AU2015346162B2 - Compositions and methods of treating amyotrophic lateral sclerosis (ALS) - Google Patents

Compositions and methods of treating amyotrophic lateral sclerosis (ALS) Download PDF

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AU2015346162B2
AU2015346162B2 AU2015346162A AU2015346162A AU2015346162B2 AU 2015346162 B2 AU2015346162 B2 AU 2015346162B2 AU 2015346162 A AU2015346162 A AU 2015346162A AU 2015346162 A AU2015346162 A AU 2015346162A AU 2015346162 B2 AU2015346162 B2 AU 2015346162B2
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sirna
aav
nucleotides
als
expression
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AU2015346162A1 (en
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Jochen DECKERT
Markus Hossbach
Jinzhao Hou
Mathieu E. NONNENMACHER
Dinah Wen-Yee Sah
Pengcheng ZHOU
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Voyager Therapeutics Inc
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Voyager Therapeutics Inc
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    • C12Y115/00—Oxidoreductases acting on superoxide as acceptor (1.15)
    • C12Y115/01—Oxidoreductases acting on superoxide as acceptor (1.15) with NAD or NADP as acceptor (1.15.1)
    • C12Y115/01001—Superoxide dismutase (1.15.1.1)
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    • C12N2310/00—Structure or type of the nucleic acid
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    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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    • C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector

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AU2015346162A 2014-11-14 2015-11-13 Compositions and methods of treating amyotrophic lateral sclerosis (ALS) Active AU2015346162B2 (en)

Priority Applications (1)

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AU2022202979A AU2022202979A1 (en) 2014-11-14 2022-05-04 Compositions and methods of treating amyotrophic lateral sclerosis (ALS)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201462079588P 2014-11-14 2014-11-14
US62/079,588 2014-11-14
US201562211992P 2015-08-31 2015-08-31
US62/211,992 2015-08-31
US201562234466P 2015-09-29 2015-09-29
US62/234,466 2015-09-29
PCT/US2015/060562 WO2016077687A1 (en) 2014-11-14 2015-11-13 Compositions and methods of treating amyotrophic lateral sclerosis (als)

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AU2022202979A Division AU2022202979A1 (en) 2014-11-14 2022-05-04 Compositions and methods of treating amyotrophic lateral sclerosis (ALS)

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AU2015346162B2 true AU2015346162B2 (en) 2022-02-10

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US (5) US10597660B2 (https=)
EP (1) EP3218484A4 (https=)
JP (4) JP2017535266A (https=)
KR (2) KR20230169197A (https=)
CN (2) CN114717264A (https=)
AU (2) AU2015346162B2 (https=)
CA (2) CA2967367C (https=)
HK (1) HK1244299A1 (https=)
IL (3) IL292999A (https=)
MX (2) MX2017006216A (https=)
RU (2) RU2020108189A (https=)
SG (1) SG11201703281RA (https=)
WO (1) WO2016077687A1 (https=)
ZA (1) ZA201702991B (https=)

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