JP6023705B2 - ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療 - Google Patents

ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療 Download PDF

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JP6023705B2
JP6023705B2 JP2013516770A JP2013516770A JP6023705B2 JP 6023705 B2 JP6023705 B2 JP 6023705B2 JP 2013516770 A JP2013516770 A JP 2013516770A JP 2013516770 A JP2013516770 A JP 2013516770A JP 6023705 B2 JP6023705 B2 JP 6023705B2
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oligonucleotide
antisense
scn1a
oligonucleotides
rna
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コラド，ジョゼフ
シャーマン，オルガ コルコワ
シャーマン，オルガ コルコワ
レオン，ベリンダ デ
レオン，ベリンダ デ
コイト，カルロス
エイチ．，ドクター． ヒシャオ，ジェーン
エイチ．，ドクター． ヒシャオ，ジェーン
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カッパーアールエヌエー，インコーポレイテッド
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JP2013516770A 2010-06-23 2011-06-23 ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療 Active JP6023705B2 (ja)

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US35777410P 2010-06-23 2010-06-23
US61/357,774 2010-06-23
PCT/US2011/041664 WO2011163499A2 (en) 2010-06-23 2011-06-23 Treatment of sodium channel, voltage-gated, alpha subunit (scna) related diseases by inhibition of natural antisense transcript to scna

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JP2016153460A Division JP6259029B2 (ja) 2010-06-23 2016-08-04 ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療

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JP2013535958A JP2013535958A (ja) 2013-09-19
JP2013535958A5 JP2013535958A5 (https=) 2016-09-29
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JP2013516770A Active JP6023705B2 (ja) 2010-06-23 2011-06-23 ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療
JP2016153460A Active JP6259029B2 (ja) 2010-06-23 2016-08-04 ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療
JP2017235295A Active JP6936717B2 (ja) 2010-06-23 2017-12-07 ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療

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JP2017235295A Active JP6936717B2 (ja) 2010-06-23 2017-12-07 ナトリウムチャネル、電位依存性、αサブユニット（ＳＣＮＡ）に対する天然アンチセンス転写物の阻害によるＳＣＮＡ関連疾患の治療

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JP2015523854A (ja) 2012-05-16 2015-08-20 ラナ セラピューティクス インコーポレイテッド Ｓｍｎ遺伝子ファミリー発現を調節するための組成物及び方法
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WO2015020993A2 (en) * 2013-08-05 2015-02-12 The Trustees Of The University Of Pennsylvania RNAi COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA
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