MX2018014154A - Polinucleotidos moduladores. - Google Patents

Polinucleotidos moduladores.

Info

Publication number
MX2018014154A
MX2018014154A MX2018014154A MX2018014154A MX2018014154A MX 2018014154 A MX2018014154 A MX 2018014154A MX 2018014154 A MX2018014154 A MX 2018014154A MX 2018014154 A MX2018014154 A MX 2018014154A MX 2018014154 A MX2018014154 A MX 2018014154A
Authority
MX
Mexico
Prior art keywords
modulatory polynucleotides
polynucleotides
modulatory
compositions
manufacture
Prior art date
Application number
MX2018014154A
Other languages
English (en)
Spanish (es)
Inventor
Wen-Yee Sah Dinah
Hou Jinzhao
Nonnenmacher Mathieu
Original Assignee
Voyager Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Voyager Therapeutics Inc filed Critical Voyager Therapeutics Inc
Publication of MX2018014154A publication Critical patent/MX2018014154A/es

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    • C12N15/09—Recombinant DNA-technology
    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • A—HUMAN NECESSITIES
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    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
    • A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
    • A—HUMAN NECESSITIES
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    • C12N15/09—Recombinant DNA-technology
    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
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    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
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    • C12N2310/53—Physical structure partially self-complementary or closed
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    • C12N2320/00—Applications; Uses
    • C12N2320/50—Methods for regulating/modulating their activity
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    • C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14121—Viruses as such, e.g. new isolates, mutants or their genomic sequences
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
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    • C12N2830/00—Vector systems having a special element relevant for transcription
    • C12N2830/50—Vector systems having a special element relevant for transcription regulating RNA stability, not being an intron, e.g. poly A signal

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  • Animal Behavior & Ethology (AREA)
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  • Immunology (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
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MX2018014154A 2016-05-18 2017-05-18 Polinucleotidos moduladores. MX2018014154A (es)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662338137P 2016-05-18 2016-05-18
US201762485050P 2017-04-13 2017-04-13
PCT/US2017/033268 WO2017201248A1 (en) 2016-05-18 2017-05-18 Modulatory polynucleotides

Publications (1)

Publication Number Publication Date
MX2018014154A true MX2018014154A (es) 2019-05-06

Family

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Application Number Title Priority Date Filing Date
MX2018014154A MX2018014154A (es) 2016-05-18 2017-05-18 Polinucleotidos moduladores.
MX2023010042A MX2023010042A (es) 2016-05-18 2018-11-16 Polinucleotidos moduladores.

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Application Number Title Priority Date Filing Date
MX2023010042A MX2023010042A (es) 2016-05-18 2018-11-16 Polinucleotidos moduladores.

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US (3) US10584337B2 (enExample)
EP (1) EP3458588B1 (enExample)
JP (3) JP7066635B2 (enExample)
KR (3) KR102392236B1 (enExample)
CN (2) CN117904112A (enExample)
AU (2) AU2017267665C1 (enExample)
CA (2) CA3024448C (enExample)
IL (2) IL302748B1 (enExample)
MX (2) MX2018014154A (enExample)
RU (1) RU2758488C2 (enExample)
SG (1) SG11201809699XA (enExample)
WO (1) WO2017201248A1 (enExample)
ZA (1) ZA201807401B (enExample)

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US20190169616A1 (en) 2019-06-06
RU2758488C2 (ru) 2021-10-28
MX2023010042A (es) 2023-09-05
ZA201807401B (en) 2020-12-23
BR112018073384A2 (pt) 2019-03-06
AU2017267665A1 (en) 2018-12-06
CA3252099A1 (en) 2025-06-05
CN117904112A (zh) 2024-04-19
JP7374254B2 (ja) 2023-11-06
KR20220054727A (ko) 2022-05-03
CN110214187B (zh) 2024-01-30

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