JP2020530307A5 - - Google Patents

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JP2020530307A5
JP2020530307A5 JP2020521488A JP2020521488A JP2020530307A5 JP 2020530307 A5 JP2020530307 A5 JP 2020530307A5 JP 2020521488 A JP2020521488 A JP 2020521488A JP 2020521488 A JP2020521488 A JP 2020521488A JP 2020530307 A5 JP2020530307 A5 JP 2020530307A5
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JP
Japan
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aav
nucleic acid
aav6
mutation
cells
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JP2020521488A
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Japanese (ja)
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JP2020530307A (ja
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Priority claimed from PCT/US2018/040480 external-priority patent/WO2019006418A2/en
Publication of JP2020530307A publication Critical patent/JP2020530307A/ja
Publication of JP2020530307A5 publication Critical patent/JP2020530307A5/ja
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JP2020521488A 2017-06-30 2018-06-29 遺伝子治療のためのアデノ随伴ウイルスベクター Pending JP2020530307A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762527937P 2017-06-30 2017-06-30
US62/527,937 2017-06-30
US201862659472P 2018-04-18 2018-04-18
US62/659,472 2018-04-18
US201862665256P 2018-05-01 2018-05-01
US62/665,256 2018-05-01
PCT/US2018/040480 WO2019006418A2 (en) 2017-06-30 2018-06-29 ADENO-ASSOCIATED VIRAL VECTORS FOR GENE THERAPY

Publications (2)

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JP2020530307A JP2020530307A (ja) 2020-10-22
JP2020530307A5 true JP2020530307A5 (OSRAM) 2021-08-05

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JP2020521488A Pending JP2020530307A (ja) 2017-06-30 2018-06-29 遺伝子治療のためのアデノ随伴ウイルスベクター

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US (3) US11098325B2 (OSRAM)
EP (1) EP3645021A4 (OSRAM)
JP (1) JP2020530307A (OSRAM)
CN (1) CN111511375A (OSRAM)
WO (1) WO2019006418A2 (OSRAM)

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