JP6702858B2 - ウイルス成分を使用して障害および疾患をターゲティングするためのＣＲＩＳＰＲ−Ｃａｓ系および組成物の送達、使用および治療上の適用 - Google Patents

ウイルス成分を使用して障害および疾患をターゲティングするためのＣＲＩＳＰＲ−Ｃａｓ系および組成物の送達、使用および治療上の適用 Download PDF

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JP6702858B2
JP6702858B2 JP2016521453A JP2016521453A JP6702858B2 JP 6702858 B2 JP6702858 B2 JP 6702858B2 JP 2016521453 A JP2016521453 A JP 2016521453A JP 2016521453 A JP2016521453 A JP 2016521453A JP 6702858 B2 JP6702858 B2 JP 6702858B2
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sequence
cas9
crispr
cells
target
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JP2016521995A (ja
JP2016521995A5 (enExample
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フェン チャン
フェン チャン
レ コン
レ コン
フェイ ラン
フェイ ラン
マティアス ハイデンライヒ
マティアス ハイデンライヒ
ルカシュ スウィッチ
ルカシュ スウィッチ
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Massachusetts Institute of Technology
Broad Institute Inc
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Broad Institute Inc
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Priority claimed from PCT/US2013/074667 external-priority patent/WO2014093622A2/en
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JP2016521453A 2013-06-17 2014-06-11 ウイルス成分を使用して障害および疾患をターゲティングするためのＣＲＩＳＰＲ−Ｃａｓ系および組成物の送達、使用および治療上の適用 Active JP6702858B2 (ja)

Applications Claiming Priority (15)

Application Number Priority Date Filing Date Title
US201361836123P 2013-06-17 2013-06-17
US61/836,123 2013-06-17
US201361847537P 2013-07-17 2013-07-17
US61/847,537 2013-07-17
US201361862355P 2013-08-05 2013-08-05
US61/862,355 2013-08-05
US201361871301P 2013-08-28 2013-08-28
US61/871,301 2013-08-28
US201361915225P 2013-12-12 2013-12-12
USPCT/US2013/074667 2013-12-12
US61/915,225 2013-12-12
PCT/US2013/074667 WO2014093622A2 (en) 2012-12-12 2013-12-12 Delivery, engineering and optimization of systems, methods and compositions for sequence manipulation and therapeutic applications
US201461979879P 2014-04-15 2014-04-15
US61/979,879 2014-04-15
PCT/US2014/041809 WO2014204729A1 (en) 2013-06-17 2014-06-11 Delivery, use and therapeutic applications of the crispr-cas systems and compositions for targeting disorders and diseases using viral components

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JP2016521995A JP2016521995A (ja) 2016-07-28
JP2016521995A5 JP2016521995A5 (enExample) 2017-07-20
JP6702858B2 true JP6702858B2 (ja) 2020-06-03

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US (2) US10946108B2 (enExample)
EP (2) EP3597755A1 (enExample)
JP (1) JP6702858B2 (enExample)
KR (2) KR20160056869A (enExample)
CN (2) CN114015726B (enExample)
AU (1) AU2014281031B2 (enExample)
BR (1) BR122021009076B1 (enExample)
CA (1) CA2915795C (enExample)
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WO (1) WO2014204729A1 (enExample)
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