HK1244299A1 - 治療肌萎縮側索硬化(als)的組合物和方法 - Google Patents

治療肌萎縮側索硬化(als)的組合物和方法

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Publication number
HK1244299A1
HK1244299A1 HK18103755.9A HK18103755A HK1244299A1 HK 1244299 A1 HK1244299 A1 HK 1244299A1 HK 18103755 A HK18103755 A HK 18103755A HK 1244299 A1 HK1244299 A1 HK 1244299A1
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HK
Hong Kong
Prior art keywords
als
compositions
methods
lateral sclerosis
amyotrophic lateral
Prior art date
Application number
HK18103755.9A
Other languages
English (en)
Inventor
Dinah Wen-Yee Sah
Jinzhao Hou
Mathieu E Nonnenmacher
Pengcheng Zhou
Markus Hossbach
Jochen Deckert
Original Assignee
Voyager Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Voyager Therapeutics Inc filed Critical Voyager Therapeutics Inc
Publication of HK1244299A1 publication Critical patent/HK1244299A1/zh

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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • C12N15/1137—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing against enzymes
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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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    • C12Y115/00—Oxidoreductases acting on superoxide as acceptor (1.15)
    • C12Y115/01—Oxidoreductases acting on superoxide as acceptor (1.15) with NAD or NADP as acceptor (1.15.1)
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector

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  • Pain & Pain Management (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
HK18103755.9A 2014-11-14 2018-03-19 治療肌萎縮側索硬化(als)的組合物和方法 HK1244299A1 (zh)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201462079588P 2014-11-14 2014-11-14
US201562211992P 2015-08-31 2015-08-31
US201562234466P 2015-09-29 2015-09-29
PCT/US2015/060562 WO2016077687A1 (en) 2014-11-14 2015-11-13 Compositions and methods of treating amyotrophic lateral sclerosis (als)

Publications (1)

Publication Number Publication Date
HK1244299A1 true HK1244299A1 (zh) 2018-08-03

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HK18103755.9A HK1244299A1 (zh) 2014-11-14 2018-03-19 治療肌萎縮側索硬化(als)的組合物和方法

Country Status (15)

Country Link
US (4) US10597660B2 (zh)
EP (1) EP3218484A4 (zh)
JP (4) JP2017535266A (zh)
KR (2) KR102599909B1 (zh)
CN (2) CN114717264A (zh)
AU (2) AU2015346162B2 (zh)
BR (1) BR112017010087A2 (zh)
CA (2) CA2967367C (zh)
HK (1) HK1244299A1 (zh)
IL (3) IL292999A (zh)
MX (2) MX2017006216A (zh)
RU (2) RU2716422C2 (zh)
SG (1) SG11201703281RA (zh)
WO (1) WO2016077687A1 (zh)
ZA (1) ZA201702991B (zh)

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