CA2966620A1 - Aadc polynucleotides for the treatment of parkinson's disease - Google Patents
Aadc polynucleotides for the treatment of parkinson's disease Download PDFInfo
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- CA2966620A1 CA2966620A1 CA2966620A CA2966620A CA2966620A1 CA 2966620 A1 CA2966620 A1 CA 2966620A1 CA 2966620 A CA2966620 A CA 2966620A CA 2966620 A CA2966620 A CA 2966620A CA 2966620 A1 CA2966620 A1 CA 2966620A1
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Landscapes
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- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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- Micro-Organisms Or Cultivation Processes Thereof (AREA)
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Applications Claiming Priority (9)
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| US201462075298P | 2014-11-05 | 2014-11-05 | |
| US62/075,298 | 2014-11-05 | ||
| US201562155692P | 2015-05-01 | 2015-05-01 | |
| US62/155,692 | 2015-05-01 | ||
| US201562199578P | 2015-07-31 | 2015-07-31 | |
| US62/199,578 | 2015-07-31 | ||
| US201562243537P | 2015-10-19 | 2015-10-19 | |
| US62/243,537 | 2015-10-19 | ||
| PCT/US2015/059201 WO2016073693A2 (en) | 2014-11-05 | 2015-11-05 | Aadc polynucleotides for the treatment of parkinson's disease |
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| CA2966620A1 true CA2966620A1 (en) | 2016-05-12 |
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| CA2966620A Abandoned CA2966620A1 (en) | 2014-11-05 | 2015-11-05 | Aadc polynucleotides for the treatment of parkinson's disease |
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| RU2749882C2 (ru) | 2014-11-14 | 2021-06-18 | Вояджер Терапьютикс, Инк. | Модулирующие полинуклеотиды |
| EP3632923A1 (en) * | 2015-01-16 | 2020-04-08 | Voyager Therapeutics, Inc. | Central nervous system targeting polynucleotides |
| AU2016362477A1 (en) | 2015-12-02 | 2018-06-14 | Voyager Therapeutics, Inc. | Assays for the detection of AAV neutralizing antibodies |
| JP7220080B2 (ja) | 2016-05-18 | 2023-02-09 | ボイジャー セラピューティクス インコーポレイテッド | ハンチントン病治療組成物及び方法 |
| JP7066635B2 (ja) | 2016-05-18 | 2022-05-13 | ボイジャー セラピューティクス インコーポレイテッド | 調節性ポリヌクレオチド |
| US11298041B2 (en) | 2016-08-30 | 2022-04-12 | The Regents Of The University Of California | Methods for biomedical targeting and delivery and devices and systems for practicing the same |
| US11111271B2 (en) | 2016-09-28 | 2021-09-07 | Cohbar, Inc. | Therapeutic peptides |
| US11117930B2 (en) | 2017-02-23 | 2021-09-14 | Adrx, Inc. | Peptide inhibitors of transcription factor aggregation |
| AU2018234918B2 (en) * | 2017-03-17 | 2023-11-02 | Adverum Biotechnologies, Inc. | Compositions and methods for enhanced gene expression |
| WO2018191450A2 (en) | 2017-04-14 | 2018-10-18 | National Taiwan University Hospital | Gene therapy for aadc deficiency |
| WO2018204803A1 (en) * | 2017-05-05 | 2018-11-08 | Voyager Therapeutics, Inc. | Compositions and methods of treating huntington's disease |
| WO2018226992A1 (en) | 2017-06-07 | 2018-12-13 | Adrx, Inc. | Tau aggregation inhibitors |
| JOP20190269A1 (ar) * | 2017-06-15 | 2019-11-20 | Voyager Therapeutics Inc | بولي نوكليوتيدات aadc لعلاج مرض باركنسون |
| US11497576B2 (en) | 2017-07-17 | 2022-11-15 | Voyager Therapeutics, Inc. | Trajectory array guide system |
| CN112501208A (zh) * | 2017-10-03 | 2021-03-16 | 普利维尔治疗公司 | 用于溶酶体障碍的基因疗法 |
| JP2021521852A (ja) * | 2018-04-27 | 2021-08-30 | ボイジャー セラピューティクス インコーポレイテッドＶｏｙａｇｅｒ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． | Ａａｄｃウイルスベクターの効力を測定する方法 |
| AU2019268330A1 (en) | 2018-05-15 | 2020-11-26 | Voyager Therapeutics, Inc. | Compositions and methods for the treatment of Parkinson's disease |
| WO2019222441A1 (en) * | 2018-05-16 | 2019-11-21 | Voyager Therapeutics, Inc. | Aav serotypes for brain specific payload delivery |
| US12060567B2 (en) | 2018-06-13 | 2024-08-13 | Voyager Therapeutics, Inc. | Engineered untranslated regions (UTR) for AAV production |
| CN114908099B (zh) * | 2018-06-28 | 2024-07-02 | 北京锦篮基因科技有限公司 | 携带设计smn1基因表达框的重组腺相关病毒及应用 |
| MX2021000810A (es) | 2018-07-24 | 2021-04-28 | Voyager Therapeutics Inc | Sistemas y metodos para producir formulaciones de terapia genetica. |
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