JP2023520924A5 - - Google Patents

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Publication number
JP2023520924A5
JP2023520924A5 JP2022561468A JP2022561468A JP2023520924A5 JP 2023520924 A5 JP2023520924 A5 JP 2023520924A5 JP 2022561468 A JP2022561468 A JP 2022561468A JP 2022561468 A JP2022561468 A JP 2022561468A JP 2023520924 A5 JP2023520924 A5 JP 2023520924A5
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JP
Japan
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formula
compound
heteroaryl
alkyl
aryl
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JP2022561468A
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English (en)
Japanese (ja)
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JP2023520924A (ja
JP7797407B2 (ja
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Priority claimed from PCT/US2021/026477 external-priority patent/WO2021207550A1/en
Publication of JP2023520924A publication Critical patent/JP2023520924A/ja
Publication of JP2023520924A5 publication Critical patent/JP2023520924A5/ja
Application granted granted Critical
Publication of JP7797407B2 publication Critical patent/JP7797407B2/ja
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JP2022561468A 2020-04-08 2021-04-08 スプライシングを調節するための化合物及び方法 Active JP7797407B2 (ja)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US202063007327P 2020-04-08 2020-04-08
US63/007,327 2020-04-08
US202063043920P 2020-06-25 2020-06-25
US63/043,920 2020-06-25
US202063072873P 2020-08-31 2020-08-31
US63/072,873 2020-08-31
US202063126493P 2020-12-16 2020-12-16
US63/126,493 2020-12-16
PCT/US2021/026477 WO2021207550A1 (en) 2020-04-08 2021-04-08 Compounds and methods for modulating splicing

Publications (3)

Publication Number Publication Date
JP2023520924A JP2023520924A (ja) 2023-05-22
JP2023520924A5 true JP2023520924A5 (https=) 2024-04-18
JP7797407B2 JP7797407B2 (ja) 2026-01-13

Family

ID=75747105

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022561469A Pending JP2023520925A (ja) 2020-04-08 2021-04-08 スプライシングを調節するための化合物及び方法
JP2022561468A Active JP7797407B2 (ja) 2020-04-08 2021-04-08 スプライシングを調節するための化合物及び方法

Family Applications Before (1)

Application Number Title Priority Date Filing Date
JP2022561469A Pending JP2023520925A (ja) 2020-04-08 2021-04-08 スプライシングを調節するための化合物及び方法

Country Status (14)

Country Link
US (2) US20240287097A1 (https=)
EP (2) EP4132935A1 (https=)
JP (2) JP2023520925A (https=)
KR (2) KR20230005210A (https=)
CN (2) CN116134036A (https=)
AU (2) AU2021253571A1 (https=)
BR (2) BR112022020337A2 (https=)
CA (2) CA3175205A1 (https=)
CL (1) CL2022002779A1 (https=)
CO (1) CO2022015926A2 (https=)
CR (1) CR20220567A (https=)
IL (1) IL297149A (https=)
MX (2) MX2022012676A (https=)
WO (2) WO2021207550A1 (https=)

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WO2019028440A1 (en) 2017-08-04 2019-02-07 Skyhawk Therapeutics, Inc. METHODS AND COMPOSITIONS FOR MODULATING SPLICING
WO2020163248A1 (en) 2019-02-04 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
CN114126613A (zh) 2019-02-05 2022-03-01 斯基霍克疗法公司 用于调节剪接的方法和组合物
CN113661162A (zh) 2019-02-06 2021-11-16 斯基霍克疗法公司 用于调节剪接的方法和组合物
BR112022023025A2 (pt) 2020-05-13 2023-03-28 Chdi Foundation Inc Moduladores de htt para tratar doença de huntington
WO2022194802A1 (en) * 2021-03-17 2022-09-22 F. Hoffmann-La Roche Ag New thiadiazolopyrimidone derivatives
BR112023018466A2 (pt) * 2021-03-17 2023-10-10 Hoffmann La Roche Derivados de tiazolopirimidinona
CN116997555A (zh) * 2021-03-17 2023-11-03 豪夫迈·罗氏有限公司 新颖噻吩并嘧啶酮衍生物
WO2023064879A1 (en) * 2021-10-13 2023-04-20 Remix Therapeutics Inc. Compounds and methods for modulating nucleic acid splicing
US12281116B2 (en) 2021-11-17 2025-04-22 Chdi Foundation, Inc. HTT modulators for treating Huntington's disease
AU2022398247A1 (en) * 2021-11-24 2024-06-13 Remix Therapeutics Inc. Compounds and methods for modulating splicing
CN115112899B (zh) * 2022-06-15 2024-08-16 四川大学华西医院 检测羧肽酶a4的试剂和/或系统在制备恶性胸腔积液筛查产品中的用途

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