KR101835386B1 - 트랜스티레틴 발현의 조절 - Google Patents

트랜스티레틴 발현의 조절 Download PDF

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KR101835386B1
KR101835386B1 KR1020127031119A KR20127031119A KR101835386B1 KR 101835386 B1 KR101835386 B1 KR 101835386B1 KR 1020127031119 A KR1020127031119 A KR 1020127031119A KR 20127031119 A KR20127031119 A KR 20127031119A KR 101835386 B1 KR101835386 B1 KR 101835386B1
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KR20130098162A (ko
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브렛 피. 모니아
수잔 엠. 프레이어
앤드류 엠. 시우코우스키
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아이오니스 파마수티컬즈, 인코포레이티드
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KR1020127031119A 2010-04-29 2011-04-29 트랜스티레틴 발현의 조절 Active KR101835386B1 (ko)

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US32953810P 2010-04-29 2010-04-29
US61/329,538 2010-04-29
US40516310P 2010-10-20 2010-10-20
US61/405,163 2010-10-20
PCT/US2011/034661 WO2011139917A1 (en) 2010-04-29 2011-04-29 Modulation of transthyretin expression

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KR101835386B1 true KR101835386B1 (ko) 2018-03-08

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PT2937418T (pt) 2008-10-20 2018-01-23 Alnylam Pharmaceuticals Inc Composições e métodos de inibição da expressão de transtirretina
EP2496238A4 (en) 2009-11-03 2013-10-02 Alnylam Pharmaceuticals Inc FORMULATED LIPID COMPOSITIONS AND METHODS FOR INHIBITING TRANSTHYRETIN EXPRESSION (TTR)
MX343559B (es) * 2010-04-29 2016-11-10 Ionis Pharmaceuticals Inc Modulacion de la expresion de transtiretina.
EP3533873A1 (en) 2011-09-14 2019-09-04 Translate Bio MA, Inc. Multimeric oligonucleotide compounds
PE20142362A1 (es) 2011-11-18 2015-01-30 Alnylam Pharmaceuticals Inc Agentes de iarn, composiciones y metodos de uso de los mismos para tratar enfermedades asociadas con transtiretina (ttr)
AU2013262709A1 (en) 2012-05-16 2015-01-22 Rana Therapeutics, Inc. Compositions and methods for modulating MECP2 expression
US10837014B2 (en) 2012-05-16 2020-11-17 Translate Bio Ma, Inc. Compositions and methods for modulating SMN gene family expression
US9574193B2 (en) 2012-05-17 2017-02-21 Ionis Pharmaceuticals, Inc. Methods and compositions for modulating apolipoprotein (a) expression
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