JP2022524434A5 - - Google Patents
Info
- Publication number
- JP2022524434A5 JP2022524434A5 JP2021554696A JP2021554696A JP2022524434A5 JP 2022524434 A5 JP2022524434 A5 JP 2022524434A5 JP 2021554696 A JP2021554696 A JP 2021554696A JP 2021554696 A JP2021554696 A JP 2021554696A JP 2022524434 A5 JP2022524434 A5 JP 2022524434A5
- Authority
- JP
- Japan
- Prior art keywords
- cedna vector
- itrs
- prior
- adjacent
- vector according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025016352A JP2025073123A (ja) | 2019-03-13 | 2025-02-03 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
| JP2025172911A JP2026002894A (ja) | 2019-03-13 | 2025-10-14 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962817904P | 2019-03-13 | 2019-03-13 | |
| US62/817,904 | 2019-03-13 | ||
| US201962856432P | 2019-06-03 | 2019-06-03 | |
| US62/856,432 | 2019-06-03 | ||
| PCT/US2020/022738 WO2020186207A2 (en) | 2019-03-13 | 2020-03-13 | Non-viral dna vectors and uses thereof for expressing fviii therapeutics |
Related Child Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025016352A Division JP2025073123A (ja) | 2019-03-13 | 2025-02-03 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
| JP2025172911A Division JP2026002894A (ja) | 2019-03-13 | 2025-10-14 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022524434A JP2022524434A (ja) | 2022-05-02 |
| JP2022524434A5 true JP2022524434A5 (enExample) | 2023-03-22 |
| JP7795357B2 JP7795357B2 (ja) | 2026-01-07 |
Family
ID=72426821
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021554696A Active JP7795357B2 (ja) | 2019-03-13 | 2020-03-13 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
| JP2025016352A Pending JP2025073123A (ja) | 2019-03-13 | 2025-02-03 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
| JP2025172911A Withdrawn JP2026002894A (ja) | 2019-03-13 | 2025-10-14 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025016352A Pending JP2025073123A (ja) | 2019-03-13 | 2025-02-03 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
| JP2025172911A Withdrawn JP2026002894A (ja) | 2019-03-13 | 2025-10-14 | Ｆｖｉｉｉ治療薬を発現するための非ウイルス性ｄｎａベクターおよびその使用 |
Country Status (13)
| Country | Link |
|---|---|
| US (2) | US12338275B2 (enExample) |
| EP (1) | EP3938523A4 (enExample) |
| JP (3) | JP7795357B2 (enExample) |
| KR (1) | KR20210151785A (enExample) |
| CN (1) | CN113874513A (enExample) |
| AU (1) | AU2020234713A1 (enExample) |
| BR (1) | BR112021017853A2 (enExample) |
| CA (1) | CA3133255A1 (enExample) |
| IL (1) | IL286284A (enExample) |
| MA (1) | MA55313A (enExample) |
| MX (1) | MX2021011039A (enExample) |
| SG (1) | SG11202109850SA (enExample) |
| WO (1) | WO2020186207A2 (enExample) |
Families Citing this family (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| MX2020001593A (es) | 2017-08-09 | 2020-07-13 | Bioverativ Therapeutics Inc | Moleculas de acido nucleico y usos de las mismas. |
| JP7602454B2 (ja) | 2018-08-09 | 2024-12-18 | バイオベラティブ セラピューティクス インコーポレイテッド | 核酸分子及び非ウイルス遺伝子治療のためのそれらの使用 |
| MX2023001109A (es) | 2020-07-27 | 2023-04-24 | Anjarium Biosciences Ag | Composiciones de moleculas de adn, metodos para elaborar las mismas, y metodos de usos de las mismas. |
| US20220356490A1 (en) * | 2020-08-23 | 2022-11-10 | Bioverativ Therapeutics Inc. | Baculovirus expression system |
| AU2022334714A1 (en) * | 2021-08-23 | 2024-04-04 | Bioverativ Therapeutics Inc. | Closed-end dna production with inverted terminal repeat sequences |
| WO2023028440A2 (en) * | 2021-08-23 | 2023-03-02 | Bioverativ Therapeutics Inc. | Baculovirus expression system |
| WO2023069948A1 (en) | 2021-10-18 | 2023-04-27 | Flagship Pioneering Innovations Vii, Llc | Dna compositions and related methods |
| WO2023078220A1 (zh) * | 2021-11-02 | 2023-05-11 | 苏州华毅乐健生物科技有限公司 | 分离的核酸分子及其应用 |
| JP2023089774A (ja) * | 2021-12-16 | 2023-06-28 | 株式会社三洋物産 | 遊技機 |
| WO2023135273A2 (en) * | 2022-01-14 | 2023-07-20 | Anjarium Biosciences Ag | Compositions of dna molecules encoding factor viii, methods of making thereof, and methods of use thereof |
| EP4598590A4 (en) * | 2022-10-08 | 2026-05-27 | Lingyi Biotech Co Ltd | CONSTRUCTION TO IMPROVE GENE EXPRESSION |
| WO2025110984A1 (en) * | 2023-11-21 | 2025-05-30 | Hydrogene Therapeutics, Inc. | Compositions and methods for treating wilson's disease |
| KR20260011950A (ko) | 2024-07-17 | 2026-01-26 | 이민형 | 수질 시료 채취 드론 |
Family Cites Families (17)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2220222A4 (en) | 2007-11-19 | 2011-10-12 | Univ California | NEW TEST FOR EGFR HEMMER |
| US20120263743A1 (en) * | 2009-04-30 | 2012-10-18 | Cytos Biotechnology Ag | Influenza hemagglutinin compositions and uses thereof |
| EP2500434A1 (en) * | 2011-03-12 | 2012-09-19 | Association Institut de Myologie | Capsid-free AAV vectors, compositions, and methods for vector production and gene delivery |
| AU2012340501A1 (en) * | 2011-12-19 | 2013-07-11 | Grifols, S.A. | Compositions, methods, and kits for preparing sialylated recombinant proteins |
| WO2013151664A1 (en) * | 2012-04-02 | 2013-10-10 | modeRNA Therapeutics | Modified polynucleotides for the production of proteins |
| RS61387B2 (sr) * | 2013-02-15 | 2024-06-28 | Bioverativ Therapeutics Inc | Gen optimizovanog faktora viii |
| ES2813698T3 (es) * | 2013-09-12 | 2021-03-24 | Biomarin Pharm Inc | Vectores de AAV que comprenden un gen que codifica el factor VIII |
| GB2526339A (en) | 2014-05-21 | 2015-11-25 | Imp Innovations Ltd | Lentiviral vectors |
| WO2017021359A1 (en) | 2015-08-03 | 2017-02-09 | Myodopa Limited | Systemic synthesis and regulation of l-dopa |
| JP2018535929A (ja) | 2015-09-24 | 2018-12-06 | バイオマリン ファーマシューティカル インコーポレイテッド | アデノ随伴ウイルス第ｖｉｉｉ因子ベクター、関連ウイルス粒子、及びそれらを含む治療的製剤 |
| US10143760B2 (en) * | 2015-10-28 | 2018-12-04 | Sangamo Therapeutics, Inc. | Liver-specific constructs, factor VIII expression cassettes and methods of use thereof |
| PE20231949A1 (es) * | 2015-10-30 | 2023-12-05 | Spark Therapeutics Inc | VARIANTES DEL FACTOR VIII REDUCIDO CON CpG, COMPOSICIONES Y METODOS Y USOS PARA EL TRATAMIENTO DE TRASTORNOS DE LA HEMOSTASIA |
| IL261524B2 (en) * | 2016-03-03 | 2023-10-01 | Univ Massachusetts | End-capped linear double-stranded DNA for non-viral gene transfer |
| PE20181922A1 (es) * | 2016-04-15 | 2018-12-11 | Univ Pennsylvania | Terapia genica para tratar la hemofilia a |
| KR102219859B1 (ko) * | 2016-06-24 | 2021-02-25 | 재단법인 목암생명과학연구소 | 재조합 단쇄 fviii 및 그 화학 접합물 |
| US20200237930A1 (en) | 2017-08-01 | 2020-07-30 | Spark Therapeutics, Inc. | Factor viii (fviii) gene therapy methods |
| MX2020001593A (es) * | 2017-08-09 | 2020-07-13 | Bioverativ Therapeutics Inc | Moleculas de acido nucleico y usos de las mismas. |
-
2020
- 2020-03-13 KR KR1020217029545A patent/KR20210151785A/ko not_active Ceased
- 2020-03-13 US US17/437,123 patent/US12338275B2/en active Active
- 2020-03-13 JP JP2021554696A patent/JP7795357B2/ja active Active
- 2020-03-13 EP EP20769344.1A patent/EP3938523A4/en not_active Withdrawn
- 2020-03-13 CN CN202080036209.7A patent/CN113874513A/zh active Pending
- 2020-03-13 WO PCT/US2020/022738 patent/WO2020186207A2/en not_active Ceased
- 2020-03-13 MA MA055313A patent/MA55313A/fr unknown
- 2020-03-13 BR BR112021017853A patent/BR112021017853A2/pt unknown
- 2020-03-13 AU AU2020234713A patent/AU2020234713A1/en active Pending
- 2020-03-13 CA CA3133255A patent/CA3133255A1/en active Pending
- 2020-03-13 MX MX2021011039A patent/MX2021011039A/es unknown
- 2020-03-13 SG SG11202109850S patent/SG11202109850SA/en unknown
-
2021
- 2021-09-12 IL IL286284A patent/IL286284A/en unknown
-
2025
- 2025-02-03 JP JP2025016352A patent/JP2025073123A/ja active Pending
- 2025-05-21 US US19/214,171 patent/US20250282848A1/en active Pending
- 2025-10-14 JP JP2025172911A patent/JP2026002894A/ja not_active Withdrawn
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