JP7221275B2 - Ａａｖを送達するための組成物および方法 - Google Patents

Ａａｖを送達するための組成物および方法 Download PDF

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JP7221275B2
JP7221275B2 JP2020505424A JP2020505424A JP7221275B2 JP 7221275 B2 JP7221275 B2 JP 7221275B2 JP 2020505424 A JP2020505424 A JP 2020505424A JP 2020505424 A JP2020505424 A JP 2020505424A JP 7221275 B2 JP7221275 B2 JP 7221275B2
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aav
seq
aavhu
aavrh
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JP2020533959A (ja
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ウェン－イー サー、ディナー
パツケ、ホルガー
ホウ、ジンジャオ
イー． ノネンマッハ、マチュー
グーレ、マーティン
カーター、トッド
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Voyager Therapeutics Inc
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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JP2020505424A 2017-08-03 2018-08-03 Ａａｖを送達するための組成物および方法 Active JP7221275B2 (ja)

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US201762540776P 2017-08-03 2017-08-03
US62/540,776 2017-08-03
US201762565264P 2017-09-29 2017-09-29
US62/565,264 2017-09-29
US201762572706P 2017-10-16 2017-10-16
US62/572,706 2017-10-16
PCT/US2018/045088 WO2019028306A2 (en) 2017-08-03 2018-08-03 COMPOSITIONS AND METHODS FOR ADMINISTRATION OF ADENO-ASSOCIATED VIRUSES

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CN (1) CN111448308A (enExample)
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