JP2020511943A5 - - Google Patents

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Publication number
JP2020511943A5
JP2020511943A5 JP2019531380A JP2019531380A JP2020511943A5 JP 2020511943 A5 JP2020511943 A5 JP 2020511943A5 JP 2019531380 A JP2019531380 A JP 2019531380A JP 2019531380 A JP2019531380 A JP 2019531380A JP 2020511943 A5 JP2020511943 A5 JP 2020511943A5
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antisense oligomer
oligomer conjugate
administered
composition
subject
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JP2019531380A
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Japanese (ja)
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JP7160807B2 (ja
JP2020511943A (ja
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Priority claimed from PCT/US2017/066509 external-priority patent/WO2018118662A1/en
Publication of JP2020511943A publication Critical patent/JP2020511943A/ja
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Priority to JP2022164800A priority Critical patent/JP7465320B2/ja
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Publication of JP7160807B2 publication Critical patent/JP7160807B2/ja
Priority to JP2023174130A priority patent/JP2023171961A/ja
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JP2019531380A 2016-12-19 2017-12-14 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート Active JP7160807B2 (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2022164800A JP7465320B2 (ja) 2016-12-19 2022-10-13 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート
JP2023174130A JP2023171961A (ja) 2016-12-19 2023-10-06 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US201662436223P 2016-12-19 2016-12-19
US62/436,223 2016-12-19
US201762443484P 2017-01-06 2017-01-06
US62/443,484 2017-01-06
US201762479178P 2017-03-30 2017-03-30
US62/479,178 2017-03-30
US201762562146P 2017-09-22 2017-09-22
US62/562,146 2017-09-22
PCT/US2017/066509 WO2018118662A1 (en) 2016-12-19 2017-12-14 Exon skipping oligomer conjugates for muscular dystrophy

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JP2022164800A Division JP7465320B2 (ja) 2016-12-19 2022-10-13 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

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JP2020511943A JP2020511943A (ja) 2020-04-23
JP2020511943A5 true JP2020511943A5 (enExample) 2021-01-21
JP7160807B2 JP7160807B2 (ja) 2022-10-25

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JP2019531380A Active JP7160807B2 (ja) 2016-12-19 2017-12-14 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート
JP2022164800A Active JP7465320B2 (ja) 2016-12-19 2022-10-13 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート
JP2023174130A Withdrawn JP2023171961A (ja) 2016-12-19 2023-10-06 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

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JP2022164800A Active JP7465320B2 (ja) 2016-12-19 2022-10-13 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート
JP2023174130A Withdrawn JP2023171961A (ja) 2016-12-19 2023-10-06 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

Country Status (27)

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US (3) US11000600B2 (enExample)
EP (2) EP3554552B1 (enExample)
JP (3) JP7160807B2 (enExample)
KR (2) KR20240006057A (enExample)
CN (1) CN110636866B (enExample)
AU (1) AU2017382773B2 (enExample)
BR (1) BR112019012664A2 (enExample)
CA (1) CA3047010A1 (enExample)
CO (1) CO2019007399A2 (enExample)
DK (1) DK3554552T3 (enExample)
ES (1) ES2928486T3 (enExample)
HR (1) HRP20221155T1 (enExample)
HU (1) HUE059905T2 (enExample)
IL (2) IL297528A (enExample)
LT (1) LT3554552T (enExample)
MD (1) MD3554552T2 (enExample)
MX (1) MX2019006879A (enExample)
MY (1) MY205772A (enExample)
NZ (1) NZ755438A (enExample)
PL (1) PL3554552T3 (enExample)
PT (1) PT3554552T (enExample)
RS (1) RS63621B1 (enExample)
SA (1) SA519402226B1 (enExample)
SG (1) SG10202100557UA (enExample)
SM (1) SMT202200403T1 (enExample)
TW (2) TWI794197B (enExample)
WO (1) WO2018118662A1 (enExample)

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EA201991450A1 (ru) 2017-09-22 2019-12-30 Сарепта Терапьютикс, Инк. Конъюгаты олигомеров для пропуска экзона при мышечной дистрофии

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