CN111479924B - 肌萎缩性侧索硬化症(als)的治疗 - Google Patents

肌萎缩性侧索硬化症(als)的治疗 Download PDF

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CN111479924B
CN111479924B CN201880081098.4A CN201880081098A CN111479924B CN 111479924 B CN111479924 B CN 111479924B CN 201880081098 A CN201880081098 A CN 201880081098A CN 111479924 B CN111479924 B CN 111479924B
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aav
sequence
promoter
nucleotides
limiting example
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CN111479924A (zh
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D·W-Y·沙
陈庆敏
H·帕泽克
侯金兆
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Voyager Therapeutics Inc
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University of Missouri St Louis
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CN201880081098.4A 2017-10-16 2018-10-16 肌萎缩性侧索硬化症(als)的治疗 Active CN111479924B (zh)

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US201762572702P 2017-10-16 2017-10-16
US62/572,702 2017-10-16
PCT/US2018/055999 WO2019079240A1 (en) 2017-10-16 2018-10-16 TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

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