JP2021526017A5 - - Google Patents

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Publication number
JP2021526017A5
JP2021526017A5 JP2020565430A JP2020565430A JP2021526017A5 JP 2021526017 A5 JP2021526017 A5 JP 2021526017A5 JP 2020565430 A JP2020565430 A JP 2020565430A JP 2020565430 A JP2020565430 A JP 2020565430A JP 2021526017 A5 JP2021526017 A5 JP 2021526017A5
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JP
Japan
Prior art keywords
exon
pharmaceutically acceptable
subject
antisense oligomer
acceptable salt
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JP2020565430A
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English (en)
Japanese (ja)
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JP2021526017A (ja
JP7370344B2 (ja
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Priority claimed from US15/993,287 external-priority patent/US10765760B2/en
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Publication of JP2021526017A5 publication Critical patent/JP2021526017A5/ja
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Publication of JP7370344B2 publication Critical patent/JP7370344B2/ja
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JP2020565430A 2018-05-29 2019-05-23 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート Active JP7370344B2 (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201862677484P 2018-05-29 2018-05-29
US62/677,484 2018-05-29
US15/993,287 US10765760B2 (en) 2018-05-29 2018-05-30 Exon skipping oligomer conjugates for muscular dystrophy
US15/993,287 2018-05-30
US15/993,267 US10758629B2 (en) 2018-05-29 2018-05-30 Exon skipping oligomer conjugates for muscular dystrophy
US15/993,267 2018-05-30
PCT/US2019/033768 WO2019231824A1 (en) 2018-05-29 2019-05-23 Exon skipping oligomer conjugates for muscular dystrophy

Publications (3)

Publication Number Publication Date
JP2021526017A JP2021526017A (ja) 2021-09-30
JP2021526017A5 true JP2021526017A5 (enExample) 2022-05-24
JP7370344B2 JP7370344B2 (ja) 2023-10-27

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JP2020565430A Active JP7370344B2 (ja) 2018-05-29 2019-05-23 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

Country Status (18)

Country Link
US (6) US10765760B2 (enExample)
EP (1) EP3801544A4 (enExample)
JP (1) JP7370344B2 (enExample)
KR (2) KR20260016949A (enExample)
CN (1) CN112384222B (enExample)
AR (1) AR117587A1 (enExample)
AU (1) AU2019276995B2 (enExample)
BR (1) BR112020024349A2 (enExample)
CA (1) CA3101228A1 (enExample)
CL (1) CL2020003030A1 (enExample)
EA (1) EA202092772A1 (enExample)
IL (1) IL278966B2 (enExample)
MA (1) MA52801A (enExample)
MX (1) MX2020012645A (enExample)
SA (1) SA520420562B1 (enExample)
SG (1) SG11202010018UA (enExample)
TW (1) TWI845511B (enExample)
WO (1) WO2019231824A1 (enExample)

Families Citing this family (11)

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US10765760B2 (en) 2018-05-29 2020-09-08 Sarepta Therapeutics, Inc. Exon skipping oligomer conjugates for muscular dystrophy
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JP2023515974A (ja) * 2020-02-28 2023-04-17 アイオーニス ファーマシューティカルズ, インコーポレーテッド Scn1a発現を調節するための化合物及び方法
KR20240009393A (ko) 2021-03-31 2024-01-22 엔트라다 테라퓨틱스, 인크. 사이클릭 세포 침투 펩티드
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US12378267B2 (en) 2021-06-17 2025-08-05 Entrada Therapeutics, Inc. Synthesis of FMOC-protected morpholino monomers and oligomers
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