CN111902148B - 治疗肌萎缩和强直性肌营养不良的组合物和方法 - Google Patents

治疗肌萎缩和强直性肌营养不良的组合物和方法 Download PDF

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CN111902148B
CN111902148B CN201880088816.0A CN201880088816A CN111902148B CN 111902148 B CN111902148 B CN 111902148B CN 201880088816 A CN201880088816 A CN 201880088816A CN 111902148 B CN111902148 B CN 111902148B
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polynucleic acid
acid molecule
sirna
conjugate
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CN111902148A (zh
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安德鲁·约翰·吉尔
文卡塔·拉马纳·多帕拉普迪
大卫·世-豪·朱
迈克尔·卡拉米安·科克伦
迈克尔·胡德
比亚特丽丝·戴安娜·达里蒙特
罗伯·伯克
石云雨
古林·埃尔多安·莫雷柳斯
巴尔博拉·马勒科娃
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Avidity Biosciences Inc
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Avidity Biosciences Inc
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Priority to CN202410788003.XA priority patent/CN118638788A/zh
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CN201880088816.0A 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法 Active CN111902148B (zh)

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CN202410788001.0A CN118667812A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法
CN202410788002.5A CN118638787A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法
CN202410788003.XA CN118638788A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法

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US201762595545P 2017-12-06 2017-12-06
US62/595,545 2017-12-06
US201862725883P 2018-08-31 2018-08-31
US62/725,883 2018-08-31
PCT/US2018/064359 WO2019113393A1 (en) 2017-12-06 2018-12-06 Compositions and methods of treating muscle atrophy and myotonic dystrophy

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CN202410788002.5A Division CN118638787A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法
CN202410788003.XA Division CN118638788A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法
CN202410788001.0A Division CN118667812A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法

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CN202410788001.0A Pending CN118667812A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法
CN202410788002.5A Pending CN118638787A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法
CN202410788003.XA Pending CN118638788A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法

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CN202410788002.5A Pending CN118638787A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法
CN202410788003.XA Pending CN118638788A (zh) 2017-12-06 2018-12-06 治疗肌萎缩和强直性肌营养不良的组合物和方法

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