CA2904151A1 - Composition a base d'arnm du gene cftr et procedes et utilisations associes - Google Patents
Composition a base d'arnm du gene cftr et procedes et utilisations associes Download PDFInfo
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- CA2904151A1 CA2904151A1 CA2904151A CA2904151A CA2904151A1 CA 2904151 A1 CA2904151 A1 CA 2904151A1 CA 2904151 A CA2904151 A CA 2904151A CA 2904151 A CA2904151 A CA 2904151A CA 2904151 A1 CA2904151 A1 CA 2904151A1
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- Prior art keywords
- mrna
- cftr
- seq
- coding sequence
- lung
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Abstract
La présente invention concerne des matériaux, des compositions, des procédés de production et des procédés d'administration d'ARNm du gène CFTR en vue de l'induction de l'expression de la protéine CFTR, y compris dans les poumons d'un mammifère. La présente invention se révèle particulièrement utile dans le cadre du traitement de la mucoviscidose.
Applications Claiming Priority (3)
Application Number | Priority Date | Filing Date | Title |
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US201361783663P | 2013-03-14 | 2013-03-14 | |
US61/783,663 | 2013-03-14 | ||
PCT/US2014/028849 WO2014153052A2 (fr) | 2013-03-14 | 2014-03-14 | Composition à base d'arnm du gène cftr et procédés et utilisations associés |
Publications (2)
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CA2904151A1 true CA2904151A1 (fr) | 2014-09-25 |
CA2904151C CA2904151C (fr) | 2023-09-12 |
Family
ID=50513499
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CA2904151A Active CA2904151C (fr) | 2013-03-14 | 2014-03-14 | Composition a base d'arnm du gene cftr et procedes et utilisations associes |
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EP (2) | EP2968586B1 (fr) |
JP (5) | JP6316930B2 (fr) |
KR (3) | KR20210122917A (fr) |
CN (2) | CN115154620A (fr) |
AU (3) | AU2014236305B2 (fr) |
BR (1) | BR112015022868B1 (fr) |
CA (1) | CA2904151C (fr) |
CL (1) | CL2015002675A1 (fr) |
CY (1) | CY1120790T1 (fr) |
DK (1) | DK2968586T3 (fr) |
EA (2) | EA037922B1 (fr) |
ES (1) | ES2689523T3 (fr) |
HK (2) | HK1218068A1 (fr) |
HR (1) | HRP20181580T1 (fr) |
HU (1) | HUE042640T2 (fr) |
IL (5) | IL305374A (fr) |
LT (1) | LT2968586T (fr) |
MX (1) | MX365409B (fr) |
NZ (1) | NZ751462A (fr) |
PE (1) | PE20151773A1 (fr) |
PL (1) | PL2968586T3 (fr) |
PT (1) | PT2968586T (fr) |
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SG (2) | SG11201507391VA (fr) |
SI (1) | SI2968586T1 (fr) |
UA (1) | UA117008C2 (fr) |
WO (1) | WO2014153052A2 (fr) |
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