JP5054975B2 - アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 - Google Patents

アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 Download PDF

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JP5054975B2
JP5054975B2 JP2006533879A JP2006533879A JP5054975B2 JP 5054975 B2 JP5054975 B2 JP 5054975B2 JP 2006533879 A JP2006533879 A JP 2006533879A JP 2006533879 A JP2006533879 A JP 2006533879A JP 5054975 B2 JP5054975 B2 JP 5054975B2
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aav
nos
sequences
syngeneic
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JP2007507223A5 (cg-RX-API-DMAC7.html
JP2007507223A (ja
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ウイルソン，ジエイムズ・エム
ガオ，グアングピング
アルビラ，モーリシオ・アール
バンデンバーグ，リユク・エイチ
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • C12N2750/14011—Parvoviridae
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    • C12N2750/14011—Parvoviridae
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    • C12N2830/80—Vector systems having a special element relevant for transcription from vertebrates
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JP2006533879A 2003-09-30 2004-09-30 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途 Expired - Lifetime JP5054975B2 (ja)

Applications Claiming Priority (5)

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US50822603P 2003-09-30 2003-09-30
US60/508,226 2003-09-30
US56654604P 2004-04-29 2004-04-29
US60/566,546 2004-04-29
PCT/US2004/028817 WO2005033321A2 (en) 2003-09-30 2004-09-30 Adeno-associated virus (aav) clades, sequences, vectors containing same, and uses therefor

Related Child Applications (2)

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JP2010272649A Division JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Division JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途

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JP2007507223A JP2007507223A (ja) 2007-03-29
JP2007507223A5 JP2007507223A5 (cg-RX-API-DMAC7.html) 2007-11-22
JP5054975B2 true JP5054975B2 (ja) 2012-10-24

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JP2006533879A Expired - Lifetime JP5054975B2 (ja) 2003-09-30 2004-09-30 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2010272649A Expired - Lifetime JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Expired - Lifetime JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2013191907A Expired - Lifetime JP5911069B2 (ja) 2003-09-30 2013-09-17 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2015114170A Expired - Lifetime JP6335141B2 (ja) 2003-09-30 2015-06-04 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2016211386A Expired - Lifetime JP6516713B2 (ja) 2003-09-30 2016-10-28 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2018067535A Expired - Lifetime JP6673963B2 (ja) 2003-09-30 2018-03-30 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2019221986A Pending JP2020054373A (ja) 2003-09-30 2019-12-09 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2022161483A Pending JP2022173573A (ja) 2003-09-30 2022-10-06 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途

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JP2010272649A Expired - Lifetime JP5797397B2 (ja) 2003-09-30 2010-12-07 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2012053003A Expired - Lifetime JP5431516B2 (ja) 2003-09-30 2012-03-09 アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
JP2013191907A Expired - Lifetime JP5911069B2 (ja) 2003-09-30 2013-09-17 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2015114170A Expired - Lifetime JP6335141B2 (ja) 2003-09-30 2015-06-04 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2016211386A Expired - Lifetime JP6516713B2 (ja) 2003-09-30 2016-10-28 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2018067535A Expired - Lifetime JP6673963B2 (ja) 2003-09-30 2018-03-30 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2019221986A Pending JP2020054373A (ja) 2003-09-30 2019-12-09 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途
JP2022161483A Pending JP2022173573A (ja) 2003-09-30 2022-10-06 アデノ随伴ウイルス（ａａｖ）の同源系統群（クレイド）、配列、それらを含有するベクターおよびそれらの用途

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US (13) US7906111B2 (cg-RX-API-DMAC7.html)
EP (7) EP2292780B1 (cg-RX-API-DMAC7.html)
JP (9) JP5054975B2 (cg-RX-API-DMAC7.html)
CN (4) CN102199626B (cg-RX-API-DMAC7.html)
AU (2) AU2004278684B2 (cg-RX-API-DMAC7.html)
BE (1) BE2021C533I2 (cg-RX-API-DMAC7.html)
CA (3) CA3072423A1 (cg-RX-API-DMAC7.html)
CY (3) CY1119833T1 (cg-RX-API-DMAC7.html)
DK (4) DK2292780T3 (cg-RX-API-DMAC7.html)
ES (5) ES2616016T3 (cg-RX-API-DMAC7.html)
FR (1) FR21C1037I1 (cg-RX-API-DMAC7.html)
HU (4) HUE035567T2 (cg-RX-API-DMAC7.html)
NZ (1) NZ545628A (cg-RX-API-DMAC7.html)
PL (2) PL2292780T3 (cg-RX-API-DMAC7.html)
PT (2) PT3211085T (cg-RX-API-DMAC7.html)
SI (2) SI2292780T1 (cg-RX-API-DMAC7.html)
WO (1) WO2005033321A2 (cg-RX-API-DMAC7.html)

Cited By (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2012175974A (ja) * 2003-09-30 2012-09-13 Trustees Of The Univ Of Pennsylvania アデノ随伴ウイルス（ａａｖ）の同源系統群、配列、それらを含有するベクターおよびそれらの用途
WO2020101042A1 (en) 2018-11-16 2020-05-22 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting utrophin gene
WO2020241903A1 (en) 2019-05-28 2020-12-03 Astellas Pharma Inc. Method for treating muscular dystrophy by targeting dmpk gene

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MX346493B (es) 2001-11-13 2017-03-21 Univ Pennsylvania Un metodo para detectar y/o identificar secuencias del virus adeno-asociado y aislamiento de secuencias novedosas identificadas de ese modo.
JP4810062B2 (ja) 2001-12-17 2011-11-09 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア アデノ随伴ウイルス（ａａｖ）血清型８の配列
US9441244B2 (en) 2003-06-30 2016-09-13 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
US9233131B2 (en) 2003-06-30 2016-01-12 The Regents Of The University Of California Mutant adeno-associated virus virions and methods of use thereof
US8394386B2 (en) 2004-04-28 2013-03-12 The Trustees Of The University Of Pennsylvania Sequential delivery of immunogenic molecules via adenovirus and adeno-associated virus-mediated administrations
EP1742657B1 (en) 2004-04-28 2013-11-06 The Trustees of The University of Pennsylvania Immunization regimen with e4-deleted adenovirus prime and e1-deleted adenovirus boost
EP2383346B1 (en) * 2005-04-07 2014-10-08 The Trustees of the University of Pennsylvania Modified AAVrh.64 capsids, compositions containing same and uses thereof
US7588772B2 (en) 2006-03-30 2009-09-15 Board Of Trustees Of The Leland Stamford Junior University AAV capsid library and AAV capsid proteins
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