KR102218562B1 - 유전적 병태를 치료하기 위한 방법 및 조성물 - Google Patents

유전적 병태를 치료하기 위한 방법 및 조성물 Download PDF

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KR102218562B1
KR102218562B1 KR1020157004852A KR20157004852A KR102218562B1 KR 102218562 B1 KR102218562 B1 KR 102218562B1 KR 1020157004852 A KR1020157004852 A KR 1020157004852A KR 20157004852 A KR20157004852 A KR 20157004852A KR 102218562 B1 KR102218562 B1 KR 102218562B1
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artificial sequence
sbs
globin
cell
gene
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KR20150047498A (ko
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그레고리 제이 코스트
필립 디 그레고리
드미트리 구스친
마이클 씨 홈즈
제프리 씨 밀러
데이비드 파숀
에드워드 제이 레바
안드레아스 레익
표도르 우르노프
레이 장
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상가모 테라퓨틱스, 인코포레이티드
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KR1020157004852A 2012-08-29 2013-08-29 유전적 병태를 치료하기 위한 방법 및 조성물 KR102218562B1 (ko)

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KR1020217004409A KR102474010B1 (ko) 2012-08-29 2013-08-29 유전적 병태를 치료하기 위한 방법 및 조성물

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US201261694693P 2012-08-29 2012-08-29
US61/694,693 2012-08-29
PCT/US2013/057214 WO2014036219A2 (en) 2012-08-29 2013-08-29 Methods and compositions for treatment of a genetic condition

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KR1020227041988A KR20220164090A (ko) 2012-08-29 2013-08-29 유전적 병태를 치료하기 위한 방법 및 조성물
KR1020157004852A KR102218562B1 (ko) 2012-08-29 2013-08-29 유전적 병태를 치료하기 위한 방법 및 조성물

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KR1020227041988A KR20220164090A (ko) 2012-08-29 2013-08-29 유전적 병태를 치료하기 위한 방법 및 조성물

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US (4) US9963715B2 (sl)
EP (1) EP2890780B8 (sl)
JP (4) JP2015533786A (sl)
KR (3) KR102474010B1 (sl)
CN (1) CN104704110B (sl)
AU (1) AU2013308770B2 (sl)
CA (2) CA2882499C (sl)
CL (1) CL2015000450A1 (sl)
DK (1) DK2890780T3 (sl)
EA (1) EA039384B1 (sl)
ES (1) ES2812599T3 (sl)
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HR (1) HRP20201443T1 (sl)
HU (1) HUE050516T2 (sl)
IL (1) IL237050B (sl)
IN (1) IN2015DN01480A (sl)
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PH (2) PH12015500433A1 (sl)
PL (1) PL2890780T3 (sl)
PT (1) PT2890780T (sl)
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SG (2) SG10201701601WA (sl)
SI (1) SI2890780T1 (sl)
UA (1) UA118957C2 (sl)
WO (1) WO2014036219A2 (sl)
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