CN112955153A - 肌肉靶向复合物及其用于治疗肌养蛋白病的用途 - Google Patents

肌肉靶向复合物及其用于治疗肌养蛋白病的用途 Download PDF

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CN112955153A
CN112955153A CN201980064966.2A CN201980064966A CN112955153A CN 112955153 A CN112955153 A CN 112955153A CN 201980064966 A CN201980064966 A CN 201980064966A CN 112955153 A CN112955153 A CN 112955153A
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complex
antibody
muscle
oligonucleotide
transferrin receptor
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Chinese (zh)
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罗梅什·R·苏布拉马尼亚
穆罕默德·T·卡塔纳尼
蒂莫西·威登
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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CN201980064966.2A 2018-08-02 2019-08-02 肌肉靶向复合物及其用于治疗肌养蛋白病的用途 Pending CN112955153A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862714031P 2018-08-02 2018-08-02
US62/714,031 2018-08-02
US201962855766P 2019-05-31 2019-05-31
US62/855,766 2019-05-31
PCT/US2019/044949 WO2020028832A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating dystrophinopathies

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CN112955153A true CN112955153A (zh) 2021-06-11

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US (9) US20210308273A1 (https=)
EP (1) EP3829595A4 (https=)
JP (2) JP7611825B2 (https=)
KR (1) KR20210081322A (https=)
CN (1) CN112955153A (https=)
AU (1) AU2019312692A1 (https=)
CA (1) CA3108282A1 (https=)
IL (1) IL280527A (https=)
MX (1) MX2021001281A (https=)
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WO (1) WO2020028832A1 (https=)

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