JP7528066B2 - 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法 - Google Patents
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| CN117624311B (zh) * | 2023-11-29 | 2024-05-28 | 广州译码基因科技有限公司 | 可提高aav病毒神经靶向性的衣壳蛋白突变体及其应用 |
| WO2025122531A1 (en) * | 2023-12-05 | 2025-06-12 | Voyager Therapeutics, Inc. | Compositions and methods for the treatment of disorders related to frataxin deficiency |
| CN118421807B (zh) * | 2024-07-01 | 2024-09-20 | 西南民族大学 | 牦牛多胸腰椎性状筛查的引物对、试剂盒及其用途和筛查方法 |
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| WO2016115503A1 (en) | 2015-01-16 | 2016-07-21 | Voyager Therapeutics, Inc. | Central nervous system targeting polynucleotides |
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| JP2017533715A (ja) | 2014-11-14 | 2017-11-16 | ボイジャー セラピューティクス インコーポレイテッドＶｏｙａｇｅｒ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． | 調節性ポリヌクレオチド |
| JP2017535291A (ja) | 2014-11-05 | 2017-11-30 | ボイジャー セラピューティクス インコーポレイテッドＶｏｙａｇｅｒ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． | パーキンソン病の治療のためのａａｄｃポリヌクレオチド |
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| US12281321B2 (en) | 2025-04-22 |
| JP7761686B2 (ja) | 2025-10-28 |
| CN113383010A (zh) | 2021-09-10 |
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| WO2020069461A1 (en) | 2020-04-02 |
| KR20210068068A (ko) | 2021-06-08 |
| AU2019346655A1 (en) | 2021-05-06 |
| JP2025179046A (ja) | 2025-12-09 |
| US20210395776A1 (en) | 2021-12-23 |
| CN121160803A (zh) | 2025-12-19 |
| EP3856762A1 (en) | 2021-08-04 |
| JP2022500066A (ja) | 2022-01-04 |
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