JP2024099745A5 - - Google Patents
Info
- Publication number
- JP2024099745A5 JP2024099745A5 JP2024071889A JP2024071889A JP2024099745A5 JP 2024099745 A5 JP2024099745 A5 JP 2024099745A5 JP 2024071889 A JP2024071889 A JP 2024071889A JP 2024071889 A JP2024071889 A JP 2024071889A JP 2024099745 A5 JP2024099745 A5 JP 2024099745A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- oligonucleotide
- alcoholic steatohepatitis
- rcd
- cirrhosis
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (6)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762514769P | 2017-06-02 | 2017-06-02 | |
| US62/514,769 | 2017-06-02 | ||
| US201862670698P | 2018-05-11 | 2018-05-11 | |
| US62/670,698 | 2018-05-11 | ||
| JP2019566839A JP7557941B2 (ja) | 2017-06-02 | 2018-06-01 | オリゴヌクレオチド組成物及びその使用方法 |
| PCT/US2018/035721 WO2018223081A1 (en) | 2017-06-02 | 2018-06-01 | Oligonucleotide compositions and methods of use thereof |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019566839A Division JP7557941B2 (ja) | 2017-06-02 | 2018-06-01 | オリゴヌクレオチド組成物及びその使用方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024099745A JP2024099745A (ja) | 2024-07-25 |
| JP2024099745A5 true JP2024099745A5 (https=) | 2025-08-08 |
Family
ID=64456268
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019566839A Active JP7557941B2 (ja) | 2017-06-02 | 2018-06-01 | オリゴヌクレオチド組成物及びその使用方法 |
| JP2024071889A Pending JP2024099745A (ja) | 2017-06-02 | 2024-04-25 | オリゴヌクレオチド組成物及びその使用方法 |
Family Applications Before (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019566839A Active JP7557941B2 (ja) | 2017-06-02 | 2018-06-01 | オリゴヌクレオチド組成物及びその使用方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (2) | US11597927B2 (https=) |
| EP (1) | EP3630789A4 (https=) |
| JP (2) | JP7557941B2 (https=) |
| CN (2) | CN110997692B (https=) |
| CA (1) | CA3065523A1 (https=) |
| TW (1) | TW201904587A (https=) |
| WO (1) | WO2018223081A1 (https=) |
Families Citing this family (60)
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| PL2872485T3 (pl) | 2012-07-13 | 2021-05-31 | Wave Life Sciences Ltd. | Asymetryczna grupa pomocnicza |
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| WO2020196662A1 (ja) | 2019-03-25 | 2020-10-01 | 国立大学法人東京医科歯科大学 | 二本鎖核酸複合体及びその使用 |
| BR112021021203A2 (pt) | 2019-04-25 | 2022-01-04 | Wave Life Sciences Ltd | Oligonucleotídeo; composição de oligonucleotídeo quiralmente controlada; composição farmacêutica; método para prevenir, tratar ou melhorar uma afecção, distúrbio ou doença relacionada a ush2a e/ou prevenir, atrasar o início, desenvolvimento e/ou progresso, e/ou tratar uma afecção, distúrbio ou doença relacionada a ush2a em um indivíduo suscetível à mesma ou que sofre da mesma; método para aumentar o nível de salto de um éxon prejudicial em uma transcrição de gene ush2a ou seu produto de gene em uma célula; método para prevenir, atrasar o início ou progressão de, tratar ou melhorar uma afecção, distúrbio ou doença relacionada a ush2a em um indivíduo suscetível à mesma ou que sofre da mesma; método para saltar um éxon prejudicial 13 em um alelo de ush2a em um indivíduo; método para produzir ou aumentar o nível de um éxon de proteína ush2a com salto 13 em um sistema; e composto, oligonucleotídeo, composição ou método |
| SG11202111387YA (en) | 2019-04-25 | 2021-11-29 | Wave Life Sciences Ltd | Oligonucleotide compositions and methods of use thereof |
| EP3965780A4 (en) | 2019-05-09 | 2023-10-25 | Wave Life Sciences Ltd. | OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE |
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| WO2021126734A1 (en) | 2019-12-16 | 2021-06-24 | Alnylam Pharmaceuticals, Inc. | Patatin-like phospholipase domain containing 3 (pnpla3) irna compositions and methods of use thereof |
| JP2023515862A (ja) | 2020-03-01 | 2023-04-14 | ウェイブ ライフ サイエンシズ リミテッド | オリゴヌクレオチド組成物及びその方法 |
| AR121672A1 (es) | 2020-03-26 | 2022-06-29 | Arrowhead Pharmaceuticals Inc | AGENTES DE ARNi PARA INHIBIR LA EXPRESIÓN DE PNPLA3, COMPOSICIONES FARMACÉUTICAS DE ESTA, Y MÉTODOS DE USO |
| AU2021277407A1 (en) | 2020-05-22 | 2022-11-17 | Wave Life Sciences Ltd. | Oligonucleotide compositions and methods thereof |
| WO2022046667A1 (en) | 2020-08-24 | 2022-03-03 | Wave Life Sciences Ltd. | Cells and non-human animals engineered to express adar1 and uses thereof |
| WO2022046723A1 (en) | 2020-08-24 | 2022-03-03 | Wave Life Sciences Ltd. | Immunoassays for detecting wild type huntingtin protein and methods of treatment employing such immunoassays |
| KR20230118716A (ko) | 2020-11-08 | 2023-08-11 | 웨이브 라이프 사이언시스 리미티드 | 올리고뉴클레오티드 조성물 및 이의 방법 |
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2018
- 2018-06-01 CA CA3065523A patent/CA3065523A1/en active Pending
- 2018-06-01 JP JP2019566839A patent/JP7557941B2/ja active Active
- 2018-06-01 WO PCT/US2018/035721 patent/WO2018223081A1/en not_active Ceased
- 2018-06-01 US US16/618,001 patent/US11597927B2/en active Active
- 2018-06-01 CN CN201880049516.1A patent/CN110997692B/zh active Active
- 2018-06-01 EP EP18810368.3A patent/EP3630789A4/en active Pending
- 2018-06-01 TW TW107119084A patent/TW201904587A/zh unknown
- 2018-06-01 CN CN202411895814.6A patent/CN120249271A/zh active Pending
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2023
- 2023-03-03 US US18/178,470 patent/US20240175018A1/en active Pending
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2024
- 2024-04-25 JP JP2024071889A patent/JP2024099745A/ja active Pending
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