JP2025067909A5 - - Google Patents

Info

Publication number
JP2025067909A5
JP2025067909A5 JP2025004577A JP2025004577A JP2025067909A5 JP 2025067909 A5 JP2025067909 A5 JP 2025067909A5 JP 2025004577 A JP2025004577 A JP 2025004577A JP 2025004577 A JP2025004577 A JP 2025004577A JP 2025067909 A5 JP2025067909 A5 JP 2025067909A5
Authority
JP
Japan
Prior art keywords
oligonucleotide
conjugate
seq
nucleotides
transferrin receptor
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2025004577A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025067909A (ja
Filing date
Publication date
Priority claimed from PCT/US2019/044987 external-priority patent/WO2020028861A1/en
Application filed filed Critical
Publication of JP2025067909A publication Critical patent/JP2025067909A/ja
Publication of JP2025067909A5 publication Critical patent/JP2025067909A5/ja
Pending legal-status Critical Current

Links

JP2025004577A 2018-08-02 2025-01-14 筋強直症ジストロフィーを処置するための筋標的化複合体およびそれらの使用 Pending JP2025067909A (ja)

Applications Claiming Priority (12)

Application Number Priority Date Filing Date Title
US201862713914P 2018-08-02 2018-08-02
US62/713,914 2018-08-02
US201862779161P 2018-12-13 2018-12-13
US62/779,161 2018-12-13
US201962855761P 2019-05-31 2019-05-31
US62/855,761 2019-05-31
US201962858888P 2019-06-07 2019-06-07
US62/858,888 2019-06-07
US201962859672P 2019-06-10 2019-06-10
US62/859,672 2019-06-10
PCT/US2019/044987 WO2020028861A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating myotonic dystrophy
JP2021529260A JP7705793B2 (ja) 2018-08-02 2019-08-02 筋強直症ジストロフィーを処置するための筋標的化複合体およびそれらの使用

Related Parent Applications (1)

Application Number Title Priority Date Filing Date
JP2021529260A Division JP7705793B2 (ja) 2018-08-02 2019-08-02 筋強直症ジストロフィーを処置するための筋標的化複合体およびそれらの使用

Publications (2)

Publication Number Publication Date
JP2025067909A JP2025067909A (ja) 2025-04-24
JP2025067909A5 true JP2025067909A5 (enExample) 2025-10-17

Family

ID=69230803

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021529260A Active JP7705793B2 (ja) 2018-08-02 2019-08-02 筋強直症ジストロフィーを処置するための筋標的化複合体およびそれらの使用
JP2025004577A Pending JP2025067909A (ja) 2018-08-02 2025-01-14 筋強直症ジストロフィーを処置するための筋標的化複合体およびそれらの使用

Family Applications Before (1)

Application Number Title Priority Date Filing Date
JP2021529260A Active JP7705793B2 (ja) 2018-08-02 2019-08-02 筋強直症ジストロフィーを処置するための筋標的化複合体およびそれらの使用

Country Status (11)

Country Link
US (1) US20210308272A1 (enExample)
EP (1) EP3829596A4 (enExample)
JP (2) JP7705793B2 (enExample)
KR (1) KR20210081323A (enExample)
CN (1) CN112955154A (enExample)
AU (2) AU2019314538B2 (enExample)
CA (1) CA3108287A1 (enExample)
IL (2) IL321905A (enExample)
MX (1) MX2021001283A (enExample)
SG (1) SG11202100925VA (enExample)
WO (1) WO2020028861A1 (enExample)

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WO2019113393A1 (en) 2017-12-06 2019-06-13 Avidity Biosciences Llc Compositions and methods of treating muscle atrophy and myotonic dystrophy
SG11202100934PA (en) 2018-08-02 2021-02-25 Dyne Therapeutics Inc Muscle targeting complexes and uses thereof for treating dystrophinopathies
US12097263B2 (en) 2018-08-02 2024-09-24 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
US12018087B2 (en) 2018-08-02 2024-06-25 Dyne Therapeutics, Inc. Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject
KR20210081324A (ko) 2018-08-02 2021-07-01 다인 세라퓨틱스, 인크. 근육 표적화 복합체 및 안면견갑상완 근육 이영양증을 치료하기 위한 그의 용도
US11911484B2 (en) 2018-08-02 2024-02-27 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
US11168141B2 (en) 2018-08-02 2021-11-09 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
US12370264B1 (en) 2018-08-02 2025-07-29 Dyne Therapeutics, Inc. Complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and method of delivering oligonucleotide to a subject
WO2021142217A1 (en) * 2020-01-10 2021-07-15 Dyne Thereapeutics, Inc. Muscle targeting complexes and uses thereof for modulation of milck1
WO2021195469A1 (en) * 2020-03-27 2021-09-30 Avidity Biosciences, Inc. Compositions and methods of treating muscle dystrophy
IL299666A (en) * 2020-07-23 2023-03-01 Dyne Therapeutics Inc Muscle targeting complexes and their uses for the treatment of FACIOSCAPULOHUMERAL muscular dystrophy
KR20230042713A (ko) * 2020-07-23 2023-03-29 다인 세라퓨틱스, 인크. 근육 표적화 복합체 및 근긴장성 이영양증을 치료하기 위한 그의 용도
UY39417A (es) * 2020-09-11 2022-03-31 Arrowhead Pharmaceuticals Inc Agentes de arni para inhibir la expresión de dux4, composiciones de dichos agentes, y métodos de uso
KR20230117182A (ko) * 2020-12-04 2023-08-07 다인 세라퓨틱스, 인크. 항체-올리고뉴클레오티드 복합체 및 그의 용도
CA3202832A1 (en) * 2020-12-31 2022-07-07 Romesh R. Subramanian Muscle targeting complexes and uses thereof for treating myotonic dystrophy
US11648318B2 (en) 2021-07-09 2023-05-16 Dyne Therapeutics, Inc. Anti-transferrin receptor (TFR) antibody and uses thereof
US11633498B2 (en) 2021-07-09 2023-04-25 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
US11771776B2 (en) 2021-07-09 2023-10-03 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
AU2022309028A1 (en) 2021-07-09 2024-01-25 Dyne Therapeutics, Inc. Muscle targeting complexes and formulations for treating dystrophinopathies
US11969475B2 (en) 2021-07-09 2024-04-30 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
US11638761B2 (en) 2021-07-09 2023-05-02 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating Facioscapulohumeral muscular dystrophy
EP4124345A1 (en) * 2021-07-30 2023-02-01 4basebio UK Ltd Nanoparticles for muscle delivery
WO2023006985A1 (en) * 2021-07-30 2023-02-02 4Basebio Uk Ltd Nanoparticles and peptides for the delivery of cargos to muscle cells
CR20240139A (es) 2021-09-01 2024-06-14 Biogen Ma Inc Anticuerpos del receptor antitransferrina y usos de los mismos
US11833221B2 (en) 2021-09-01 2023-12-05 Ionis Pharmaceuticals, Inc. Oligomeric compounds for reducing DMPK expression
IL316143A (en) 2022-04-15 2024-12-01 Dyne Therapeutics Inc Muscle targeting complexes and formulations for the treatment of myotonic dystrophy

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2009005793A2 (en) 2007-06-29 2009-01-08 Avi Biopharma, Inc. Tissue specific peptide conjugates and methods
CN103167883B (zh) 2010-07-19 2016-08-03 F·C·贝内特 肌强直性营养障碍蛋白激酶(dmpk)表达的调节
WO2013138662A1 (en) * 2012-03-16 2013-09-19 4S3 Bioscience, Inc. Antisense conjugates for decreasing expression of dmpk
US10111962B2 (en) 2012-09-25 2018-10-30 Genzyme Corporation Peptide-linked morpholino antisense oligonucleotides for treatment of myotonic dystrophy
SMT202300208T1 (it) * 2012-10-23 2023-09-06 Synaffix Bv Anticorpo modificato, coniugato di anticorpo e processo per la preparazione degli stessi
TW201536329A (zh) * 2013-08-09 2015-10-01 Isis Pharmaceuticals Inc 用於調節失養性肌強直蛋白質激酶(dmpk)表現之化合物及方法
US20190240346A1 (en) 2016-06-20 2019-08-08 Genahead Bio, Inc. Antibody-drug conjugate
MX2019008199A (es) 2017-01-06 2019-11-25 Avidity Biosciences Llc Composiciones de acido nucleico polipeptido y metodos de induccion de la omision de exon.

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