KR102604510B1 - 신규 아데노-관련 바이러스 캡시드 단백질 - Google Patents

신규 아데노-관련 바이러스 캡시드 단백질 Download PDF

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KR102604510B1
KR102604510B1 KR1020197001930A KR20197001930A KR102604510B1 KR 102604510 B1 KR102604510 B1 KR 102604510B1 KR 1020197001930 A KR1020197001930 A KR 1020197001930A KR 20197001930 A KR20197001930 A KR 20197001930A KR 102604510 B1 KR102604510 B1 KR 102604510B1
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KR20190032375A (ko
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피터 카메론 콜로시
마이클 로취리
로버트 엔지
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바이오마린 파머수티컬 인크.
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    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
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    • C12N15/85—Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
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    • C07K14/46—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
    • C07K14/47—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals
    • C07K14/4701—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals not used
    • C07K14/4707—Muscular dystrophy
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14122—New viral proteins or individual genes, new structural or functional aspects of known viral proteins or genes
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    • C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
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    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
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    • C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14151—Methods of production or purification of viral material
    • C12N2750/14152—Methods of production or purification of viral material relating to complementing cells and packaging systems for producing virus or viral particles
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    • C12N2799/00—Uses of viruses
    • C12N2799/02—Uses of viruses as vector
    • C12N2799/021—Uses of viruses as vector for the expression of a heterologous nucleic acid
    • C12N2799/025—Uses of viruses as vector for the expression of a heterologous nucleic acid where the vector is derived from a parvovirus

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  • Biomedical Technology (AREA)
  • General Engineering & Computer Science (AREA)
  • Animal Behavior & Ethology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Microbiology (AREA)
  • Physics & Mathematics (AREA)
  • Plant Pathology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Neurology (AREA)
  • Epidemiology (AREA)
  • Toxicology (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Peptides Or Proteins (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Saccharide Compounds (AREA)
KR1020197001930A 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질 Active KR102604510B1 (ko)

Priority Applications (1)

Application Number Priority Date Filing Date Title
KR1020237039466A KR20230161535A (ko) 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662366838P 2016-07-26 2016-07-26
US62/366,838 2016-07-26
PCT/US2017/043703 WO2018022608A2 (en) 2016-07-26 2017-07-25 Novel adeno-associated virus capsid proteins

Related Child Applications (1)

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KR1020237039466A Division KR20230161535A (ko) 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질

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KR20190032375A KR20190032375A (ko) 2019-03-27
KR102604510B1 true KR102604510B1 (ko) 2023-11-23

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KR1020237039466A Abandoned KR20230161535A (ko) 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질

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US (3) US11584780B2 (https=)
EP (1) EP3491008A2 (https=)
JP (4) JP6994018B2 (https=)
KR (2) KR102604510B1 (https=)
CN (1) CN109715650B (https=)
AU (2) AU2017301600B2 (https=)
BR (1) BR112019001532A2 (https=)
CA (1) CA3031026A1 (https=)
CL (6) CL2019000167A1 (https=)
IL (2) IL305149A (https=)
MX (1) MX2019000962A (https=)
PE (1) PE20190401A1 (https=)
PH (1) PH12019500068A1 (https=)
SG (1) SG11201811603WA (https=)
WO (1) WO2018022608A2 (https=)

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