EA201890908A1 - Композиции и способы для лечения мышечной дистрофии дюшенна и сходных нарушений - Google Patents

Композиции и способы для лечения мышечной дистрофии дюшенна и сходных нарушений

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Publication number
EA201890908A1
EA201890908A1 EA201890908A EA201890908A EA201890908A1 EA 201890908 A1 EA201890908 A1 EA 201890908A1 EA 201890908 A EA201890908 A EA 201890908A EA 201890908 A EA201890908 A EA 201890908A EA 201890908 A1 EA201890908 A1 EA 201890908A1
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Prior art keywords
treatment
muscular dystrophy
compositions
methods
young
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EA201890908A
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English (en)
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Джордж Диксон
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Сарепта Терапьютикс, Инк.
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Publication of EA201890908A1 publication Critical patent/EA201890908A1/ru

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Abstract

Изобретение относится к композициям и способам для лечения мышечной дистрофии Дюшенна и сходных нарушений. Описаны модифицированные антисмысловые олигомеры для лечения мышечной дистрофии Дюшенна и сходных нарушений.
EA201890908A 2015-10-09 2016-10-07 Композиции и способы для лечения мышечной дистрофии дюшенна и сходных нарушений EA201890908A1 (ru)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201562239812P 2015-10-09 2015-10-09
PCT/US2016/056093 WO2017062835A2 (en) 2015-10-09 2016-10-07 Compositions and methods for treating duchenne muscular dystrophy and related disorders

Publications (1)

Publication Number Publication Date
EA201890908A1 true EA201890908A1 (ru) 2018-10-31

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EA201890908A EA201890908A1 (ru) 2015-10-09 2016-10-07 Композиции и способы для лечения мышечной дистрофии дюшенна и сходных нарушений

Country Status (9)

Country Link
US (1) US20190177723A1 (ru)
EP (2) EP3858993A1 (ru)
JP (2) JP2018530560A (ru)
CN (1) CN108699555A (ru)
BR (1) BR112018007066A2 (ru)
EA (1) EA201890908A1 (ru)
IL (2) IL258069A (ru)
MA (1) MA45819A (ru)
WO (1) WO2017062835A2 (ru)

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