JP2020537501A5 - - Google Patents

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Publication number
JP2020537501A5
JP2020537501A5 JP2020515158A JP2020515158A JP2020537501A5 JP 2020537501 A5 JP2020537501 A5 JP 2020537501A5 JP 2020515158 A JP2020515158 A JP 2020515158A JP 2020515158 A JP2020515158 A JP 2020515158A JP 2020537501 A5 JP2020537501 A5 JP 2020537501A5
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JP
Japan
Prior art keywords
composition
antisense oligomer
administered
exon
oligomer conjugate
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2020515158A
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English (en)
Japanese (ja)
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JP2020537501A (ja
Filing date
Publication date
Priority claimed from PCT/US2017/066509 external-priority patent/WO2018118662A1/en
Application filed filed Critical
Priority claimed from PCT/US2018/035660 external-priority patent/WO2019059973A1/en
Publication of JP2020537501A publication Critical patent/JP2020537501A/ja
Publication of JP2020537501A5 publication Critical patent/JP2020537501A5/ja
Pending legal-status Critical Current

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JP2020515158A 2017-09-22 2018-06-01 筋ジストロフィーのためのエクソンスキッピングオリゴマーコンジュゲート Pending JP2020537501A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201762562146P 2017-09-22 2017-09-22
US62/562,146 2017-09-22
USPCT/US2017/066509 2017-12-14
PCT/US2017/066509 WO2018118662A1 (en) 2016-12-19 2017-12-14 Exon skipping oligomer conjugates for muscular dystrophy
PCT/US2018/035660 WO2019059973A1 (en) 2017-09-22 2018-06-01 OLIGOMERIC CONJUGATES FOR THE EXON JUMP FOR MUSCLE DYSTROPHY

Publications (2)

Publication Number Publication Date
JP2020537501A JP2020537501A (ja) 2020-12-24
JP2020537501A5 true JP2020537501A5 (enExample) 2021-07-26

Family

ID=65810491

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2020515158A Pending JP2020537501A (ja) 2017-09-22 2018-06-01 筋ジストロフィーのためのエクソンスキッピングオリゴマーコンジュゲート

Country Status (9)

Country Link
US (1) US20200377886A1 (enExample)
JP (1) JP2020537501A (enExample)
KR (1) KR20200057029A (enExample)
AU (1) AU2018336569A1 (enExample)
CA (1) CA3075964A1 (enExample)
EA (2) EA201991450A1 (enExample)
IL (1) IL273289A (enExample)
MX (1) MX2020003227A (enExample)
WO (1) WO2019059973A1 (enExample)

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US11638761B2 (en) 2021-07-09 2023-05-02 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating Facioscapulohumeral muscular dystrophy
US11771776B2 (en) 2021-07-09 2023-10-03 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
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CN119156395A (zh) 2022-04-22 2024-12-17 恩特拉达治疗学股份有限公司 用于递送治疗剂的环肽

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