JP7049248B2 - 常染色体優性精神遅滞－５とドラベ症候群の処置のためのアンチセンスオリゴマー - Google Patents

常染色体優性精神遅滞－５とドラベ症候群の処置のためのアンチセンスオリゴマー Download PDF

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JP7049248B2
JP7049248B2 JP2018529250A JP2018529250A JP7049248B2 JP 7049248 B2 JP7049248 B2 JP 7049248B2 JP 2018529250 A JP2018529250 A JP 2018529250A JP 2018529250 A JP2018529250 A JP 2018529250A JP 7049248 B2 JP7049248 B2 JP 7049248B2
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aso
intron
syngap1
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JP2019501892A (ja
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アズナレズ，イザベル
エム． ナッシュ，ヒュー
クライナー，エイドリアン
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コールド スプリング ハーバー ラボラトリー
ストーク セラピューティクス，インク．
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JP2018529250A 2015-12-14 2016-12-14 常染色体優性精神遅滞－５とドラベ症候群の処置のためのアンチセンスオリゴマー Expired - Fee Related JP7049248B2 (ja)

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US201562267251P 2015-12-14 2015-12-14
US62/267,251 2015-12-14
PCT/US2016/066708 WO2017106377A1 (en) 2015-12-14 2016-12-14 Antisense oligomers for treatment of autosomal dominant mental retardation-5 and dravet syndrome

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JP2022013860A Pending JP2022062140A (ja) 2015-12-14 2022-02-01 常染色体優性精神遅滞－５とドラベ症候群の処置のためのアンチセンスオリゴマー

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US (2) US11083745B2 (https=)
EP (2) EP3933041B1 (https=)
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CN (2) CN109312343B (https=)
AU (2) AU2016370653A1 (https=)
CA (1) CA3005256A1 (https=)
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