JP7611825B2 - ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用 - Google Patents

ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用 Download PDF

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JP7611825B2
JP7611825B2 JP2021529254A JP2021529254A JP7611825B2 JP 7611825 B2 JP7611825 B2 JP 7611825B2 JP 2021529254 A JP2021529254 A JP 2021529254A JP 2021529254 A JP2021529254 A JP 2021529254A JP 7611825 B2 JP7611825 B2 JP 7611825B2
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antibody
transferrin receptor
muscle
oligonucleotide
exon
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JPWO2020028832A5 (enExample
JP2021532831A (ja
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スブラマニアン，ロメシ，アール．
カタナニ，モハメド，ティー．
ウィーデン，ティモシー
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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JP2021529254A 2018-08-02 2019-08-02 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用 Active JP7611825B2 (ja)

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US201862714031P 2018-08-02 2018-08-02
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PCT/US2019/044949 WO2020028832A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating dystrophinopathies

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