JP2022551744A5 - - Google Patents

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Publication number
JP2022551744A5
JP2022551744A5 JP2022522332A JP2022522332A JP2022551744A5 JP 2022551744 A5 JP2022551744 A5 JP 2022551744A5 JP 2022522332 A JP2022522332 A JP 2022522332A JP 2022522332 A JP2022522332 A JP 2022522332A JP 2022551744 A5 JP2022551744 A5 JP 2022551744A5
Authority
JP
Japan
Prior art keywords
aav
sequence
introduction cassette
cassette according
protein
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022522332A
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English (en)
Japanese (ja)
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JP2022551744A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/056015 external-priority patent/WO2021076911A1/en
Publication of JP2022551744A publication Critical patent/JP2022551744A/ja
Publication of JP2022551744A5 publication Critical patent/JP2022551744A5/ja
Pending legal-status Critical Current

Links

JP2022522332A 2019-10-17 2020-10-16 Aav導入カセット Pending JP2022551744A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962916749P 2019-10-17 2019-10-17
US62/916,749 2019-10-17
US201962923253P 2019-10-18 2019-10-18
US62/923,253 2019-10-18
PCT/US2020/056015 WO2021076911A1 (en) 2019-10-17 2020-10-16 Aav transfer cassette

Publications (2)

Publication Number Publication Date
JP2022551744A JP2022551744A (ja) 2022-12-13
JP2022551744A5 true JP2022551744A5 (enExample) 2023-11-20

Family

ID=73344131

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022522332A Pending JP2022551744A (ja) 2019-10-17 2020-10-16 Aav導入カセット

Country Status (14)

Country Link
US (2) US12611436B2 (enExample)
EP (1) EP4045524A1 (enExample)
JP (1) JP2022551744A (enExample)
KR (1) KR20220083708A (enExample)
CN (1) CN114585743A (enExample)
AU (1) AU2020367825A1 (enExample)
BR (1) BR112022006946A2 (enExample)
CA (1) CA3157702A1 (enExample)
CL (1) CL2022000938A1 (enExample)
CO (1) CO2022004652A2 (enExample)
IL (1) IL292264B2 (enExample)
MX (1) MX2022004353A (enExample)
TW (1) TW202128737A (enExample)
WO (1) WO2021076911A1 (enExample)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
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MX2020010465A (es) 2018-04-03 2021-01-08 Vectores de virus para direccionamiento a tejidos oftalmicos.
BR112020020266A2 (pt) 2018-04-03 2021-01-19 Stridebio, Inc. Vetores de vírus com evasão de anticorpos
CA3095179A1 (en) 2018-04-03 2019-10-10 Stridebio, Inc. Antibody-evading virus vectors
CN113727992A (zh) 2019-03-21 2021-11-30 斯特里迪比奥公司 重组腺相关病毒载体
CN114787180A (zh) 2019-10-17 2022-07-22 斯特里迪比奥公司 用于治疗c型尼曼-匹克病的腺相关病毒载体
JP2023542614A (ja) 2020-08-19 2023-10-11 サレプタ セラピューティクス, インコーポレイテッド レット症候群の治療のためのアデノ随伴ウイルスベクター
CN119213133B (zh) 2022-05-16 2026-01-06 上海天泽云泰生物医药有限公司 用于治疗i型戊二酸尿症的重组aav载体

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