JP2020522510A - オリゴヌクレオチド組成物及びその使用方法 - Google Patents

オリゴヌクレオチド組成物及びその使用方法 Download PDF

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JP2020522510A
JP2020522510A JP2019566651A JP2019566651A JP2020522510A JP 2020522510 A JP2020522510 A JP 2020522510A JP 2019566651 A JP2019566651 A JP 2019566651A JP 2019566651 A JP2019566651 A JP 2019566651A JP 2020522510 A JP2020522510 A JP 2020522510A
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oligonucleotide
composition
fmfmm
independently
oligonucleotides
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JP2020522510A5 (https=
Inventor
ヴァージェシー，チャンドラ
直樹 岩本
直樹 岩本
チャールズ ドネル バトラー，デイビット
チャールズ ドネル バトラー，デイビット
マラッパン，スブラマニアン
ル，ゲンリャン
ジンシン チャン，ジェイソン
ジンシン チャン，ジェイソン
ヴァシパディーカル，ヴィノッド
デイビッド フランク−カメネットスキー，マリア
デイビッド フランク−カメネットスキー，マリア
エンリケ アッポニ，ルチアーノ
エンリケ アッポニ，ルチアーノ
ジン チョ，ヤング
ジン チョ，ヤング
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Wave Life Sciences Pte Ltd
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Wave Life Sciences Pte Ltd
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Publication of JP2020522510A publication Critical patent/JP2020522510A/ja
Publication of JP2020522510A5 publication Critical patent/JP2020522510A5/ja
Priority to JP2023122841A priority Critical patent/JP2023145620A/ja
Priority to JP2025167006A priority patent/JP2026004488A/ja
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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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JP2019566651A 2017-06-02 2018-06-01 オリゴヌクレオチド組成物及びその使用方法 Pending JP2020522510A (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2023122841A JP2023145620A (ja) 2017-06-02 2023-07-27 オリゴヌクレオチド組成物及びその使用方法
JP2025167006A JP2026004488A (ja) 2017-06-02 2025-10-02 オリゴヌクレオチド組成物及びその使用方法

Applications Claiming Priority (11)

Application Number Priority Date Filing Date Title
US201762514769P 2017-06-02 2017-06-02
US201762514771P 2017-06-02 2017-06-02
US62/514,769 2017-06-02
US62/514,771 2017-06-02
US201862656949P 2018-04-12 2018-04-12
US62/656,949 2018-04-12
US201862670686P 2018-05-11 2018-05-11
US201862670709P 2018-05-11 2018-05-11
US62/670,709 2018-05-11
US62/670,686 2018-05-11
PCT/US2018/035687 WO2018223056A1 (en) 2017-06-02 2018-06-01 Oligonucleotide compositions and methods of use thereof

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JP2020522510A5 JP2020522510A5 (https=) 2021-07-26

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JP2023122841A Pending JP2023145620A (ja) 2017-06-02 2023-07-27 オリゴヌクレオチド組成物及びその使用方法
JP2025167006A Pending JP2026004488A (ja) 2017-06-02 2025-10-02 オリゴヌクレオチド組成物及びその使用方法

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JP2025167006A Pending JP2026004488A (ja) 2017-06-02 2025-10-02 オリゴヌクレオチド組成物及びその使用方法

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US (2) US11603532B2 (https=)
EP (1) EP3630199A4 (https=)
JP (3) JP2020522510A (https=)
CN (2) CN111050806A (https=)
WO (1) WO2018223056A1 (https=)

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