CN114717264A - 治疗肌萎缩性侧索硬化(als)的组合物和方法 - Google Patents

治疗肌萎缩性侧索硬化(als)的组合物和方法 Download PDF

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CN114717264A
CN114717264A CN202210354987.1A CN202210354987A CN114717264A CN 114717264 A CN114717264 A CN 114717264A CN 202210354987 A CN202210354987 A CN 202210354987A CN 114717264 A CN114717264 A CN 114717264A
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sod1
nucleotides
sirna
aav
vector
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Chinese (zh)
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D·W-Y·沙
侯金兆
M·E·农嫩马赫
周鹏程
M·霍斯巴赫
J·德克特
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Voyager Therapeutics Inc
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Voyager Therapeutics Inc
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CN202210354987.1A 2014-11-14 2015-11-13 治疗肌萎缩性侧索硬化(als)的组合物和方法 Pending CN114717264A (zh)

Applications Claiming Priority (8)

Application Number Priority Date Filing Date Title
US201462079588P 2014-11-14 2014-11-14
US62/079,588 2014-11-14
US201562211992P 2015-08-31 2015-08-31
US62/211,992 2015-08-31
US201562234466P 2015-09-29 2015-09-29
US62/234,466 2015-09-29
PCT/US2015/060562 WO2016077687A1 (en) 2014-11-14 2015-11-13 Compositions and methods of treating amyotrophic lateral sclerosis (als)
CN201580072992.1A CN107109407A (zh) 2014-11-14 2015-11-13 治疗肌萎缩性侧索硬化(als)的组合物和方法

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