CN110606874B - 用于基因转移到细胞、器官和组织中的变异aav和组合物、方法及用途 - Google Patents

用于基因转移到细胞、器官和组织中的变异aav和组合物、方法及用途 Download PDF

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CN110606874B
CN110606874B CN201910746995.9A CN201910746995A CN110606874B CN 110606874 B CN110606874 B CN 110606874B CN 201910746995 A CN201910746995 A CN 201910746995A CN 110606874 B CN110606874 B CN 110606874B
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CN110606874A (zh
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凯瑟琳·A·海
穆斯塔法·N·亚兹乔鲁
泽维尔·安谷拉
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Childrens Hospital of Philadelphia CHOP
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CN201910746995.9A 2013-07-22 2014-07-22 用于基因转移到细胞、器官和组织中的变异aav和组合物、方法及用途 Active CN110606874B (zh)

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US201361857161P 2013-07-22 2013-07-22
US61/857,161 2013-07-22
US201461985365P 2014-04-28 2014-04-28
US61/985,365 2014-04-28
CN201910746995.9A CN110606874B (zh) 2013-07-22 2014-07-22 用于基因转移到细胞、器官和组织中的变异aav和组合物、方法及用途
PCT/US2014/047670 WO2015013313A2 (en) 2013-07-22 2014-07-22 Variant aav and compositions, methods and uses for gene transfer to cells, organs and tissues
CN201480048028.0A CN105579465B (zh) 2013-07-22 2014-07-22 用于基因转移到细胞、器官和组织中的变异aav和组合物、方法及用途

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CN201480048028.0A Active CN105579465B (zh) 2013-07-22 2014-07-22 用于基因转移到细胞、器官和组织中的变异aav和组合物、方法及用途

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