US6924128B2
(en)
*
|
1994-12-06 |
2005-08-02 |
Targeted Genetics Corporation |
Packaging cell lines for generation of high titers of recombinant AAV vectors
|
US6989264B2
(en)
*
|
1997-09-05 |
2006-01-24 |
Targeted Genetics Corporation |
Methods for generating high titer helper-free preparations of released recombinant AAV vectors
|
US6346415B1
(en)
*
|
1997-10-21 |
2002-02-12 |
Targeted Genetics Corporation |
Transcriptionally-activated AAV inverted terminal repeats (ITRS) for use with recombinant AAV vectors
|
US6953690B1
(en)
*
|
1998-03-20 |
2005-10-11 |
The Trustees Of The University Of Pennsylvania |
Compositions and methods for helper-free production of recombinant adeno-associated viruses
|
US6759237B1
(en)
|
1998-11-05 |
2004-07-06 |
The Trustees Of The University Of Pennsylvania |
Adeno-associated virus serotype 1 nucleic acid sequences, vectors and host cells containing same
|
JP4693244B2
(ja)
*
|
1999-03-18 |
2011-06-01 |
ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア |
組換えアデノ随伴ウイルスのヘルパー無しの生産のための組成物および方法
|
US6893865B1
(en)
|
1999-04-28 |
2005-05-17 |
Targeted Genetics Corporation |
Methods, compositions, and cells for encapsidating recombinant vectors in AAV particles
|
US6627617B1
(en)
|
1999-10-01 |
2003-09-30 |
University Of North Carolina At Chapel Hill |
Temperature-sensitive regulation of viral vector production
|
WO2001027303A1
(en)
*
|
1999-10-12 |
2001-04-19 |
The University Of North Carolina At Chapel Hill |
Adeno-associated virus vectors encoding factor viii and methods of using the same
|
CN1310231A
(zh)
*
|
2000-02-24 |
2001-08-29 |
董小岩 |
用含有生长激素基因或相关基因的重组腺病毒相关病毒促进猪的快速生长及改进肉质
|
DE10056210A1
(de)
*
|
2000-11-13 |
2002-05-29 |
Arimedes Biotechnology Gmbh |
Virales Expressionssystem
|
WO2002046359A2
(en)
*
|
2000-12-07 |
2002-06-13 |
Universite De Nantes |
Inducible highly productive raav packaging cell-lines
|
JP2005517387A
(ja)
*
|
2001-10-01 |
2005-06-16 |
ザ ジェネラル ホスピタル コーポレーション |
心疾患の診断および治療の方法
|
EP3108899A1
(en)
|
2001-11-21 |
2016-12-28 |
The Trustees of the University of Pennsylvania |
Simian adenovirus adsv1 nucleic acid and amino acid sequences, vectors containing same, and methods of use
|
EP1944043A1
(en)
|
2001-11-21 |
2008-07-16 |
The Trustees of the University of Pennsylvania |
Simian adenovirus nucleic acid and amino acid sequences, vectors containing same, and methods of use
|
ES2975413T3
(es)
|
2001-12-17 |
2024-07-05 |
Univ Pennsylvania |
Secuencias de serotipo 8 de virus adenoasociado (AAV), vectores que las contienen y usos de las mismas
|
EP1575481A4
(en)
|
2002-03-01 |
2010-01-06 |
Celltech R & D Inc |
PROCESS FOR INCREASING OR REDUCING THE BONE DENSITY
|
US7858367B2
(en)
|
2002-04-30 |
2010-12-28 |
Duke University |
Viral vectors and methods for producing and using the same
|
US7510872B2
(en)
*
|
2003-02-26 |
2009-03-31 |
Nationwide Children's Hospital |
Recombinant adeno-associated virus production
|
KR100794102B1
(ko)
|
2003-12-31 |
2008-01-10 |
(주)아모레퍼시픽 |
인슐린 유사 성장 인자 - ⅰ프로모터를 발현하는 형질감염 세포주 및 이를 이용한 인슐린 유사 성장 인자 -ⅰ프로모터 부위의 활성 측정 방법
|
KR20080043775A
(ko)
|
2005-07-11 |
2008-05-19 |
글로브이뮨 |
표적 치료용 회피 돌연변이체에 대한 면역 반응의 유발방법 및 조성물
|
US20100035973A1
(en)
*
|
2006-07-17 |
2010-02-11 |
Nationwide Children's Hospital, Inc. |
Disruption of programmed death 1 (pd-1) ligand to adjuvant adeno-associated virus vector vaccines
|
WO2008013692A2
(en)
|
2006-07-25 |
2008-01-31 |
Celladon Corporation |
Extended antegrade epicardial coronary infusion of adeno-associated viral vectors for gene therapy
|
CA2693178C
(en)
*
|
2006-11-29 |
2018-12-04 |
Nationwide Children's Hospital, Inc. |
Myostatin inhibition for enhancing muscle and/or improving muscle function
|
KR20100015661A
(ko)
*
|
2007-03-19 |
2010-02-12 |
글로브이뮨 |
암의 표적 치료법의 돌연변이성 이탈의 표적 절제를 위한 조성물 및 방법
|
US8685387B2
(en)
|
2007-11-28 |
2014-04-01 |
The Trustees Of The University Of Pennsylvania |
Simian E adenoviruses SAdV-39, -25.2, -26, -30, -37, and -38
|
KR101614369B1
(ko)
|
2007-11-28 |
2016-04-21 |
더 트러스티스 오브 더 유니버시티 오브 펜실바니아 |
유인원 아과 c 아데노바이러스 sadv-40, -31, 및 -34 및 그것의 사용
|
US8470310B2
(en)
|
2008-03-04 |
2013-06-25 |
The Trustees Of The University Of Pennsylvania |
Simian adenoviruses SAdV-36, -42.1, -42.2, and -44 and uses thereof
|
ES2552688T3
(es)
|
2008-10-31 |
2015-12-01 |
The Trustees Of The University Of Pennsylvania |
Adenovirus de simio con proteínas de la cápside hexónica de SAdV-46 y usos del mismo
|
US11219696B2
(en)
|
2008-12-19 |
2022-01-11 |
Nationwide Children's Hospital |
Delivery of polynucleotides using recombinant AAV9
|
US9415121B2
(en)
|
2008-12-19 |
2016-08-16 |
Nationwide Children's Hospital |
Delivery of MECP2 polynucleotide using recombinant AAV9
|
US8846031B2
(en)
|
2009-05-29 |
2014-09-30 |
The Trustees Of The University Of Pennsylvania |
Simian adenovirus 41 and uses thereof
|
JP2013544600A
(ja)
|
2010-11-23 |
2013-12-19 |
プレサージュ バイオサイエンシズ,インコーポレイテッド |
固体デリバリーのための治療方法および組成物
|
AU2011332025B2
(en)
|
2010-11-23 |
2015-06-25 |
The Trustees Of The University Of Pennsylvania |
Subfamily E simian adenoviruses A1321, A1325, A1295, A1309 and A1322 and uses thereof
|
EP2699673B1
(en)
|
2011-04-21 |
2018-09-19 |
Nationwide Children's Hospital, Inc. |
Recombinant virus products and methods for inhibition of expression of myotilin
|
US10196636B2
(en)
|
2011-04-21 |
2019-02-05 |
Nationwide Children's Hospital, Inc. |
Recombinant virus products and methods for inhibition of expression of myotilin
|
US9249425B2
(en)
*
|
2011-05-16 |
2016-02-02 |
The Trustees Of The University Of Pennslyvania |
Proviral plasmids and production of recombinant adeno-associated virus
|
US20130039888A1
(en)
|
2011-06-08 |
2013-02-14 |
Nationwide Children's Hospital Inc. |
Products and methods for delivery of polynucleotides by adeno-associated virus for lysosomal storage disorders
|
EP3290055B1
(en)
|
2011-07-25 |
2024-08-28 |
Nationwide Children's Hospital, Inc. |
Recombinant virus products and methods for inhibition of expression of dux4
|
US9434928B2
(en)
|
2011-11-23 |
2016-09-06 |
Nationwide Children's Hospital, Inc. |
Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides
|
BR112014028684A2
(pt)
|
2012-05-18 |
2017-07-25 |
Univ Pennsylvania |
subfamília e adenovírus de símio a1302, a1320, a1331 e a1337 e usos dos mesmos
|
DK2879719T3
(en)
|
2012-08-01 |
2018-09-03 |
Nationwide Childrens Hospital |
INTRATEKAL ADMINISTRATION OF RECOMBINANT ADENOASSOCATED VIRUSES
|
JP2015529685A
(ja)
|
2012-09-17 |
2015-10-08 |
ザ・リサーチ・インスティテュート・アット・ネイションワイド・チルドレンズ・ホスピタルThe Research Institute Atnationwide Children’S Hospital |
筋萎縮性側索硬化症の処置のための組成物および方法
|
CA2909807C
(en)
|
2013-04-20 |
2023-08-08 |
Research Institute At Nationwide Children's Hospital |
Recombinant adeno-associated virus delivery of exon 2-targeted u7snrna polynucleotide constructs
|
ES2799437T3
(es)
|
2013-08-27 |
2020-12-17 |
The Res Institute At Nationwide Childrens Hospital |
Productos y métodos para el tratamiento de la esclerosis lateral amiotrófica
|
EP3065784A4
(en)
|
2013-11-05 |
2017-05-10 |
The Research Institute at Nationwide Children's Hospital |
COMPOSITIONS AND METHODS FOR INHIBITING NF- kB AND SOD-1 TO TREAT AMYOTROPHIC LATERAL SCLEROSIS
|
WO2015077717A1
(en)
|
2013-11-25 |
2015-05-28 |
The Broad Institute Inc. |
Compositions and methods for diagnosing, evaluating and treating cancer by means of the dna methylation status
|
US11725237B2
(en)
|
2013-12-05 |
2023-08-15 |
The Broad Institute Inc. |
Polymorphic gene typing and somatic change detection using sequencing data
|
AU2014368898B2
(en)
|
2013-12-20 |
2020-06-11 |
Dana-Farber Cancer Institute, Inc. |
Combination therapy with neoantigen vaccine
|
PL3116900T3
(pl)
|
2014-03-09 |
2021-03-08 |
The Trustees Of The University Of Pennsylvania |
Kompozycje użyteczne w leczeniu niedoboru transkarbamylazy ornitynowej (otc)
|
US10577627B2
(en)
|
2014-06-09 |
2020-03-03 |
Voyager Therapeutics, Inc. |
Chimeric capsids
|
CA2957661A1
(en)
|
2014-08-09 |
2016-02-18 |
Kevin FLANIGAN |
Methods and materials for activating an internal ribosome entry site in exon 5 of the dmd gene
|
US10842886B2
(en)
|
2014-10-10 |
2020-11-24 |
Research Institute At Nationwide Children's Hospital |
Guided injections for AAV gene transfer to muscle
|
EP3690024A1
(en)
|
2014-11-05 |
2020-08-05 |
The Research Institute at Nationwide Children's Hospital |
Methods and materials for producing recombinant viruses in eukaryotic microalgae
|
MX2017005834A
(es)
|
2014-11-05 |
2017-11-17 |
Voyager Therapeutics Inc |
Polinucleotidos aad para el tratamiento de la enfermedad de parkinson.
|
RU2749882C2
(ru)
|
2014-11-14 |
2021-06-18 |
Вояджер Терапьютикс, Инк. |
Модулирующие полинуклеотиды
|
EP3218484A4
(en)
|
2014-11-14 |
2018-05-30 |
Voyager Therapeutics, Inc. |
Compositions and methods of treating amyotrophic lateral sclerosis (als)
|
US11697825B2
(en)
|
2014-12-12 |
2023-07-11 |
Voyager Therapeutics, Inc. |
Compositions and methods for the production of scAAV
|
US10993997B2
(en)
|
2014-12-19 |
2021-05-04 |
The Broad Institute, Inc. |
Methods for profiling the t cell repertoire
|
WO2016100975A1
(en)
|
2014-12-19 |
2016-06-23 |
Massachsetts Institute Ot Technology |
Molecular biomarkers for cancer immunotherapy
|
ES2900973T3
(es)
|
2015-01-07 |
2022-03-21 |
UNIV AUTòNOMA DE BARCELONA |
Constructo genético de vector individual que comprende genes de insulina y glucoquinasa
|
MA41451A
(fr)
|
2015-02-04 |
2017-12-12 |
Univ Washington |
Constructions anti-tau
|
EP3262171A2
(en)
|
2015-02-23 |
2018-01-03 |
Crispr Therapeutics AG |
Materials and methods for treatment of hemoglobinopathies
|
US20180271891A1
(en)
|
2015-03-11 |
2018-09-27 |
The Broad Institute Inc. |
Selective treatment of prmt5 dependent cancer
|
EP3297660A2
(en)
|
2015-05-20 |
2018-03-28 |
The Broad Institute Inc. |
Shared neoantigens
|
TWI750122B
(zh)
|
2015-06-09 |
2021-12-21 |
美商博德研究所有限公司 |
用於贅瘤疫苗之調配物及其製備方法
|
US10017832B2
(en)
|
2015-08-25 |
2018-07-10 |
Washington University |
Compositions and methods for site specific recombination at asymmetric sites
|
AU2016323575B2
(en)
|
2015-09-17 |
2022-10-27 |
Research Institute At Nationwide Children's Hospital |
Methods and materials for GALGT2 gene therapy
|
JP2018532402A
(ja)
|
2015-09-24 |
2018-11-08 |
クリスパー セラピューティクス アーゲー |
Rnaプログラム可能エンドヌクレアーゼの新規のファミリーならびにゲノム編集および他の適用におけるそれらの使用
|
CA3000931A1
(en)
|
2015-10-28 |
2017-05-04 |
Crispr Therapeutics Ag |
Materials and methods for treatment of duchenne muscular dystrophy
|
US20180230489A1
(en)
|
2015-10-28 |
2018-08-16 |
Voyager Therapeutics, Inc. |
Regulatable expression using adeno-associated virus (aav)
|
MX2018005332A
(es)
|
2015-11-06 |
2018-11-09 |
Crispr Therapeutics Ag |
Materiales y metodos para tratamiento de la enfermedad de almacenamiento de glucogeno tipo 1a.
|
CA3005633C
(en)
|
2015-11-16 |
2023-11-21 |
Research Institute Of Nationwide Children's Hospital |
Materials and methods for treatment of titin-based myopathies and other titinopathies
|
EP3384024B1
(en)
|
2015-12-01 |
2022-02-02 |
CRISPR Therapeutics AG |
Materials and methods for treatment of alpha-1 antitrypsin deficiency
|
MX2018007840A
(es)
|
2015-12-23 |
2019-05-02 |
Crispr Therapeutics Ag |
Materiales y metodos para el tratamiento de la esclerosis lateral amiotrofica y/o la degeneracion lobar frontotemporal.
|
WO2017120589A1
(en)
|
2016-01-08 |
2017-07-13 |
Washington University |
Compositions comprising chemerin and methods of use thereof
|
EP3411078A1
(en)
|
2016-02-02 |
2018-12-12 |
Crispr Therapeutics AG |
Materials and methods for treatment of severe combined immunodeficiency (scid) or omenn syndrome
|
US20190112353A1
(en)
|
2016-02-18 |
2019-04-18 |
Crispr Therapeutics Ag |
Materials and methods for treatment of severe combined immunodeficiency (scid) or omenn syndrome
|
US11066456B2
(en)
|
2016-02-25 |
2021-07-20 |
Washington University |
Compositions comprising TREM2 and methods of use thereof
|
CA3015633A1
(en)
|
2016-02-26 |
2017-08-31 |
Research Institute At Nationwide Children's Hospital |
Recombinant virus products and methods for inducing dux4 exon skipping
|
EP3429632B1
(en)
|
2016-03-16 |
2023-01-04 |
CRISPR Therapeutics AG |
Materials and methods for treatment of hereditary haemochromatosis
|
BR112018070249A2
(pt)
|
2016-04-02 |
2019-01-29 |
Research Institute At Nationwide Children's Hospital |
sistema promotor de u6 modificada para expressão específica de tecido
|
LT3442600T
(lt)
|
2016-04-15 |
2024-05-27 |
Research Institute At Nationwide Children's Hospital |
Su adeno virusu susijusio viruso vektoriaus iš β-sarkoglikano ir mikro- rnr-29 pristatymas ir raumenų distrofijos gydymas
|
MA45477A
(fr)
|
2016-04-15 |
2019-02-20 |
Res Inst Nationwide Childrens Hospital |
Administration à vecteurs de virus adéno-associé de microarn-29 et micro-dystrophine pour traiter la dystrophie musculaire
|
WO2017184590A1
(en)
|
2016-04-18 |
2017-10-26 |
The Broad Institute Inc. |
Improved hla epitope prediction
|
US20200330609A1
(en)
|
2016-04-18 |
2020-10-22 |
Crispr Therapeutics Ag |
Materials and methods for treatment of hemoglobinopathies
|
US11299751B2
(en)
|
2016-04-29 |
2022-04-12 |
Voyager Therapeutics, Inc. |
Compositions for the treatment of disease
|
EP3448874A4
(en)
|
2016-04-29 |
2020-04-22 |
Voyager Therapeutics, Inc. |
COMPOSITIONS FOR TREATING A DISEASE
|
WO2017191503A1
(en)
|
2016-05-05 |
2017-11-09 |
Crispr Therapeutics Ag |
Materials and methods for treatment of hemoglobinopathies
|
RU2758488C2
(ru)
|
2016-05-18 |
2021-10-28 |
Вояджер Терапьютикс, Инк. |
Модулирующие полинуклеотиды
|
JP7220080B2
(ja)
|
2016-05-18 |
2023-02-09 |
ボイジャー セラピューティクス インコーポレイテッド |
ハンチントン病治療組成物及び方法
|
EP3478828B1
(en)
|
2016-06-29 |
2024-09-04 |
CRISPR Therapeutics AG |
Materials and methods for treatment of friedreich ataxia and other related disorders
|
WO2018002762A1
(en)
|
2016-06-29 |
2018-01-04 |
Crispr Therapeutics Ag |
Materials and methods for treatment of amyotrophic lateral sclerosis (als) and other related disorders
|
EP3478829A1
(en)
|
2016-06-29 |
2019-05-08 |
Crispr Therapeutics AG |
Materials and methods for treatment of myotonic dystrophy type 1 (dm1) and other related disorders
|
AU2017292169B2
(en)
|
2016-07-06 |
2021-12-23 |
Vertex Pharmaceuticals Incorporated |
Materials and methods for treatment of pain related disorders
|
CN109843914B
(zh)
|
2016-07-06 |
2024-03-15 |
沃泰克斯药物股份有限公司 |
用于治疗疼痛相关病症的材料和方法
|
WO2018007871A1
(en)
|
2016-07-08 |
2018-01-11 |
Crispr Therapeutics Ag |
Materials and methods for treatment of transthyretin amyloidosis
|
WO2018020323A2
(en)
|
2016-07-25 |
2018-02-01 |
Crispr Therapeutics Ag |
Materials and methods for treatment of fatty acid disorders
|
CN110225975A
(zh)
|
2016-08-23 |
2019-09-10 |
阿库斯股份有限公司 |
用于治疗人受试者中非年龄相关的听力损害的组合物和方法
|
EP3506817A4
(en)
|
2016-08-30 |
2020-07-22 |
The Regents of The University of California |
METHOD FOR BIOMEDICAL TARGETING AND RELEASE, AND DEVICES AND SYSTEMS FOR IMPLEMENTING THEM
|
AU2017362491B2
(en)
|
2016-11-17 |
2023-02-02 |
Nationwide Children's Hospital Inc. |
Intrathecal delivery of recombinant Adeno-associated virus encoding Methyl-CpG binding protein 2
|
CN110191955B
(zh)
|
2016-12-13 |
2024-05-31 |
西雅图儿童医院(Dba西雅图儿童研究所) |
在体外和体内对工程化的细胞中表达的化学物质诱导的信号传导复合物进行外源性药物激活的方法
|
US11549149B2
(en)
|
2017-01-24 |
2023-01-10 |
The Broad Institute, Inc. |
Compositions and methods for detecting a mutant variant of a polynucleotide
|
CA3053133A1
(en)
|
2017-02-12 |
2018-08-16 |
Neon Therapeutics, Inc. |
Hla-based methods and compositions and uses thereof
|
WO2018154439A1
(en)
|
2017-02-22 |
2018-08-30 |
Crispr Therapeutics Ag |
Materials and methods for treatment of spinocerebellar ataxia type 1 (sca1) and other spinocerebellar ataxia type 1 protein (atxn1) gene related conditions or disorders
|
WO2018154418A1
(en)
|
2017-02-22 |
2018-08-30 |
Crispr Therapeutics Ag |
Materials and methods for treatment of early onset parkinson's disease (park1) and other synuclein, alpha (snca) gene related conditions or disorders
|
EP3585900B1
(en)
|
2017-02-22 |
2022-12-21 |
CRISPR Therapeutics AG |
Materials and methods for treatment of spinocerebellar ataxia type 2 (sca2) and other spinocerebellar ataxia type 2 protein (atxn2) gene related conditions or disorders
|
CA3054031A1
(en)
|
2017-02-22 |
2018-08-30 |
Crispr Therapeutics Ag |
Compositions and methods for gene editing
|
EP3585899A1
(en)
|
2017-02-22 |
2020-01-01 |
CRISPR Therapeutics AG |
Materials and methods for treatment of primary hyperoxaluria type 1 (ph1) and other alanine-glyoxylate aminotransferase (agxt) gene related conditions or disorders
|
MA47800A
(fr)
|
2017-03-17 |
2020-01-22 |
Univ Newcastle |
Délivrance par vecteur viral adéno-associé d'un fragment de micro-dystrophine pour traiter la dystrophie musculaire
|
JP2020513811A
(ja)
|
2017-03-17 |
2020-05-21 |
リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル |
筋ジストロフィーを治療するための筋肉特異的マイクロジストロフィンのアデノ随伴ウイルスベクター送達
|
WO2018204803A1
(en)
|
2017-05-05 |
2018-11-08 |
Voyager Therapeutics, Inc. |
Compositions and methods of treating huntington's disease
|
WO2018204786A1
(en)
|
2017-05-05 |
2018-11-08 |
Voyager Therapeutics, Inc. |
Compositions and methods of treating amyotrophic lateral sclerosis (als)
|
IL270415B2
(en)
|
2017-05-12 |
2024-08-01 |
Crispr Therapeutics Ag |
Materials and methods for cell engineering and their uses in immuno-oncology
|
JOP20190269A1
(ar)
|
2017-06-15 |
2019-11-20 |
Voyager Therapeutics Inc |
بولي نوكليوتيدات aadc لعلاج مرض باركنسون
|
US20200370069A1
(en)
|
2017-07-08 |
2020-11-26 |
Genethon |
Treatment of spinal muscular atrophy
|
JP7229989B2
(ja)
|
2017-07-17 |
2023-02-28 |
ボイジャー セラピューティクス インコーポレイテッド |
軌道アレイガイドシステム
|
EP3662060A2
(en)
|
2017-08-03 |
2020-06-10 |
Voyager Therapeutics, Inc. |
Compositions and methods for delivery of aav
|
EP4124658A3
(en)
|
2017-10-16 |
2023-04-19 |
Voyager Therapeutics, Inc. |
Treatment of amyotrophic lateral sclerosis (als)
|
EP3697908A1
(en)
|
2017-10-16 |
2020-08-26 |
Voyager Therapeutics, Inc. |
Treatment of amyotrophic lateral sclerosis (als)
|
CA3079172A1
(en)
|
2017-10-17 |
2019-04-25 |
Crispr Therapeutics Ag |
Compositions and methods for gene editing for hemophilia a
|
US11534501B2
(en)
|
2017-10-18 |
2022-12-27 |
Research Institute At Nationwide Children's Hospital |
Adeno-associated virus vector delivery of muscle specific micro-dystrophin to treat muscular dystrophy
|
CA3079416A1
(en)
|
2017-10-20 |
2019-04-25 |
Research Institute At Nationwide Children's Hospital |
Methods and materials for nt-3 gene therapy
|
MA50849A
(fr)
|
2017-10-26 |
2020-09-02 |
Vertex Pharma |
Substances et procédés pour le traitement d'hémoglobinopathies
|
IL314692A
(en)
|
2017-11-08 |
2024-10-01 |
Novartis Ag |
Means and method for preparing viral vectors and their uses
|
EP3707155A2
(en)
|
2017-11-09 |
2020-09-16 |
Vertex Pharmaceuticals Incorporated |
Crispr/cas systems for treatment of dmd
|
EP3714055A1
(en)
|
2017-11-21 |
2020-09-30 |
CRISPR Therapeutics AG |
Materials and methods for treatment of autosomal dominant retinitis pigmentosa
|
AU2018386301A1
(en)
|
2017-12-14 |
2020-06-18 |
Bayer Healthcare Llc |
Novel RNA-programmable endonuclease systems and their use in genome editing and other applications
|
US11793867B2
(en)
|
2017-12-18 |
2023-10-24 |
Biontech Us Inc. |
Neoantigens and uses thereof
|
EP3728595A1
(en)
|
2017-12-21 |
2020-10-28 |
CRISPR Therapeutics AG |
Materials and methods for treatment of usher syndrome type 2a and/or non-syndromic autosomal recessive retinitis pigmentosa (arrp)
|
WO2019123429A1
(en)
|
2017-12-21 |
2019-06-27 |
Casebia Therapeutics Llp |
Materials and methods for treatment of usher syndrome type 2a
|
CA3088180A1
(en)
|
2018-01-12 |
2019-07-18 |
Crispr Therapeutics Ag |
Compositions and methods for gene editing by targeting transferrin
|
EP3749768A1
(en)
|
2018-02-05 |
2020-12-16 |
Vertex Pharmaceuticals Incorporated |
Materials and methods for treatment of hemoglobinopathies
|
US11566236B2
(en)
|
2018-02-05 |
2023-01-31 |
Vertex Pharmaceuticals Incorporated |
Materials and methods for treatment of hemoglobinopathies
|
US20210130824A1
(en)
|
2018-02-16 |
2021-05-06 |
Crispr Therapeutics Ag |
Compositions and methods for gene editing by targeting fibrinogen-alpha
|
EP3762500A1
(en)
|
2018-03-06 |
2021-01-13 |
Voyager Therapeutics, Inc. |
Insect cell manufactured partial self-complementary aav genomes
|
CA3092497A1
(en)
|
2018-03-19 |
2019-09-26 |
Crispr Therapeutics Ag |
Novel rna-programmable endonuclease systems and uses thereof
|
WO2019204668A1
(en)
|
2018-04-18 |
2019-10-24 |
Casebia Therapeutics Limited Liability Partnership |
Compositions and methods for knockdown of apo(a) by gene editing for treatment of cardiovascular disease
|
KR20210016353A
(ko)
|
2018-04-27 |
2021-02-15 |
시애틀 칠드런즈 호스피탈 디/비/에이 시애틀 칠드런즈 리서치 인스티튜트 |
라파마이신 내성 세포
|
JP2021521852A
(ja)
|
2018-04-27 |
2021-08-30 |
ボイジャー セラピューティクス インコーポレイテッドVoyager Therapeutics,Inc. |
Aadcウイルスベクターの効力を測定する方法
|
MA52631A
(fr)
|
2018-05-15 |
2021-03-24 |
Voyager Therapeutics Inc |
Compositions et méthodes pour le traitement de la maladie de parkinson
|
WO2019222329A1
(en)
|
2018-05-15 |
2019-11-21 |
Voyager Therapeutics, Inc. |
Compositions and methods for delivery of aav
|
WO2019222441A1
(en)
|
2018-05-16 |
2019-11-21 |
Voyager Therapeutics, Inc. |
Aav serotypes for brain specific payload delivery
|
WO2019222444A2
(en)
|
2018-05-16 |
2019-11-21 |
Voyager Therapeutics, Inc. |
Directed evolution
|
JP7478675B2
(ja)
|
2018-06-08 |
2024-05-07 |
ノバルティス アーゲー |
薬物製品の効力を測定するための細胞ベースアッセイ
|
GB201809588D0
(en)
|
2018-06-12 |
2018-07-25 |
Univ Bristol |
Materials and methods for modulating intraocular and intracranial pressure
|
EP3807404A1
(en)
|
2018-06-13 |
2021-04-21 |
Voyager Therapeutics, Inc. |
Engineered 5' untranslated regions (5' utr) for aav production
|
CA3104471A1
(en)
|
2018-06-18 |
2019-12-26 |
Research Institute At Nationwide Children's Hospital |
Recombinant adeno-associated virus products and methods for treating dystroglycanopathies and laminin-deficient muscular dystrophies
|
SG11202012450QA
(en)
|
2018-06-18 |
2021-01-28 |
Res Inst Nationwide Childrens Hospital |
Adeno-associated virus vector delivery of muscle specific micro-dystrophin to treat muscular dystrophy
|
US20210277362A1
(en)
|
2018-06-29 |
2021-09-09 |
Research Institute At Nationwide Children's Hospital |
Recombinant adeno-associated virus products and methods for treating limb girdle muscular dystrophy 2a
|
JP7565218B2
(ja)
|
2018-07-02 |
2024-10-10 |
ボイジャー セラピューティクス インコーポレイテッド |
筋萎縮性側索硬化症および脊髄に関連する障害の治療
|
US20210355454A1
(en)
|
2018-07-24 |
2021-11-18 |
Voyager Therapeutics, Inc. |
Systems and methods for producing gene therapy formulations
|
EP3844284A1
(en)
|
2018-08-29 |
2021-07-07 |
Research Institute at Nationwide Children's Hospital |
Products and methods for inhibition of expression of mutant gars protein
|
WO2020072683A1
(en)
|
2018-10-02 |
2020-04-09 |
Voyager Therapeutics, Inc. |
Redirection of tropism of aav capsids
|
US20210382068A1
(en)
|
2018-10-02 |
2021-12-09 |
Dana-Farber Cancer Institute, Inc. |
Hla single allele lines
|
US20210348242A1
(en)
|
2018-10-04 |
2021-11-11 |
Voyager Therapeutics, Inc. |
Methods for measuring the titer and potency of viral vector particles
|
JP2022512621A
(ja)
|
2018-10-05 |
2022-02-07 |
ボイジャー セラピューティクス インコーポレイテッド |
Aav産生タンパク質をコードする操作された核酸コンストラクト
|
WO2020077165A1
(en)
|
2018-10-12 |
2020-04-16 |
Voyager Therapeutics, Inc. |
Compositions and methods for delivery of aav
|
CA3116701A1
(en)
|
2018-10-15 |
2020-04-23 |
Voyager Therapeutics, Inc. |
Expression vectors for large-scale production of raav in the baculovirus/sf9 system
|
WO2020081843A1
(en)
|
2018-10-17 |
2020-04-23 |
Casebia Therapeutics Limited Liability Partnership |
Compositions and methods for delivering transgenes
|
AU2019389047A1
(en)
|
2018-11-30 |
2021-05-20 |
Novartis Ag |
AAV viral vectors and uses thereof
|
WO2020131586A2
(en)
|
2018-12-17 |
2020-06-25 |
The Broad Institute, Inc. |
Methods for identifying neoantigens
|
US20220042045A1
(en)
|
2018-12-21 |
2022-02-10 |
Genethon |
Expression cassettes for gene therapy vectors
|
BR112021012278A2
(pt)
|
2018-12-21 |
2021-12-14 |
Biontech Us Inc |
Método e sistema para a preparação de células hla de classe ii-específica de epitopes e de síntese de cd4 + t
|
KR20210110345A
(ko)
|
2018-12-31 |
2021-09-07 |
더 리서치 인스티튜트 앳 네이션와이드 칠드런스 하스피탈 |
RNA 표적화 CRISPR-Cas13b를 사용한 DUX4 RNA 침묵화
|
US20220064671A1
(en)
|
2019-01-18 |
2022-03-03 |
Voyager Therapeutics, Inc. |
Methods and systems for producing aav particles
|
CN113924115A
(zh)
|
2019-01-31 |
2022-01-11 |
俄勒冈健康与科学大学 |
用于aav衣壳的使用转录依赖性定向进化的方法
|
BR112021015285A2
(pt)
|
2019-02-04 |
2021-10-05 |
Research Institute At Nationwide Children's Hospital |
Entrega de vírus adenoassociado de polinucleotídeo cln3
|
JP2022519597A
(ja)
|
2019-02-04 |
2022-03-24 |
リサーチ・インスティチュート・アット・ネーションワイド・チルドレンズ・ホスピタル |
Cln6ポリヌクレオチドのアデノ随伴ウイルス送達
|
SG11202108357PA
(en)
|
2019-02-15 |
2021-08-30 |
Crispr Therapeutics Ag |
Gene editing for hemophilia a with improved factor viii expression
|
US20230241252A1
(en)
|
2019-02-26 |
2023-08-03 |
Research Institute At Nationwide Children's Hospital |
Adeno-associated virus vector delivery of b-sarcoglycan and the treatment of muscular dystrophy
|
WO2020186059A2
(en)
|
2019-03-12 |
2020-09-17 |
Crispr Therapeutics Ag |
Novel high fidelity rna-programmable endonuclease systems and uses thereof
|
CA3137080A1
(en)
|
2019-04-15 |
2020-10-22 |
Sanford Research |
Gene therapy for treating or preventing visual effects in batten disease
|
EP3962536A1
(en)
|
2019-04-29 |
2022-03-09 |
Voyager Therapeutics, Inc. |
Systems and methods for producing baculoviral infected insect cells (biics) in bioreactors
|
EP3966227A1
(en)
|
2019-05-07 |
2022-03-16 |
Voyager Therapeutics, Inc. |
Compositions and methods for the vectored augmentation of protein destruction, expression and/or regulation
|
US20210047649A1
(en)
|
2019-05-08 |
2021-02-18 |
Vertex Pharmaceuticals Incorporated |
Crispr/cas all-in-two vector systems for treatment of dmd
|
AR118696A1
(es)
|
2019-05-17 |
2021-10-27 |
Res Institute At Nationwide ChildrenS Hospital |
Administración mejorada de vectores de tratamiento génico a células retinianas mediante el uso de una enzima glicósido hidrolasa
|
EP3990636A1
(en)
|
2019-06-28 |
2022-05-04 |
CRISPR Therapeutics AG |
Materials and methods for controlling gene editing
|
KR20220035937A
(ko)
|
2019-07-25 |
2022-03-22 |
노파르티스 아게 |
조절 가능한 발현 시스템
|
EP4010465A1
(en)
|
2019-08-09 |
2022-06-15 |
Voyager Therapeutics, Inc. |
Cell culture medium for use in producing gene therapy products in bioreactors
|
HUE066215T2
(hu)
|
2019-08-21 |
2024-07-28 |
Res Institute At Nationwide |
Alfa-szarkoglikán bevitele adenoasszociáltvírus-vektorral és izomdisztrófia kezelése
|
US20220364114A1
(en)
|
2019-08-26 |
2022-11-17 |
Voyager Therapeutics, Inc. |
Controlled expression of viral proteins
|
US20220333133A1
(en)
|
2019-09-03 |
2022-10-20 |
Voyager Therapeutics, Inc. |
Vectorized editing of nucleic acids to correct overt mutations
|
US20220389453A1
(en)
|
2019-10-18 |
2022-12-08 |
Research Institute At Nationwide Children's Hospital |
Materials and methods for the treatment of disorders associated with the irf2bpl gene
|
CA3158286A1
(en)
|
2019-10-18 |
2021-04-22 |
Research Institute At Nationwide Children's Hospital |
Gene therapy targeting cochlear cells
|
JP2023502474A
(ja)
|
2019-11-22 |
2023-01-24 |
リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル |
Ighmbp2遺伝子に関連する障害の治療のための材料および方法
|
CA3165469A1
(en)
|
2019-12-20 |
2021-06-24 |
Research Institute At Nationwide Children's Hospital |
Optimized gene therapy for targeting muscle in muscle diseases
|
CN115485382A
(zh)
|
2020-02-18 |
2022-12-16 |
全国儿童医院研究所 |
X连锁病症的治疗中的AAV介导的MiRNA靶向
|
AU2021225035A1
(en)
|
2020-02-21 |
2022-10-13 |
Akouos, Inc. |
Compositions and methods for treating non-age-associated hearing impairment in a human subject
|
US20230131352A1
(en)
|
2020-04-01 |
2023-04-27 |
Voyager Therapeutics, Inc. |
Redirection of tropism of aav capsids
|
CA3174863A1
(en)
|
2020-04-14 |
2021-10-21 |
Ana BUJ BELLO |
Vectors for the treatment of acid ceramidase deficiency
|
WO2021211753A1
(en)
|
2020-04-15 |
2021-10-21 |
Voyager Therapeutics, Inc. |
Tau binding compounds
|
GB202005732D0
(en)
|
2020-04-20 |
2020-06-03 |
Synpromics Ltd |
Regulatory nucleic acid sequences
|
BR112022023106A2
(pt)
|
2020-05-13 |
2023-01-17 |
Voyager Therapeutics Inc |
Redirecionamento de tropismo de capsídeos de aav
|
WO2021247995A2
(en)
|
2020-06-04 |
2021-12-09 |
Voyager Therapeutics, Inc. |
Compositions and methods of treating neuropathic pain
|
AU2021293197A1
(en)
|
2020-06-15 |
2023-02-09 |
Research Institute At Nationwide Children's Hospital |
Adeno-associated virus vector delivery for muscular dystrophies
|
WO2022018638A1
(en)
|
2020-07-21 |
2022-01-27 |
Crispr Therapeutics Ag |
Genome-editing compositions and methods to modulate faah for treatment of neurological disorders
|
WO2022032153A1
(en)
|
2020-08-06 |
2022-02-10 |
Voyager Therapeutics, Inc. |
Cell culture medium for use in producing gene therapy products in bioreactors
|
GB202013940D0
(en)
|
2020-09-04 |
2020-10-21 |
Synpromics Ltd |
Regulatory nucleic acid sequences
|
TW202227634A
(zh)
|
2020-09-08 |
2022-07-16 |
美商薩羅塔治療公司 |
表現γ—肌聚醣之腺相關病毒載體之全身性遞送及肌肉失養症之治療
|
US20230357795A1
(en)
|
2020-09-15 |
2023-11-09 |
Research Institute At Nationwide Children's Hospital |
Aav-mediated homology-independent targeted integration gene editing for correction of diverse dmd mutations in patients with muscular dystrophy
|
JP2023543029A
(ja)
|
2020-09-28 |
2023-10-12 |
リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル |
筋ジストロフィーの治療のための製品及び方法
|
US20220290136A1
(en)
|
2020-09-30 |
2022-09-15 |
Crispr Therapeutics Ag |
Materials and methods for treatment of amyotrophic lateral sclerosis
|
JP2023548067A
(ja)
|
2020-11-02 |
2023-11-15 |
バイオマリン ファーマシューティカル インコーポレイテッド |
アデノ随伴ウイルスを濃縮するためのプロセス
|
WO2022115745A1
(en)
|
2020-11-30 |
2022-06-02 |
Research Institute At Nationwide Children's Hospital |
Compositions and methods for treating facioscapulohumeral muscular dystrophy (fshd)
|
CN117083081A
(zh)
|
2020-12-14 |
2023-11-17 |
百欧恩泰美国公司 |
用于癌症免疫疗法的组织特异性抗原
|
US20220228142A1
(en)
|
2020-12-17 |
2022-07-21 |
Vertex Pharmaceuticals Incorporated |
Compositions and methods for editing beta-globin for treatment of hemaglobinopathies
|
AU2022212922A1
(en)
|
2021-01-27 |
2023-08-17 |
Research Institute At Nationwide Children's Hospital |
Materials and methods for the treatment of lysosomal acid lipase deficiency (lal-d)
|
AU2022214429A1
(en)
|
2021-02-01 |
2023-09-14 |
Regenxbio Inc. |
Gene therapy for neuronal ceroid lipofuscinoses
|
US20240093191A1
(en)
|
2021-02-03 |
2024-03-21 |
Research Institute At Nationwide Children's Hospital |
Compositions and methods for treating disease associated with dux4 overexpression
|
WO2022170038A1
(en)
|
2021-02-05 |
2022-08-11 |
Amicus Therapeutics, Inc. |
Adeno-associated virus delivery of cln3 polynucleotide
|
US20240141378A1
(en)
|
2021-03-03 |
2024-05-02 |
Voyager Therapeutics, Inc. |
Controlled expression of viral proteins
|
WO2022187473A2
(en)
|
2021-03-03 |
2022-09-09 |
Voyager Therapeutics, Inc. |
Controlled expression of viral proteins
|
JP2024508324A
(ja)
|
2021-03-04 |
2024-02-26 |
リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル |
Dmdエクソンの重複を修正するためのcrispr-cas9を使用したジストロフィンベースのミオパチーの治療のための生成物及び方法
|
WO2022188797A1
(en)
|
2021-03-09 |
2022-09-15 |
Huigene Therapeutics Co., Ltd. |
Engineered crispr/cas13 system and uses thereof
|
EP4323010A1
(en)
|
2021-04-13 |
2024-02-21 |
Research Institute at Nationwide Children's Hospital |
Recombinant adeno-associated virus encoding methyl-cpg binding protein 2 for treating pitt hopkins syndrome via intrathecal delivery
|
CA3216491A1
(en)
|
2021-04-16 |
2022-10-20 |
Asklepios Biopharmaceutical, Inc. |
Rational polyploid aav virions that cross the blood brain barrier and elicit reduced humoral response
|
AU2022262420A1
(en)
|
2021-04-23 |
2023-11-16 |
Research Institute At Nationwide Children's Hospital |
Products and methods for treating muscular dystrophy
|
WO2022234295A1
(en)
|
2021-05-07 |
2022-11-10 |
Ucl Business Ltd |
Abca4 genome editing
|
KR20240021765A
(ko)
|
2021-05-17 |
2024-02-19 |
사렙타 쎄러퓨틱스 인코퍼레이티드 |
근이영양증 치료를 위한 재조합 aav 벡터의 제조
|
EP4108263A3
(en)
|
2021-06-02 |
2023-03-22 |
Research Institute at Nationwide Children's Hospital |
Recombinant adeno-associated virus products and methods for treating limb girdle muscular dystrophy 2a
|
EP4101928A1
(en)
|
2021-06-11 |
2022-12-14 |
Bayer AG |
Type v rna programmable endonuclease systems
|
EP4352214A1
(en)
|
2021-06-11 |
2024-04-17 |
Bayer AG |
Type v rna programmable endonuclease systems
|
WO2023283962A1
(en)
|
2021-07-16 |
2023-01-19 |
Huigene Therapeutics Co., Ltd. |
Modified aav capsid for gene therapy and methods thereof
|
EP4384628A2
(en)
|
2021-08-11 |
2024-06-19 |
Solid Biosciences Inc. |
Treatment of muscular dystrophy
|
EP4396201A1
(en)
|
2021-09-03 |
2024-07-10 |
BioMarin Pharmaceutical Inc. |
Aav capsid compositions and methods for delivery
|
JP2024533174A
(ja)
|
2021-09-03 |
2024-09-12 |
ビオマリン プハルマセウトイカル インコーポレイテッド |
Aavカプシド組成物及び送達方法
|
WO2023034980A1
(en)
|
2021-09-03 |
2023-03-09 |
Bomarin Pharmaceutical Inc. |
Aav capsid compositions and methods for delivery
|
WO2023034990A1
(en)
|
2021-09-03 |
2023-03-09 |
Biomarin Pharmaceutical Inc. |
Aav capsid compositions and methods for delivery
|
EP4396203A1
(en)
|
2021-09-03 |
2024-07-10 |
BioMarin Pharmaceutical Inc. |
Aav capsid compositions and methods for delivery
|
WO2023034996A1
(en)
|
2021-09-03 |
2023-03-09 |
Biomarin Pharmaceutical Inc. |
Aav capsid compositions and methods for delivery
|
EP4144841A1
(en)
|
2021-09-07 |
2023-03-08 |
Bayer AG |
Novel small rna programmable endonuclease systems with impoved pam specificity and uses thereof
|
CN117980484A
(zh)
|
2021-09-16 |
2024-05-03 |
诺华股份有限公司 |
新颖的转录因子
|
EP4405396A2
(en)
|
2021-09-20 |
2024-07-31 |
Voyager Therapeutics, Inc. |
Compositions and methods for the treatment of her2 positive cancer
|
AU2022360382A1
(en)
|
2021-10-07 |
2024-05-09 |
Research Institute At Nationwide Children's Hospital |
Products and methods for myelin protein zero silencing and treating cmt1b disease
|
WO2023060233A1
(en)
|
2021-10-08 |
2023-04-13 |
Amicus Therapeutics, Inc. |
Biomarkers for lysosomal storage diseases
|
EP4219726A1
(en)
|
2021-10-15 |
2023-08-02 |
Research Institute at Nationwide Children's Hospital |
Self-complementary adeno-associated virus vector and its use in treatment of muscular dystrophy
|
TW202334436A
(zh)
|
2021-11-02 |
2023-09-01 |
美商航海家醫療公司 |
Aav衣殼變異體及其用途
|
TW202334181A
(zh)
|
2021-11-17 |
2023-09-01 |
美商航海家醫療公司 |
Aav蛋白殼變異體及其用途
|
EP4186919A1
(en)
|
2021-11-30 |
2023-05-31 |
Research Institute at Nationwide Children's Hospital |
Self-complementary adeno-associated virus vector and its use in treatment of muscular dystrophy
|
EP4198048A1
(en)
|
2021-12-16 |
2023-06-21 |
Genethon |
Calpain-3 gene transfer increase using modified itr sequences
|
EP4198046A1
(en)
|
2021-12-16 |
2023-06-21 |
Genethon |
Alpha-sarcoglycan gene transfer increase using modified itr sequences
|
EP4198134A1
(en)
|
2021-12-16 |
2023-06-21 |
Genethon |
Gamma-sarcoglycan gene transfer increase using modified itr sequences
|
CA3240342A1
(en)
|
2021-12-16 |
2023-06-22 |
Gopal SAPKOTA |
Targeted degradation of alpha-synuclein
|
EP4198047A1
(en)
|
2021-12-16 |
2023-06-21 |
Genethon |
Fukutin related protein gene transfer increase using modified itr sequences
|
WO2023122669A1
(en)
|
2021-12-21 |
2023-06-29 |
Research Institute At Nationwide Children's Hospital |
Materials and methods for the treatment of limb girdle muscular dystrophy
|
WO2023118068A1
(en)
|
2021-12-23 |
2023-06-29 |
Bayer Aktiengesellschaft |
Novel small type v rna programmable endonuclease systems
|
WO2023147374A2
(en)
|
2022-01-25 |
2023-08-03 |
Voyager Therapeutics, Inc. |
Baculovirus expression system
|
IL314156A
(en)
|
2022-02-08 |
2024-09-01 |
Voyager Therapeutics Inc |
Adeno-associated virus capsid variants and their uses
|
GB202201713D0
(en)
|
2022-02-10 |
2022-03-30 |
Univ Dundee |
An affinity directed phosphatase system for targeted protein dephosphorylation
|
WO2023166425A1
(en)
|
2022-03-01 |
2023-09-07 |
Crispr Therapeutics Ag |
Methods and compositions for treating angiopoietin-like 3 (angptl3) related conditions
|
AU2023227586A1
(en)
|
2022-03-03 |
2024-09-12 |
Research Institute At Nationwide Children's Hospital |
Materials and methods for the treatment of eif2b5 mutations and diseases resulting therefrom
|
WO2023196818A1
(en)
|
2022-04-04 |
2023-10-12 |
The Regents Of The University Of California |
Genetic complementation compositions and methods
|
WO2023214346A1
(en)
|
2022-05-06 |
2023-11-09 |
Novartis Ag |
Novel recombinant aav vp2 fusion polypeptides
|
TW202417466A
(zh)
|
2022-06-02 |
2024-05-01 |
美商航海家醫療公司 |
Aav蛋白殼變異體及其用途
|
WO2023240177A1
(en)
|
2022-06-08 |
2023-12-14 |
Research Instiitute At Nationwide Children's Hospital |
Products and methods for treating diseases or conditions associated with mutant or pathogenic kcnq3 expression
|
WO2023237587A1
(en)
|
2022-06-10 |
2023-12-14 |
Bayer Aktiengesellschaft |
Novel small type v rna programmable endonuclease systems
|
AR129733A1
(es)
|
2022-06-28 |
2024-09-25 |
Voyager Therapeutics Inc |
Variantes de cápsides de aav y sus usos
|
WO2024011112A1
(en)
|
2022-07-06 |
2024-01-11 |
Voyager Therapeutics, Inc. |
Aav capsid variants and uses thereof
|
WO2024011115A1
(en)
|
2022-07-06 |
2024-01-11 |
Research Institute At Nationwide Children's Hospital |
Adeno-associated virus delivery of cln1 polynucleotide
|
WO2024015892A1
(en)
|
2022-07-13 |
2024-01-18 |
The Broad Institute, Inc. |
Hla-ii immunopeptidome methods and systems for antigen discovery
|
WO2024035782A1
(en)
|
2022-08-10 |
2024-02-15 |
Aav Gene Therapeutics, Inc. |
Aav-mediated intramuscular delivery of insulin
|
WO2024054983A1
(en)
|
2022-09-08 |
2024-03-14 |
Voyager Therapeutics, Inc. |
Controlled expression of viral proteins
|
WO2024059739A1
(en)
|
2022-09-15 |
2024-03-21 |
Voyager Therapeutics, Inc. |
Tau binding compounds
|
WO2024064856A1
(en)
|
2022-09-22 |
2024-03-28 |
Biomarin Pharmaceutical Inc. |
Treatment of cardiomyopathy with aav gene therapy vectors
|
WO2024064863A2
(en)
|
2022-09-22 |
2024-03-28 |
Biomarin Pharmaceutical Inc. |
Treatment of arrhythmogenic cardiomyopathy with aav gene therapy vectors
|
WO2024064913A1
(en)
|
2022-09-23 |
2024-03-28 |
Sarepta Therapeutics, Inc. |
Recombinant aav vectors for treating muscular dystrophy
|
WO2024081706A1
(en)
|
2022-10-11 |
2024-04-18 |
Research Institute At Nationwide Children's Hospital |
Adeno-associated virus delivery to treat spinal muscular atrophy with respiratory distress type 1 (smard1) and charcot-marie-tooth type 2s (cmt2s)
|
WO2024092126A1
(en)
|
2022-10-27 |
2024-05-02 |
Cargo Therapeutics, Inc. |
Compositions and methods for improved immunotherapies
|
WO2024129743A2
(en)
|
2022-12-13 |
2024-06-20 |
Bluerock Therapeutics Lp |
Engineered type v rna programmable endonucleases and their uses
|
WO2024145474A2
(en)
|
2022-12-29 |
2024-07-04 |
Voyager Therapeutics, Inc. |
Compositions and methods for regulating mapt
|
WO2024151982A1
(en)
|
2023-01-13 |
2024-07-18 |
Amicus Therapeutics, Inc. |
Gene therapy constructs for the treatment of pompe disease
|
WO2024163560A1
(en)
|
2023-02-01 |
2024-08-08 |
Sarepta Therapeutics, Inc. |
Raav production methods
|
WO2024168276A2
(en)
|
2023-02-09 |
2024-08-15 |
Cargo Therapeutics, Inc. |
Compositions and methods for immunotherapies
|