CN112912499A - 肌肉靶向复合物及其用于治疗面肩肱型肌营养不良的用途 - Google Patents

肌肉靶向复合物及其用于治疗面肩肱型肌营养不良的用途 Download PDF

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CN112912499A
CN112912499A CN201980064591.XA CN201980064591A CN112912499A CN 112912499 A CN112912499 A CN 112912499A CN 201980064591 A CN201980064591 A CN 201980064591A CN 112912499 A CN112912499 A CN 112912499A
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complex
antibody
muscle
oligonucleotide
transferrin receptor
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罗梅什·R·苏布拉马尼亚
穆罕默德·T·卡塔纳尼
蒂莫西·威登
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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CN201980064591.XA 2018-08-02 2019-08-02 肌肉靶向复合物及其用于治疗面肩肱型肌营养不良的用途 Pending CN112912499A (zh)

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US201862713933P 2018-08-02 2018-08-02
US62/713,933 2018-08-02
PCT/US2019/044990 WO2020028864A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy

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CN112912499A true CN112912499A (zh) 2021-06-04

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