KR20220108216A - 헌팅톤 질환을 치료하기 위한 조성물 및 방법 - Google Patents
헌팅톤 질환을 치료하기 위한 조성물 및 방법 Download PDFInfo
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- KR20220108216A KR20220108216A KR1020227025973A KR20227025973A KR20220108216A KR 20220108216 A KR20220108216 A KR 20220108216A KR 1020227025973 A KR1020227025973 A KR 1020227025973A KR 20227025973 A KR20227025973 A KR 20227025973A KR 20220108216 A KR20220108216 A KR 20220108216A
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Classifications
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- A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
- A61K48/0025—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid
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- A61P25/00—Drugs for disorders of the nervous system
- A61P25/14—Drugs for disorders of the nervous system for treating abnormal movements, e.g. chorea, dyskinesia
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- C07H—SUGARS; DERIVATIVES THEREOF; NUCLEOSIDES; NUCLEOTIDES; NUCLEIC ACIDS
- C07H21/00—Compounds containing two or more mononucleotide units having separate phosphate or polyphosphate groups linked by saccharide radicals of nucleoside groups, e.g. nucleic acids
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- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C—CHEMISTRY; METALLURGY
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- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
- C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
- C12N2750/00011—Details
- C12N2750/14011—Parvoviridae
- C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
- C12N2750/14141—Use of virus, viral particle or viral elements as a vector
- C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
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Applications Claiming Priority (6)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201662338113P | 2016-05-18 | 2016-05-18 | |
| US62/338,113 | 2016-05-18 | ||
| US201762485049P | 2017-04-13 | 2017-04-13 | |
| US62/485,049 | 2017-04-13 | ||
| PCT/US2017/033281 WO2017201258A1 (en) | 2016-05-18 | 2017-05-18 | Compositions and methods of treating huntington's disease |
| KR1020187033504A KR102427379B1 (ko) | 2016-05-18 | 2017-05-18 | 헌팅톤 질환을 치료하기 위한 조성물 및 방법 |
Related Parent Applications (1)
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| KR1020187033504A Division KR102427379B1 (ko) | 2016-05-18 | 2017-05-18 | 헌팅톤 질환을 치료하기 위한 조성물 및 방법 |
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| KR20220108216A true KR20220108216A (ko) | 2022-08-02 |
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| KR1020187033504A Active KR102427379B1 (ko) | 2016-05-18 | 2017-05-18 | 헌팅톤 질환을 치료하기 위한 조성물 및 방법 |
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| KR1020187033504A Active KR102427379B1 (ko) | 2016-05-18 | 2017-05-18 | 헌팅톤 질환을 치료하기 위한 조성물 및 방법 |
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| EP (1) | EP3458589A4 (enExample) |
| JP (1) | JP7220080B2 (enExample) |
| KR (2) | KR20220108216A (enExample) |
| CN (1) | CN109831916B (enExample) |
| AU (1) | AU2017268382B2 (enExample) |
| BR (1) | BR112018073472A2 (enExample) |
| CA (1) | CA3024449A1 (enExample) |
| IL (2) | IL297576B2 (enExample) |
| MX (1) | MX2018014152A (enExample) |
| RU (1) | RU2764587C2 (enExample) |
| SG (1) | SG11201809643UA (enExample) |
| WO (1) | WO2017201258A1 (enExample) |
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| AU2017268382A1 (en) | 2018-11-29 |
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| AU2017268382B2 (en) | 2023-09-28 |
| RU2764587C2 (ru) | 2022-01-18 |
| US20240415868A1 (en) | 2024-12-19 |
| CN109831916B (zh) | 2023-07-21 |
| CA3024449A1 (en) | 2017-11-23 |
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