JP2021502060A5 - - Google Patents

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JP2021502060A5
JP2021502060A5 JP2020521439A JP2020521439A JP2021502060A5 JP 2021502060 A5 JP2021502060 A5 JP 2021502060A5 JP 2020521439 A JP2020521439 A JP 2020521439A JP 2020521439 A JP2020521439 A JP 2020521439A JP 2021502060 A5 JP2021502060 A5 JP 2021502060A5
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seq
nucleotide sequence
sequence
regulatory polynucleotide
strand sequence
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JP2020521439A
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JP2021502060A (ja
JP7502991B2 (ja
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Priority claimed from PCT/US2018/055999 external-priority patent/WO2019079240A1/en
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Priority to JP2024056219A priority Critical patent/JP2024095717A/ja
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JP2020521439A 2017-10-16 2018-10-16 筋萎縮性側索硬化症(als)の治療 Active JP7502991B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024056219A JP2024095717A (ja) 2017-10-16 2024-03-29 筋萎縮性側索硬化症(als)の治療

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US201762572702P 2017-10-16 2017-10-16
US62/572,702 2017-10-16
PCT/US2018/055999 WO2019079240A1 (en) 2017-10-16 2018-10-16 TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

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JP2024056219A Division JP2024095717A (ja) 2017-10-16 2024-03-29 筋萎縮性側索硬化症(als)の治療

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JP2021502060A JP2021502060A (ja) 2021-01-28
JP2021502060A5 true JP2021502060A5 (enExample) 2021-11-25
JP7502991B2 JP7502991B2 (ja) 2024-06-19

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JP2020521439A Active JP7502991B2 (ja) 2017-10-16 2018-10-16 筋萎縮性側索硬化症(als)の治療
JP2024056219A Pending JP2024095717A (ja) 2017-10-16 2024-03-29 筋萎縮性側索硬化症(als)の治療

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US (3) US11434502B2 (enExample)
EP (2) EP3697905A1 (enExample)
JP (2) JP7502991B2 (enExample)
CN (2) CN111479924B (enExample)
AU (1) AU2018352236B2 (enExample)
CA (1) CA3077426A1 (enExample)
TW (2) TWI804518B (enExample)
WO (1) WO2019079240A1 (enExample)

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MA54383A (fr) 2018-12-06 2021-10-13 Biogen Ma Inc Protéine neurofilamenteuse pour guider une intervention thérapeutique dans la sclérose laterale amyotrophique
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CN120202298A (zh) * 2023-08-29 2025-06-24 石药集团中奇制药技术(石家庄)有限公司 一种抑制sod1基因表达的dsRNA分子及其应用

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