CN107083400A - 神经退行性疾病的基因治疗 - Google Patents

神经退行性疾病的基因治疗 Download PDF

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Publication number
CN107083400A
CN107083400A CN201610906309.6A CN201610906309A CN107083400A CN 107083400 A CN107083400 A CN 107083400A CN 201610906309 A CN201610906309 A CN 201610906309A CN 107083400 A CN107083400 A CN 107083400A
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aav
cell
sma
mouse
disease
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Chinese (zh)
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M·A·帕西尼
L·谢哈布丁
S·H·程
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Genzyme Corp
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Genzyme Corp
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CN201610906309.6A 2009-05-02 2010-04-27 神经退行性疾病的基因治疗 Pending CN107083400A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US17498209P 2009-05-02 2009-05-02
US61/174,982 2009-05-02
US26805909P 2009-06-08 2009-06-08
US61/268,059 2009-06-08
CN201080027833.7A CN102459611B (zh) 2009-05-02 2010-04-27 神经退行性疾病的基因治疗

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US (9) US20130287736A1 (https=)
EP (5) EP3421603B1 (https=)
JP (3) JP5879256B2 (https=)
KR (2) KR101835490B1 (https=)
CN (2) CN107083400A (https=)
CA (1) CA2759801C (https=)
CY (1) CY1120982T1 (https=)
DK (4) DK3988660T3 (https=)
ES (4) ES3038109T3 (https=)
FI (2) FI3988660T3 (https=)
HR (4) HRP20250897T1 (https=)
HU (4) HUE072713T2 (https=)
IL (2) IL216094A0 (https=)
LT (4) LT3421603T (https=)
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PL (4) PL3421603T3 (https=)
PT (4) PT2424991T (https=)
RS (3) RS62779B1 (https=)
RU (2) RU2743398C2 (https=)
SG (3) SG10202109219SA (https=)
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CN109266682A (zh) * 2018-09-29 2019-01-25 中国科学院武汉物理与数学研究所 一种神经细胞快速逆行跨突触标记的方法及应用
CN108096243B (zh) * 2017-11-24 2020-05-29 江苏康缘药业股份有限公司 银杏内酯组合物的医药用途
CN112567246A (zh) * 2018-01-25 2021-03-26 比奥根Ma公司 治疗脊髓性肌萎缩症的方法
CN114903010A (zh) * 2022-05-19 2022-08-16 暨南大学 神经退行性疾病模型的构建方法
CN118045206A (zh) * 2024-04-12 2024-05-17 四川至善唯新生物科技有限公司 一种治疗脊髓型肌肉萎缩的药物组合物及其用途

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WO2016100575A1 (en) 2014-12-16 2016-06-23 Board Of Regents Of The University Of Nebraska Gene therapy for juvenile batten disease
HRP20190992T1 (hr) * 2014-12-24 2019-09-20 Uniqure Ip B.V. Suprimiranje gena za huntingtin inducirano s rnai
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RU2603740C2 (ru) 2016-11-27
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CA2759801A1 (en) 2010-11-11
SI4342992T1 (sl) 2025-09-30
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KR20120006073A (ko) 2012-01-17
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