JP2024160045A5 - - Google Patents

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Publication number
JP2024160045A5
JP2024160045A5 JP2024092815A JP2024092815A JP2024160045A5 JP 2024160045 A5 JP2024160045 A5 JP 2024160045A5 JP 2024092815 A JP2024092815 A JP 2024092815A JP 2024092815 A JP2024092815 A JP 2024092815A JP 2024160045 A5 JP2024160045 A5 JP 2024160045A5
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JP
Japan
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pharmaceutical composition
transferrin receptor
covalently linked
exon skipping
receptor antibody
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JP2024092815A
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English (en)
Japanese (ja)
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JP2024160045A (ja
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Priority claimed from PCT/US2019/044949 external-priority patent/WO2020028832A1/en
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Publication of JP2024160045A publication Critical patent/JP2024160045A/ja
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JP2024092815A 2018-08-02 2024-06-07 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用 Pending JP2024160045A (ja)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201862714031P 2018-08-02 2018-08-02
US62/714,031 2018-08-02
US201962855766P 2019-05-31 2019-05-31
US62/855,766 2019-05-31
PCT/US2019/044949 WO2020028832A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating dystrophinopathies
JP2021529254A JP7611825B2 (ja) 2018-08-02 2019-08-02 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用

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JP2021529254A Division JP7611825B2 (ja) 2018-08-02 2019-08-02 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用

Publications (2)

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JP2024160045A JP2024160045A (ja) 2024-11-11
JP2024160045A5 true JP2024160045A5 (enExample) 2025-05-22

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JP2021529254A Active JP7611825B2 (ja) 2018-08-02 2019-08-02 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用
JP2024092815A Pending JP2024160045A (ja) 2018-08-02 2024-06-07 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用

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JP2021529254A Active JP7611825B2 (ja) 2018-08-02 2019-08-02 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用

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US (9) US20210308273A1 (enExample)
EP (1) EP3829595A4 (enExample)
JP (2) JP7611825B2 (enExample)
KR (1) KR20210081322A (enExample)
CN (1) CN112955153A (enExample)
AU (1) AU2019312692A1 (enExample)
CA (1) CA3108282A1 (enExample)
IL (1) IL280527A (enExample)
MX (1) MX2021001281A (enExample)
SG (1) SG11202100934PA (enExample)
WO (1) WO2020028832A1 (enExample)

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