06-25
KR102268473B9 true KR102268473B9 (ko) 2023-03-31

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KR1020217018724A KR102413498B1 (ko) 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달
KR1020157033190A KR102268473B1 (ko) 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달
KR1020237016263A KR20230074604A (ko) 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달
KR1020227021096A KR20220090593A (ko) 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달

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KR1020227021096A KR20220090593A (ko) 2013-04-20 2014-04-18 엑손 2-표적 U7snRNA 폴리뉴클레오티드 작제물의 재조합형 아데노 부속 바이러스 전달

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EP (2) EP2986632B1 (ko)
JP (4) JP6461917B2 (ko)
KR (4) KR102413498B1 (ko)
CN (2) CN109652385A (ko)
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