JP6637442B2 - 補体ｂ因子発現を調節するための組成物及び方法 - Google Patents

補体ｂ因子発現を調節するための組成物及び方法 Download PDF

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JP6637442B2
JP6637442B2 JP2016565465A JP2016565465A JP6637442B2 JP 6637442 B2 JP6637442 B2 JP 6637442B2 JP 2016565465 A JP2016565465 A JP 2016565465A JP 2016565465 A JP2016565465 A JP 2016565465A JP 6637442 B2 JP6637442 B2 JP 6637442B2
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certain embodiments
compound
nucleic acid
antisense
modified
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JP2017514489A (ja
JP2017514489A5 (enExample
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プラカシュ，タジャ・ピー
セス，プニット・ピー
スウェイジ，エリック・イー
グロスマン，タマル・アール
マッカレブ，マイケル・エル
ワット，アンドリュー・ティー
フレアー，スーザン・エム
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Ionis Pharmaceuticals Inc
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JP2016565465A 2014-05-01 2015-05-01 補体ｂ因子発現を調節するための組成物及び方法 Active JP6637442B2 (ja)

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US201461987471P 2014-05-01 2014-05-01
US61/987,471 2014-05-01
US201462076273P 2014-11-06 2014-11-06
US62/076,273 2014-11-06
PCT/US2015/028916 WO2015168635A2 (en) 2014-05-01 2015-05-01 Compositions and methods for modulating complement factor b expression

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JP2023523790A (ja) * 2020-04-30 2023-06-07 アルナイラム ファーマシューティカルズ， インコーポレイテッド 補体因子Ｂ（ＣＦＢ）ｉＲＮＡ組成物およびその使用方法
JP2024525868A (ja) * 2021-07-17 2024-07-12 サーナオミクス インコーポレイテッド 産物及び組成物
EP4396346A1 (en) 2021-09-02 2024-07-10 Silence Therapeutics GmbH Nucleic acids for inhibiting expression of complement factor b (cfb) in a cell
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AU2023372971A1 (en) * 2022-11-02 2025-05-15 Ionis Pharmaceuticals, Inc. Methods for modulating complement factor b expression
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TW202513799A (zh) * 2023-06-02 2025-04-01 大陸商維亞臻生物技術（蘇州）有限公司 用於免疫類疾病的雙鏈核苷酸化合物及其用途
CN118620964A (zh) * 2023-06-28 2024-09-10 百奥赛图(北京)医药科技股份有限公司 一种cfb基因修饰的非人动物
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