JP2021532831A5 - - Google Patents

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Publication number
JP2021532831A5
JP2021532831A5 JP2021529254A JP2021529254A JP2021532831A5 JP 2021532831 A5 JP2021532831 A5 JP 2021532831A5 JP 2021529254 A JP2021529254 A JP 2021529254A JP 2021529254 A JP2021529254 A JP 2021529254A JP 2021532831 A5 JP2021532831 A5 JP 2021532831A5
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JP
Japan
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exon
oligonucleotide
transferrin receptor
dmd
complex
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JP2021529254A
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Japanese (ja)
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JP2021532831A (ja
JP7611825B2 (ja
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Priority claimed from PCT/US2019/044949 external-priority patent/WO2020028832A1/en
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Priority to JP2024092815A priority Critical patent/JP2024160045A/ja
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Publication of JP7611825B2 publication Critical patent/JP7611825B2/ja
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JP2021529254A 2018-08-02 2019-08-02 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用 Active JP7611825B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024092815A JP2024160045A (ja) 2018-08-02 2024-06-07 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862714031P 2018-08-02 2018-08-02
US62/714,031 2018-08-02
US201962855766P 2019-05-31 2019-05-31
US62/855,766 2019-05-31
PCT/US2019/044949 WO2020028832A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating dystrophinopathies

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JP2024092815A Division JP2024160045A (ja) 2018-08-02 2024-06-07 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用

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JP2021532831A JP2021532831A (ja) 2021-12-02
JP2021532831A5 true JP2021532831A5 (enExample) 2022-08-09
JP7611825B2 JP7611825B2 (ja) 2025-01-10

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JP2021529254A Active JP7611825B2 (ja) 2018-08-02 2019-08-02 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用
JP2024092815A Pending JP2024160045A (ja) 2018-08-02 2024-06-07 ジストロフィン異常症を処置するための筋標的化複合体およびそれらの使用

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US (9) US20210308273A1 (enExample)
EP (1) EP3829595A4 (enExample)
JP (2) JP7611825B2 (enExample)
KR (1) KR20210081322A (enExample)
CN (1) CN112955153A (enExample)
AU (1) AU2019312692A1 (enExample)
CA (1) CA3108282A1 (enExample)
IL (1) IL280527A (enExample)
MX (1) MX2021001281A (enExample)
SG (1) SG11202100934PA (enExample)
WO (1) WO2020028832A1 (enExample)

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