TR201902952T4 - Dmd için ekson atlama bileşimleri. - Google Patents

Dmd için ekson atlama bileşimleri. Download PDF

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Publication number
TR201902952T4
TR201902952T4 TR2019/02952T TR201902952T TR201902952T4 TR 201902952 T4 TR201902952 T4 TR 201902952T4 TR 2019/02952 T TR2019/02952 T TR 2019/02952T TR 201902952 T TR201902952 T TR 201902952T TR 201902952 T4 TR201902952 T4 TR 201902952T4
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Turkey
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exon
dmd
combinations
exon jump
oligonucleotide
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TR2019/02952T
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English (en)
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Sazani Peter
Kole Ryszard
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Sarepta Therapeutics Inc
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Application filed by Sarepta Therapeutics Inc filed Critical Sarepta Therapeutics Inc
Publication of TR201902952T4 publication Critical patent/TR201902952T4/tr

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    • C12Q2527/00—Reactions demanding special reaction conditions
    • C12Q2527/107—Temperature of melting, i.e. Tm

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  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)

Abstract

Mevcut buluş, ekson atlamasını indükleyen insan distrofin geninin bir eksonundaki bir hedef bölgeye spesifik olarak hibritlenen bir oligonükleotid ile ilgilidir. Mevcut buluş ayrıca, ekson atlama prosesini indükleyen insan distrofin geninin bir eksonundaki bir hedef bölgeye spesifik olarak hibritlenen bir oligonükleotid içeren bir farmasötik bileşim ile ilgilidir.
TR2019/02952T 2008-10-24 2009-10-23 Dmd için ekson atlama bileşimleri. TR201902952T4 (tr)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US10841608P 2008-10-24 2008-10-24

Publications (1)

Publication Number Publication Date
TR201902952T4 true TR201902952T4 (tr) 2019-03-21

Family

ID=41510869

Family Applications (1)

Application Number Title Priority Date Filing Date
TR2019/02952T TR201902952T4 (tr) 2008-10-24 2009-10-23 Dmd için ekson atlama bileşimleri.

Country Status (22)

Country Link
US (14) US8871918B2 (tr)
EP (7) EP2762567B1 (tr)
JP (10) JP5864257B2 (tr)
KR (5) KR20180118828A (tr)
CN (3) CN112574988A (tr)
AU (1) AU2009308167B2 (tr)
BR (3) BR122020021379B1 (tr)
CA (2) CA3066050A1 (tr)
CY (1) CY1122369T1 (tr)
DK (1) DK3133160T3 (tr)
ES (2) ES2714787T3 (tr)
HK (1) HK1200868A1 (tr)
HR (1) HRP20190387T1 (tr)
HU (1) HUE042979T2 (tr)
IL (6) IL304042A (tr)
LT (1) LT3133160T (tr)
PL (1) PL3133160T3 (tr)
PT (1) PT3133160T (tr)
SI (1) SI3133160T1 (tr)
TR (1) TR201902952T4 (tr)
TW (6) TWI488965B (tr)
WO (1) WO2010048586A1 (tr)

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