JP2020527333A - パーキンソン病を治療するためのａａｄｃポリヌクレオチド - Google Patents

パーキンソン病を治療するためのａａｄｃポリヌクレオチド Download PDF

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JP2020527333A
JP2020527333A JP2019569267A JP2019569267A JP2020527333A JP 2020527333 A JP2020527333 A JP 2020527333A JP 2019569267 A JP2019569267 A JP 2019569267A JP 2019569267 A JP2019569267 A JP 2019569267A JP 2020527333 A JP2020527333 A JP 2020527333A
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aav
seq
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aavhu
aavrh
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JP2020527333A5 (enExample
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シェール、マリア
ラビナ、バーナード
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Voyager Therapeutics Inc
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Voyager Therapeutics Inc
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    • A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
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  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
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JP2019569267A 2017-06-15 2018-06-14 パーキンソン病を治療するためのａａｄｃポリヌクレオチド Pending JP2020527333A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201762520084P 2017-06-15 2017-06-15
US62/520,084 2017-06-15
US201762554155P 2017-09-05 2017-09-05
US62/554,155 2017-09-05
PCT/US2018/037437 WO2018232055A1 (en) 2017-06-15 2018-06-14 Aadc polynucleotides for the treatment of parkinson's disease

Publications (2)

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JP2020527333A true JP2020527333A (ja) 2020-09-10
JP2020527333A5 JP2020527333A5 (enExample) 2021-07-26

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JP2019569267A Pending JP2020527333A (ja) 2017-06-15 2018-06-14 パーキンソン病を治療するためのａａｄｃポリヌクレオチド

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US (2) US20190060425A1 (enExample)
EP (1) EP3638315A4 (enExample)
JP (1) JP2020527333A (enExample)
KR (1) KR20200018455A (enExample)
CN (1) CN111107879A (enExample)
AU (2) AU2018284960B2 (enExample)
BR (1) BR112019025122A2 (enExample)
CA (1) CA3065471A1 (enExample)
CL (1) CL2019003636A1 (enExample)
CO (1) CO2019013707A2 (enExample)
IL (1) IL270821A (enExample)
JO (1) JOP20190269A1 (enExample)
MA (1) MA49402A (enExample)
MX (1) MX2019014974A (enExample)
PE (1) PE20200494A1 (enExample)
PH (1) PH12019502793A1 (enExample)
SG (1) SG11201912154XA (enExample)
TW (1) TW201919713A (enExample)
WO (1) WO2018232055A1 (enExample)

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