RU2716421C2 - Доставка, применение и применения в терапии систем crispr-cas и композиций для целенаправленного воздействия на нарушения и заболевания с использованием вирусных компонентов - Google Patents

Доставка, применение и применения в терапии систем crispr-cas и композиций для целенаправленного воздействия на нарушения и заболевания с использованием вирусных компонентов Download PDF

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RU2716421C2
RU2716421C2 RU2016101198A RU2016101198A RU2716421C2 RU 2716421 C2 RU2716421 C2 RU 2716421C2 RU 2016101198 A RU2016101198 A RU 2016101198A RU 2016101198 A RU2016101198 A RU 2016101198A RU 2716421 C2 RU2716421 C2 RU 2716421C2
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sequence
cas9
crispr
cells
target
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RU2016101198A
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Russian (ru)
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RU2016101198A (ru
RU2016101198A3 (OSRAM
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Фэн ЧЖАН
Лэ ЦУН
Фэй ЖАНЬ
Маттиас ХАЙДЕНРАЙХ
Лукаш СУИЧ
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Те Брод Инститьют Инк.
Массачусетс Инститьют Оф Текнолоджи
Президент Энд Фэллоуз Оф Харвард Коллидж
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Priority claimed from PCT/US2013/074667 external-priority patent/WO2014093622A2/en
Application filed by Те Брод Инститьют Инк., Массачусетс Инститьют Оф Текнолоджи, Президент Энд Фэллоуз Оф Харвард Коллидж filed Critical Те Брод Инститьют Инк.
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RU2016101198A 2013-06-17 2014-06-11 Доставка, применение и применения в терапии систем crispr-cas и композиций для целенаправленного воздействия на нарушения и заболевания с использованием вирусных компонентов RU2716421C2 (ru)

Applications Claiming Priority (15)

Application Number Priority Date Filing Date Title
US201361836123P 2013-06-17 2013-06-17
US61/836,123 2013-06-17
US201361847537P 2013-07-17 2013-07-17
US61/847,537 2013-07-17
US201361862355P 2013-08-05 2013-08-05
US61/862,355 2013-08-05
US201361871301P 2013-08-28 2013-08-28
US61/871,301 2013-08-28
US201361915225P 2013-12-12 2013-12-12
USPCT/US2013/074667 2013-12-12
PCT/US2013/074667 WO2014093622A2 (en) 2012-12-12 2013-12-12 Delivery, engineering and optimization of systems, methods and compositions for sequence manipulation and therapeutic applications
US61/915,225 2013-12-12
US201461979879P 2014-04-15 2014-04-15
US61/979,879 2014-04-15
PCT/US2014/041809 WO2014204729A1 (en) 2013-06-17 2014-06-11 Delivery, use and therapeutic applications of the crispr-cas systems and compositions for targeting disorders and diseases using viral components

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RU2016101198A RU2016101198A (ru) 2019-03-27
RU2016101198A3 RU2016101198A3 (OSRAM) 2019-03-27
RU2716421C2 true RU2716421C2 (ru) 2020-03-11

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US (2) US10946108B2 (OSRAM)
EP (2) EP3597755A1 (OSRAM)
JP (1) JP6702858B2 (OSRAM)
KR (2) KR20250012194A (OSRAM)
CN (2) CN105793425B (OSRAM)
AU (1) AU2014281031B2 (OSRAM)
BR (1) BR122021009076B1 (OSRAM)
CA (1) CA2915795C (OSRAM)
IL (1) IL243195B (OSRAM)
MX (1) MX374532B (OSRAM)
RU (1) RU2716421C2 (OSRAM)
SG (2) SG10201710487VA (OSRAM)
WO (1) WO2014204729A1 (OSRAM)
ZA (1) ZA201508961B (OSRAM)

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