DK3137596T3 - Sammensætninger og fremgangsmåder til modulation af komplement faktor b-ekspression - Google Patents

Sammensætninger og fremgangsmåder til modulation af komplement faktor b-ekspression Download PDF

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Publication number
DK3137596T3
DK3137596T3 DK15786214.5T DK15786214T DK3137596T3 DK 3137596 T3 DK3137596 T3 DK 3137596T3 DK 15786214 T DK15786214 T DK 15786214T DK 3137596 T3 DK3137596 T3 DK 3137596T3
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modulation
procedures
expression
compositions
complement factor
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DK15786214.5T
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Danish (da)
English (en)
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Thazha P Prakash
Punit P Seth
Eric E Swayze
Tamar R Grossman
Michael L Mccaleb
Andrew T Watt
Susan M Freier
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Ionis Pharmaceuticals Inc
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DK15786214.5T 2014-05-01 2015-05-01 Sammensætninger og fremgangsmåder til modulation af komplement faktor b-ekspression DK3137596T3 (da)

Applications Claiming Priority (3)

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US201461987471P 2014-05-01 2014-05-01
US201462076273P 2014-11-06 2014-11-06
PCT/US2015/028916 WO2015168635A2 (en) 2014-05-01 2015-05-01 Compositions and methods for modulating complement factor b expression

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JP (2) JP6637442B2 (enExample)
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CN (2) CN106232804B (enExample)
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CL (2) CL2016002764A1 (enExample)
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DO (1) DOP2016000291A (enExample)
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IL (2) IL247883B (enExample)
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PE (2) PE20190626A1 (enExample)
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IL297680A (en) * 2020-04-30 2022-12-01 Alnylam Pharmaceuticals Inc Complement factor b (cfb) irna compositions and methods of use thereof
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MX2024002767A (es) 2021-09-02 2024-08-20 Silence Therapeutics Gmbh Ácidos nucleicos para inhibir la expresión del factor b del complemento (cfb) en una célula.
CA3234636A1 (en) * 2021-10-29 2023-05-04 Alnylam Pharmaceuticals, Inc. Complement factor b (cfb) irna compositions and methods of use thereof
AU2023372971A1 (en) * 2022-11-02 2025-05-15 Ionis Pharmaceuticals, Inc. Methods for modulating complement factor b expression
CN120569477A (zh) * 2022-12-19 2025-08-29 美国圣因生物股份有限公司 靶向cfb的小干扰rna及其用途
WO2024197017A2 (en) * 2023-03-21 2024-09-26 Arrowhead Pharmaceuticals, Inc. Rnai agents for inhibiting expression of complement factor b (cfb) pharmaceutical compositions thereof, and methods of use
TW202513799A (zh) * 2023-06-02 2025-04-01 大陸商維亞臻生物技術（蘇州）有限公司 用於免疫類疾病的雙鏈核苷酸化合物及其用途
WO2025002401A1 (zh) * 2023-06-28 2025-01-02 百奥赛图(北京)医药科技股份有限公司 一种cfb基因修饰的非人动物
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